JP2023528755A5 - - Google Patents

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Publication number
JP2023528755A5
JP2023528755A5 JP2022569071A JP2022569071A JP2023528755A5 JP 2023528755 A5 JP2023528755 A5 JP 2023528755A5 JP 2022569071 A JP2022569071 A JP 2022569071A JP 2022569071 A JP2022569071 A JP 2022569071A JP 2023528755 A5 JP2023528755 A5 JP 2023528755A5
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JP
Japan
Prior art keywords
sequence
seq
nucleic acid
oligomer compound
equal
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2022569071A
Other languages
English (en)
Japanese (ja)
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JP2023528755A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/036873 external-priority patent/WO2021252799A2/en
Publication of JP2023528755A publication Critical patent/JP2023528755A/ja
Publication of JP2023528755A5 publication Critical patent/JP2023528755A5/ja
Pending legal-status Critical Current

Links

JP2022569071A 2020-06-11 2021-06-10 Msh3の発現を低減するための化合物及び方法 Pending JP2023528755A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202063038024P 2020-06-11 2020-06-11
US63/038,024 2020-06-11
US202063045728P 2020-06-29 2020-06-29
US63/045,728 2020-06-29
US202163178203P 2021-04-22 2021-04-22
US63/178,203 2021-04-22
PCT/US2021/036873 WO2021252799A2 (en) 2020-06-11 2021-06-10 Compounds and methods for reducing msh3 expression

Publications (2)

Publication Number Publication Date
JP2023528755A JP2023528755A (ja) 2023-07-06
JP2023528755A5 true JP2023528755A5 (https=) 2024-06-17

Family

ID=78846536

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2022569071A Pending JP2023528755A (ja) 2020-06-11 2021-06-10 Msh3の発現を低減するための化合物及び方法

Country Status (4)

Country Link
US (1) US20230235331A1 (https=)
EP (1) EP4164656A4 (https=)
JP (1) JP2023528755A (https=)
WO (1) WO2021252799A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20230313185A1 (en) * 2020-05-08 2023-10-05 Triplet Therapeutics, Inc. Methods for the treatment of nucleotide repeat expansion disorders associated with msh3 activity
CN119173632A (zh) * 2022-05-10 2024-12-20 豪夫迈·罗氏有限公司 靶向cfp-elk1基因间区域的反义寡核苷酸

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP1432724A4 (en) * 2002-02-20 2006-02-01 Sirna Therapeutics Inc RNA inhibition mediated inhibition of MAP KINASE GENES
EP2462937A1 (en) * 2005-05-24 2012-06-13 Isis Pharmaceuticals, Inc. Modulation of LMW-PTPase Expression
WO2015051283A1 (en) * 2013-10-04 2015-04-09 Rana Therapeutics, Inc. Compositions and methods for treating amyotrophic lateral sclerosis
WO2015171918A2 (en) * 2014-05-07 2015-11-12 Louisiana State University And Agricultural And Mechanical College Compositions and uses for treatment thereof
US10633410B2 (en) * 2014-12-22 2020-04-28 University Of Iowa Research Foundation Nucleic acid aptamers to treat histone-induced disease states
AU2016344609B2 (en) * 2015-10-28 2022-05-12 Vertex Pharmaceuticals Incorporated Materials and methods for treatment of duchenne muscular dystrophy
JP7714162B6 (ja) * 2018-12-03 2025-09-08 タケダ ファーマシューティカルズ ユーエスエー インコーポレイテッド Msh3活性に関連するトリヌクレオチドリピート伸長障害の処置のための方法
US20210355491A1 (en) * 2020-04-20 2021-11-18 University Of Massachusetts Oligonucleotides for msh3 modulation
US20230313185A1 (en) * 2020-05-08 2023-10-05 Triplet Therapeutics, Inc. Methods for the treatment of nucleotide repeat expansion disorders associated with msh3 activity

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