JP2025512061A5 - - Google Patents

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Publication number
JP2025512061A5
JP2025512061A5 JP2024560444A JP2024560444A JP2025512061A5 JP 2025512061 A5 JP2025512061 A5 JP 2025512061A5 JP 2024560444 A JP2024560444 A JP 2024560444A JP 2024560444 A JP2024560444 A JP 2024560444A JP 2025512061 A5 JP2025512061 A5 JP 2025512061A5
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JP
Japan
Application number
JP2024560444A
Other languages
Japanese (ja)
Other versions
JP2025512061A (ja
JPWO2023198663A5 (https=
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Publication date
Application filed filed Critical
Priority claimed from PCT/EP2023/059361 external-priority patent/WO2023198663A1/en
Publication of JP2025512061A publication Critical patent/JP2025512061A/ja
Publication of JPWO2023198663A5 publication Critical patent/JPWO2023198663A5/ja
Publication of JP2025512061A5 publication Critical patent/JP2025512061A5/ja
Pending legal-status Critical Current

Links

JP2024560444A 2022-04-12 2023-04-11 Sncaの核酸調節 Pending JP2025512061A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
EP22168001.0 2022-04-12
EP22168001 2022-04-12
PCT/EP2023/059361 WO2023198663A1 (en) 2022-04-12 2023-04-11 Nucleic acid regulation of snca

Publications (3)

Publication Number Publication Date
JP2025512061A JP2025512061A (ja) 2025-04-16
JPWO2023198663A5 JPWO2023198663A5 (https=) 2026-03-26
JP2025512061A5 true JP2025512061A5 (https=) 2026-03-26

Family

ID=81580388

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024560444A Pending JP2025512061A (ja) 2022-04-12 2023-04-11 Sncaの核酸調節

Country Status (4)

Country Link
US (1) US20250297252A1 (https=)
EP (1) EP4508216A1 (https=)
JP (1) JP2025512061A (https=)
WO (1) WO2023198663A1 (https=)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2025160429A1 (en) * 2024-01-26 2025-07-31 Genzyme Corporation Artificial micrornas targeting snca

Family Cites Families (12)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US6103526A (en) 1998-10-08 2000-08-15 Protein Sciences Corporation Spodoptera frugiperda single cell suspension cell line in serum-free media, methods of producing and using
EP2311967B1 (en) 2005-10-20 2017-09-20 UniQure IP B.V. Improved AAV vectors produced in insect cells
KR101589259B1 (ko) 2006-06-21 2016-02-01 유니큐어 아이피 비.브이. 곤충세포 내 aav의 생산에 유용한 aav-rep78의 번역을 위한 변형된 개시 코돈을 갖는 벡터
SI3093345T1 (sl) 2007-07-26 2019-08-30 Uniqure Ip B.V. Bakulovirusni vektorji, ki vsebujejo ponavljajoča kodirna zaporedja z različnimi kodonskimi preferencami
EP3257937B1 (en) 2008-02-19 2022-08-03 uniQure IP B.V. Optimisation of expression of parvoviral rep and cap proteins in insect cells
WO2011122950A1 (en) 2010-04-01 2011-10-06 Amsterdam Molecular Therapeutics (Amt) Ip B.V. Monomeric duplex aav vectors
WO2012027558A2 (en) * 2010-08-25 2012-03-01 The Trustees Of Columbia University In The City Of New York OPTIMIZED miRNA CONSTRUCTS
PT2744895E (pt) 2011-09-08 2016-02-08 Uniqure Ip Bv Remoção de vírus contaminantes de preparações de aav
WO2015137802A1 (en) 2014-03-10 2015-09-17 Uniqure Ip B.V. Further improved aav vectors produced in insect cells
AU2015370903B2 (en) 2014-12-24 2021-06-17 Uniqure Ip B.V. RNAi induced huntingtin gene suppression
JP7666922B2 (ja) 2017-07-20 2025-04-22 ユニキュアー アイピー ビー.ブイ. 昆虫細胞における向上したaavカプシド産生
EP3850098A1 (en) * 2018-09-12 2021-07-21 uniQure IP B.V. Rnai induced c9orf72 suppression for the treatment of als/ftd

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