JP2025516186A5 - - Google Patents

Info

Publication number
JP2025516186A5
JP2025516186A5 JP2024563225A JP2024563225A JP2025516186A5 JP 2025516186 A5 JP2025516186 A5 JP 2025516186A5 JP 2024563225 A JP2024563225 A JP 2024563225A JP 2024563225 A JP2024563225 A JP 2024563225A JP 2025516186 A5 JP2025516186 A5 JP 2025516186A5
Authority
JP
Japan
Prior art keywords
aav
polynucleotide
disease
use according
expression vector
Prior art date
Application number
JP2024563225A
Other languages
English (en)
Japanese (ja)
Other versions
JP2025516186A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2023/066117 external-priority patent/WO2023212521A2/en
Publication of JP2025516186A publication Critical patent/JP2025516186A/ja
Publication of JP2025516186A5 publication Critical patent/JP2025516186A5/ja
Pending legal-status Critical Current

Links

JP2024563225A 2022-04-25 2023-04-24 ミエリンの障害の治療 Pending JP2025516186A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202263363529P 2022-04-25 2022-04-25
US63/363,529 2022-04-25
PCT/US2023/066117 WO2023212521A2 (en) 2022-04-25 2023-04-24 Treatments of disorders of myelin

Publications (2)

Publication Number Publication Date
JP2025516186A JP2025516186A (ja) 2025-05-27
JP2025516186A5 true JP2025516186A5 (https=) 2026-05-01

Family

ID=88519762

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024563225A Pending JP2025516186A (ja) 2022-04-25 2023-04-24 ミエリンの障害の治療

Country Status (5)

Country Link
US (1) US20250171778A1 (https=)
EP (1) EP4514402A2 (https=)
JP (1) JP2025516186A (https=)
CN (1) CN119451703A (https=)
WO (1) WO2023212521A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025160429A1 (en) * 2024-01-26 2025-07-31 Genzyme Corporation Artificial micrornas targeting snca
WO2025228394A1 (zh) * 2024-04-30 2025-11-06 艾码生物科技(南京)有限公司 递送初级微小rna的方法及其应用

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
IL248102B (en) * 2014-05-02 2022-07-01 Genzyme Corp aav vectors for gene therapy of the central nervous system and retina
CA3193406A1 (en) * 2020-09-21 2022-03-24 Asklepios Biopharmaceutical, Inc. Methods for treating neurological disease

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