JP2025509262A5 - - Google Patents

Info

Publication number
JP2025509262A5
JP2025509262A5 JP2024553307A JP2024553307A JP2025509262A5 JP 2025509262 A5 JP2025509262 A5 JP 2025509262A5 JP 2024553307 A JP2024553307 A JP 2024553307A JP 2024553307 A JP2024553307 A JP 2024553307A JP 2025509262 A5 JP2025509262 A5 JP 2025509262A5
Authority
JP
Japan
Application number
JP2024553307A
Other languages
Japanese (ja)
Other versions
JPWO2023172535A5 (https=
JP2025509262A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/014680 external-priority patent/WO2023172535A2/en
Publication of JP2025509262A publication Critical patent/JP2025509262A/ja
Publication of JPWO2023172535A5 publication Critical patent/JPWO2023172535A5/ja
Publication of JP2025509262A5 publication Critical patent/JP2025509262A5/ja
Pending legal-status Critical Current

Links

JP2024553307A 2022-03-07 2023-03-07 アンジェルマン症候群における父方由来UBE3A遺伝子発現を回復させるためのSNORD115の位置を標的とするshRNA Pending JP2025509262A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263317155P 2022-03-07 2022-03-07
US63/317,155 2022-03-07
PCT/US2023/014680 WO2023172535A2 (en) 2022-03-07 2023-03-07 shRNA TARGETING SNORD115 LOCATIONS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN ANGELMAN SYNDROME

Publications (3)

Publication Number Publication Date
JP2025509262A JP2025509262A (ja) 2025-04-11
JPWO2023172535A5 JPWO2023172535A5 (https=) 2026-03-16
JP2025509262A5 true JP2025509262A5 (https=) 2026-03-16

Family

ID=87935834

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024553307A Pending JP2025509262A (ja) 2022-03-07 2023-03-07 アンジェルマン症候群における父方由来UBE3A遺伝子発現を回復させるためのSNORD115の位置を標的とするshRNA

Country Status (10)

Country Link
US (1) US20230332150A1 (https=)
EP (1) EP4473116A2 (https=)
JP (1) JP2025509262A (https=)
KR (1) KR20240155345A (https=)
CN (1) CN119384504A (https=)
AU (1) AU2023231550A1 (https=)
CA (1) CA3259398A1 (https=)
IL (1) IL315359A (https=)
MX (1) MX2024010820A (https=)
WO (1) WO2023172535A2 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025101533A1 (en) * 2023-11-09 2025-05-15 Encoded Therapeutics, Inc. Methods and compositions for increasing expression of ube3a

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20150329857A1 (en) * 2011-12-28 2015-11-19 Universite Pierre Et Marie Curie (Paris 6) Rna interference to activate stem cells
PT3717646T (pt) * 2017-12-01 2025-07-28 Texas A & M Univ Sys Tratamento antisense da síndrome de angelman
CA3113648A1 (en) * 2018-09-21 2020-03-26 University Of Connecticut Compositions and methods to restore paternal ube3a gene expression in human angelman syndrome
CA3133294A1 (en) * 2019-03-15 2020-09-24 Mir Scientific, Llc Methods for predicting prostate cancer and uses thereof

Similar Documents

Publication Publication Date Title
JP2025509262A5 (https=)
BR102022025291A2 (https=)
BR102023014872A2 (https=)
BR102023012440A2 (https=)
BR102023010976A2 (https=)
BR102023009641A2 (https=)
BR102023008688A2 (https=)
BR102023007252A2 (https=)
BR102023005164A2 (https=)
BR102023000289A2 (https=)
BR102022026909A2 (https=)
BR202022009269U2 (https=)
BR202022005961U2 (https=)
BR202022001779U2 (https=)
BR202022000931U2 (https=)
BY13150U (https=)
BY13159U (https=)
BY13140U (https=)
BY13141U (https=)
BY13142U (https=)
BY13143U (https=)
BY13144U (https=)
BY13145U (https=)
BY13149U (https=)
BY13135U (https=)