JP2024530050A5 - - Google Patents
Info
- Publication number
- JP2024530050A5 JP2024530050A5 JP2024508455A JP2024508455A JP2024530050A5 JP 2024530050 A5 JP2024530050 A5 JP 2024530050A5 JP 2024508455 A JP2024508455 A JP 2024508455A JP 2024508455 A JP2024508455 A JP 2024508455A JP 2024530050 A5 JP2024530050 A5 JP 2024530050A5
- Authority
- JP
- Japan
- Prior art keywords
- hemisphere
- patient
- aav
- acid sequence
- aav vector
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163232053P | 2021-08-11 | 2021-08-11 | |
| US63/232,053 | 2021-08-11 | ||
| US202263331614P | 2022-04-15 | 2022-04-15 | |
| US63/331,614 | 2022-04-15 | ||
| PCT/EP2022/072487 WO2023017098A2 (en) | 2021-08-11 | 2022-08-10 | Compositions and methods for improved treatment of disorders affecting the central nervous system |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024530050A JP2024530050A (ja) | 2024-08-14 |
| JP2024530050A5 true JP2024530050A5 (https=) | 2025-08-20 |
Family
ID=83232657
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024508455A Pending JP2024530050A (ja) | 2021-08-11 | 2022-08-10 | 中枢神経系に影響を及ぼす障害の改善された治療のための組成物及び方法 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20240358794A1 (https=) |
| EP (1) | EP4384195A2 (https=) |
| JP (1) | JP2024530050A (https=) |
| AU (1) | AU2022327583A1 (https=) |
| CA (1) | CA3228916A1 (https=) |
| WO (1) | WO2023017098A2 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN117286119A (zh) * | 2023-09-06 | 2023-12-26 | 复旦大学附属中山医院 | 可静脉注射给药的tpk表达病毒及其治疗阿尔茨海默病的应用 |
Family Cites Families (18)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5139941A (en) | 1985-10-31 | 1992-08-18 | University Of Florida Research Foundation, Inc. | AAV transduction vectors |
| US5541307A (en) | 1990-07-27 | 1996-07-30 | Isis Pharmaceuticals, Inc. | Backbone modified oligonucleotide analogs and solid phase synthesis thereof |
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| DK0752248T3 (da) | 1992-11-13 | 2000-11-13 | Idec Pharma Corp | Terapeutisk anvendelse af kimæriske og radioaktivt mærkede antistoffer mod humant B-lymfocytbegrænset differentieringsantig |
| US5869305A (en) | 1992-12-04 | 1999-02-09 | The University Of Pittsburgh | Recombinant viral vector system |
| US6204059B1 (en) | 1994-06-30 | 2001-03-20 | University Of Pittsburgh | AAV capsid vehicles for molecular transfer |
| US6001650A (en) | 1995-08-03 | 1999-12-14 | Avigen, Inc. | High-efficiency wild-type-free AAV helper functions |
| WO1998011244A2 (en) | 1996-09-11 | 1998-03-19 | The Government Of The United States Of America, Represented By The Secretary, Department Of Health And Human Services | Aav4 vector and uses thereof |
| US6156303A (en) | 1997-06-11 | 2000-12-05 | University Of Washington | Adeno-associated virus (AAV) isolates and AAV vectors derived therefrom |
| WO1999061601A2 (en) | 1998-05-28 | 1999-12-02 | The Government Of The United States Of America, As Represented By The Secretary, Department Of Health And Human Services | Aav5 vector and uses thereof |
| ATE362542T1 (de) | 1998-11-05 | 2007-06-15 | Univ Pennsylvania | Nukleinsäuresequenzen des adeno-assoziierten virus des serotyps i, und vektoren und wirtszellen, die diese enthalten |
| DK2311848T3 (da) | 2002-12-23 | 2013-10-14 | Vical Inc | Kodon-optimerede polynukleotidbaserede vacciner mod human cytomegalovirus-infektion |
| US7561973B1 (en) | 2008-07-31 | 2009-07-14 | Dna Twopointo, Inc. | Methods for determining properties that affect an expression property value of polynucleotides in an expression system |
| US7561972B1 (en) | 2008-06-06 | 2009-07-14 | Dna Twopointo, Inc. | Synthetic nucleic acids for expression of encoded proteins |
| US20130090374A1 (en) * | 2011-04-20 | 2013-04-11 | Miguel Sena-Esteves | Methods for the treatment of tay-sachs disease, sandhoff disease, and gm1-gangliosidosis |
| JP6028979B2 (ja) | 2012-01-30 | 2016-11-24 | 日東電工株式会社 | 核酸固相合成用リンカー及び担体 |
| WO2021016505A1 (en) * | 2019-07-24 | 2021-01-28 | Voyager Therapeutics, Inc. | Compositions and methods for treating huntington's disease |
| GB201913974D0 (en) * | 2019-09-27 | 2019-11-13 | King S College London | Vector |
-
2022
- 2022-08-10 CA CA3228916A patent/CA3228916A1/en active Pending
- 2022-08-10 EP EP22765761.6A patent/EP4384195A2/en active Pending
- 2022-08-10 US US18/682,625 patent/US20240358794A1/en active Pending
- 2022-08-10 WO PCT/EP2022/072487 patent/WO2023017098A2/en not_active Ceased
- 2022-08-10 AU AU2022327583A patent/AU2022327583A1/en active Pending
- 2022-08-10 JP JP2024508455A patent/JP2024530050A/ja active Pending
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