JP2025512709A5 - - Google Patents

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Publication number
JP2025512709A5
JP2025512709A5 JP2024553306A JP2024553306A JP2025512709A5 JP 2025512709 A5 JP2025512709 A5 JP 2025512709A5 JP 2024553306 A JP2024553306 A JP 2024553306A JP 2024553306 A JP2024553306 A JP 2024553306A JP 2025512709 A5 JP2025512709 A5 JP 2025512709A5
Authority
JP
Japan
Application number
JP2024553306A
Other languages
Japanese (ja)
Other versions
JP2025512709A (ja
JPWO2023172534A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/014679 external-priority patent/WO2023172534A2/en
Publication of JP2025512709A publication Critical patent/JP2025512709A/ja
Publication of JP2025512709A5 publication Critical patent/JP2025512709A5/ja
Publication of JPWO2023172534A5 publication Critical patent/JPWO2023172534A5/ja
Pending legal-status Critical Current

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JP2024553306A 2022-03-07 2023-03-07 アンジェルマン症候群における父方由来UBE3A遺伝子発現を回復させるためのUBE3A-ATSを標的とするshRNA Pending JP2025512709A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263317154P 2022-03-07 2022-03-07
US63/317,154 2022-03-07
PCT/US2023/014679 WO2023172534A2 (en) 2022-03-07 2023-03-07 shRNA TARGETING UBE3A-ATS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN ANGELMAN SYNDROME

Publications (3)

Publication Number Publication Date
JP2025512709A JP2025512709A (ja) 2025-04-22
JP2025512709A5 true JP2025512709A5 (https=) 2026-03-16
JPWO2023172534A5 JPWO2023172534A5 (https=) 2026-03-16

Family

ID=87935840

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024553306A Pending JP2025512709A (ja) 2022-03-07 2023-03-07 アンジェルマン症候群における父方由来UBE3A遺伝子発現を回復させるためのUBE3A-ATSを標的とするshRNA

Country Status (10)

Country Link
US (1) US20230332157A1 (https=)
EP (1) EP4473114A2 (https=)
JP (1) JP2025512709A (https=)
KR (1) KR20240154664A (https=)
CN (1) CN119053703A (https=)
AU (1) AU2023232014A1 (https=)
CA (1) CA3254296A1 (https=)
IL (1) IL315364A (https=)
MX (1) MX2024010821A (https=)
WO (1) WO2023172534A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025101991A1 (en) * 2023-11-09 2025-05-15 Ionis Pharmaceuticals, Inc. Methods for modulating ube3a-ats

Family Cites Families (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US8058516B2 (en) * 2000-07-19 2011-11-15 Monsanto Technology Llc Rice metallothionein promoters
WO2017083722A1 (en) * 2015-11-11 2017-05-18 Greenberg Kenneth P Crispr compositions and methods of using the same for gene therapy
US12467929B2 (en) * 2020-04-27 2025-11-11 Biogen Ma Inc. Methods of detecting UBE3A protein

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