JP2022554141A5 - - Google Patents
Info
- Publication number
- JP2022554141A5 JP2022554141A5 JP2022523856A JP2022523856A JP2022554141A5 JP 2022554141 A5 JP2022554141 A5 JP 2022554141A5 JP 2022523856 A JP2022523856 A JP 2022523856A JP 2022523856 A JP2022523856 A JP 2022523856A JP 2022554141 A5 JP2022554141 A5 JP 2022554141A5
- Authority
- JP
- Japan
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962926282P | 2019-10-25 | 2019-10-25 | |
| US62/926,282 | 2019-10-25 | ||
| US202063083349P | 2020-09-25 | 2020-09-25 | |
| US63/083,349 | 2020-09-25 | ||
| PCT/US2020/057081 WO2021081338A1 (en) | 2019-10-25 | 2020-10-23 | Compositions and methods for treating glycogen storage disorders |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022554141A JP2022554141A (ja) | 2022-12-28 |
| JPWO2021081338A5 JPWO2021081338A5 (https=) | 2023-10-31 |
| JP2022554141A5 true JP2022554141A5 (https=) | 2023-10-31 |
Family
ID=75620302
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2022523856A Pending JP2022554141A (ja) | 2019-10-25 | 2020-10-23 | 糖原病を治療するための組成物及び方法 |
Country Status (14)
| Country | Link |
|---|---|
| US (1) | US20220387562A1 (https=) |
| EP (1) | EP4048286A4 (https=) |
| JP (1) | JP2022554141A (https=) |
| KR (1) | KR20220105643A (https=) |
| CN (1) | CN114828858A (https=) |
| AU (1) | AU2020372429A1 (https=) |
| BR (1) | BR112022007674A2 (https=) |
| CA (1) | CA3158281A1 (https=) |
| CO (1) | CO2022006772A2 (https=) |
| IL (1) | IL292401A (https=) |
| MX (1) | MX2022004799A (https=) |
| PH (1) | PH12022550977A1 (https=) |
| TW (2) | TWI885000B (https=) |
| WO (1) | WO2021081338A1 (https=) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20240145491A (ko) * | 2022-02-03 | 2024-10-07 | 아스텔라스 진 테라피스, 인크. | 폼페병의 개선된 치료를 위한 조성물 및 방법 |
| JP2025527694A (ja) | 2022-08-23 | 2025-08-22 | マストバイオ株式会社 | Il2変異体及びそれを含むタンパク質複合体 |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| ATE437944T1 (de) * | 2000-04-28 | 2009-08-15 | Asklepios Biopharmaceutical In | Für das dystrophin-minigen kodierende dna- sequenzen und verfahren zu deren verwendung |
| ATE400656T1 (de) * | 2000-10-06 | 2008-07-15 | Univ Michigan | Mini-dystrophin nukleinsäure- und peptidsequenzen |
| RS61055B1 (sr) * | 2012-06-19 | 2020-12-31 | Univ Florida | Kompozicije i postupci za lečenje bolesti |
| EA201890543A1 (ru) * | 2015-09-17 | 2018-08-31 | Рисёрч Инститьют Эт Нэйшнвайд Чилдрен'С Хоспитэл | Способы и материалы для генной терапии galgt2 |
| EP3293260A1 (en) * | 2016-09-12 | 2018-03-14 | Genethon | Acid-alpha glucosidase variants and uses thereof |
| WO2019012336A2 (en) * | 2017-03-17 | 2019-01-17 | Newcastle University | ADENO-ASSOCIATED VIRAL VECTOR DELIVERY OF A MICRO-DYSTROPHIN FRAGMENT FOR TREATING MUSCLE DYSTROPHY |
| EP3648776A4 (en) * | 2017-07-06 | 2021-04-07 | The Medical College of Wisconsin, Inc. | NEW IN-VITRO AND IN-VIVO ENRICHMENT STRATEGY AGAINST LYMPHOCYTE FROM VECTOR-TRANSDUCED HSC FOR THE TREATMENT OF DISEASES |
| US12296026B2 (en) * | 2018-02-05 | 2025-05-13 | Astellas Gene Therapies, Inc. | Transcription regulatory elements and uses thereof |
| EP3749771A1 (en) * | 2018-02-07 | 2020-12-16 | Genethon | Hybrid regulatory elements |
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2020
- 2020-10-23 WO PCT/US2020/057081 patent/WO2021081338A1/en not_active Ceased
- 2020-10-23 BR BR112022007674A patent/BR112022007674A2/pt unknown
- 2020-10-23 JP JP2022523856A patent/JP2022554141A/ja active Pending
- 2020-10-23 EP EP20880074.8A patent/EP4048286A4/en active Pending
- 2020-10-23 CA CA3158281A patent/CA3158281A1/en active Pending
- 2020-10-23 TW TW109136852A patent/TWI885000B/zh active
- 2020-10-23 MX MX2022004799A patent/MX2022004799A/es unknown
- 2020-10-23 TW TW114116784A patent/TW202600177A/zh unknown
- 2020-10-23 PH PH1/2022/550977A patent/PH12022550977A1/en unknown
- 2020-10-23 KR KR1020227017631A patent/KR20220105643A/ko active Pending
- 2020-10-23 US US17/771,627 patent/US20220387562A1/en active Pending
- 2020-10-23 CN CN202080086069.4A patent/CN114828858A/zh active Pending
- 2020-10-23 AU AU2020372429A patent/AU2020372429A1/en active Pending
- 2020-10-23 IL IL292401A patent/IL292401A/en unknown
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2022
- 2022-05-23 CO CONC2022/0006772A patent/CO2022006772A2/es unknown