JP2022554141A5 - - Google Patents

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Publication number
JP2022554141A5
JP2022554141A5 JP2022523856A JP2022523856A JP2022554141A5 JP 2022554141 A5 JP2022554141 A5 JP 2022554141A5 JP 2022523856 A JP2022523856 A JP 2022523856A JP 2022523856 A JP2022523856 A JP 2022523856A JP 2022554141 A5 JP2022554141 A5 JP 2022554141A5
Authority
JP
Japan
Application number
JP2022523856A
Other languages
Japanese (ja)
Other versions
JP2022554141A (ja
JPWO2021081338A5 (https=
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2020/057081 external-priority patent/WO2021081338A1/en
Publication of JP2022554141A publication Critical patent/JP2022554141A/ja
Publication of JPWO2021081338A5 publication Critical patent/JPWO2021081338A5/ja
Publication of JP2022554141A5 publication Critical patent/JP2022554141A5/ja
Pending legal-status Critical Current

Links

JP2022523856A 2019-10-25 2020-10-23 糖原病を治療するための組成物及び方法 Pending JP2022554141A (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201962926282P 2019-10-25 2019-10-25
US62/926,282 2019-10-25
US202063083349P 2020-09-25 2020-09-25
US63/083,349 2020-09-25
PCT/US2020/057081 WO2021081338A1 (en) 2019-10-25 2020-10-23 Compositions and methods for treating glycogen storage disorders

Publications (3)

Publication Number Publication Date
JP2022554141A JP2022554141A (ja) 2022-12-28
JPWO2021081338A5 JPWO2021081338A5 (https=) 2023-10-31
JP2022554141A5 true JP2022554141A5 (https=) 2023-10-31

Family

ID=75620302

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022523856A Pending JP2022554141A (ja) 2019-10-25 2020-10-23 糖原病を治療するための組成物及び方法

Country Status (14)

Country Link
US (1) US20220387562A1 (https=)
EP (1) EP4048286A4 (https=)
JP (1) JP2022554141A (https=)
KR (1) KR20220105643A (https=)
CN (1) CN114828858A (https=)
AU (1) AU2020372429A1 (https=)
BR (1) BR112022007674A2 (https=)
CA (1) CA3158281A1 (https=)
CO (1) CO2022006772A2 (https=)
IL (1) IL292401A (https=)
MX (1) MX2022004799A (https=)
PH (1) PH12022550977A1 (https=)
TW (2) TWI885000B (https=)
WO (1) WO2021081338A1 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR20240145491A (ko) * 2022-02-03 2024-10-07 아스텔라스 진 테라피스, 인크. 폼페병의 개선된 치료를 위한 조성물 및 방법
JP2025527694A (ja) 2022-08-23 2025-08-22 マストバイオ株式会社 Il2変異体及びそれを含むタンパク質複合体

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
ATE437944T1 (de) * 2000-04-28 2009-08-15 Asklepios Biopharmaceutical In Für das dystrophin-minigen kodierende dna- sequenzen und verfahren zu deren verwendung
ATE400656T1 (de) * 2000-10-06 2008-07-15 Univ Michigan Mini-dystrophin nukleinsäure- und peptidsequenzen
RS61055B1 (sr) * 2012-06-19 2020-12-31 Univ Florida Kompozicije i postupci za lečenje bolesti
EA201890543A1 (ru) * 2015-09-17 2018-08-31 Рисёрч Инститьют Эт Нэйшнвайд Чилдрен'С Хоспитэл Способы и материалы для генной терапии galgt2
EP3293260A1 (en) * 2016-09-12 2018-03-14 Genethon Acid-alpha glucosidase variants and uses thereof
WO2019012336A2 (en) * 2017-03-17 2019-01-17 Newcastle University ADENO-ASSOCIATED VIRAL VECTOR DELIVERY OF A MICRO-DYSTROPHIN FRAGMENT FOR TREATING MUSCLE DYSTROPHY
EP3648776A4 (en) * 2017-07-06 2021-04-07 The Medical College of Wisconsin, Inc. NEW IN-VITRO AND IN-VIVO ENRICHMENT STRATEGY AGAINST LYMPHOCYTE FROM VECTOR-TRANSDUCED HSC FOR THE TREATMENT OF DISEASES
US12296026B2 (en) * 2018-02-05 2025-05-13 Astellas Gene Therapies, Inc. Transcription regulatory elements and uses thereof
EP3749771A1 (en) * 2018-02-07 2020-12-16 Genethon Hybrid regulatory elements

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