JP2025512061A5 - - Google Patents
Info
- Publication number
- JP2025512061A5 JP2025512061A5 JP2024560444A JP2024560444A JP2025512061A5 JP 2025512061 A5 JP2025512061 A5 JP 2025512061A5 JP 2024560444 A JP2024560444 A JP 2024560444A JP 2024560444 A JP2024560444 A JP 2024560444A JP 2025512061 A5 JP2025512061 A5 JP 2025512061A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- rna
- nucleic acid
- sequence encoding
- expression cassette
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| EP22168001 | 2022-04-12 | ||
| EP22168001.0 | 2022-04-12 | ||
| PCT/EP2023/059361 WO2023198663A1 (en) | 2022-04-12 | 2023-04-11 | Nucleic acid regulation of snca |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2025512061A JP2025512061A (ja) | 2025-04-16 |
| JP2025512061A5 true JP2025512061A5 (https=) | 2026-03-26 |
Family
ID=81580388
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024560444A Pending JP2025512061A (ja) | 2022-04-12 | 2023-04-11 | Ｓｎｃａの核酸調節 |
Country Status (4)
| Country | Link |
|---|---|
| US (1) | US20250297252A1 (https=) |
| EP (1) | EP4508216A1 (https=) |
| JP (1) | JP2025512061A (https=) |
| WO (1) | WO2023198663A1 (https=) |
Families Citing this family (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| WO2025160429A1 (en) * | 2024-01-26 | 2025-07-31 | Genzyme Corporation | Artificial micrornas targeting snca |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US6103526A (en) | 1998-10-08 | 2000-08-15 | Protein Sciences Corporation | Spodoptera frugiperda single cell suspension cell line in serum-free media, methods of producing and using |
| EP2311966A3 (en) | 2005-10-20 | 2012-09-05 | Amsterdam Molecular Therapeutics (AMT) B.V. | Improved AAV vectors produced in insect cells |
| CN103849629B (zh) | 2006-06-21 | 2017-06-09 | 尤尼克尔Ip股份有限公司 | 具有经修饰的用于在昆虫细胞中产生aav的aav‑rep78翻译起始密码子的载体 |
| DK2173888T3 (en) | 2007-07-26 | 2016-11-28 | Uniqure Ip Bv | Baculovirus vectors comprising repeating coding sequences WITH differential preferred codons |
| JP2011512156A (ja) | 2008-02-19 | 2011-04-21 | アムステルダム モレキュラー セラピューティクス ビー．ブイ． | 昆虫細胞におけるパルボウイルスｒｅｐ及びｃａｐタンパク質の発現の最適化 |
| WO2011122950A1 (en) | 2010-04-01 | 2011-10-06 | Amsterdam Molecular Therapeutics (Amt) Ip B.V. | Monomeric duplex aav vectors |
| US9290759B2 (en) * | 2010-08-25 | 2016-03-22 | The Trustees Of Columbia University In The City Of New York | Optimized miRNA constructs |
| JP6198278B2 (ja) | 2011-09-08 | 2017-09-20 | ユニキュアー アイピー ビー．ブイ． | Ａａｖ調製物からの混入ウイルスの除去 |
| CA2942289C (en) | 2014-03-10 | 2024-05-21 | Uniqure Ip B.V. | Further improved aav vectors produced in insect cells |
| HRP20190992T1 (hr) | 2014-12-24 | 2019-09-20 | Uniqure Ip B.V. | Suprimiranje gena za huntingtin inducirano s rnai |
| EP3655538A1 (en) | 2017-07-20 | 2020-05-27 | uniQure IP B.V. | Improved aav capsid production in insect cells |
| WO2020053258A1 (en) * | 2018-09-12 | 2020-03-19 | Uniqure Ip B.V. | Rnai induced c9orf72 suppression for the treatment of als/ftd |
-
2023
- 2023-04-11 EP EP23719660.5A patent/EP4508216A1/en active Pending
- 2023-04-11 JP JP2024560444A patent/JP2025512061A/ja active Pending
- 2023-04-11 WO PCT/EP2023/059361 patent/WO2023198663A1/en not_active Ceased
- 2023-04-11 US US18/853,724 patent/US20250297252A1/en active Pending
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