JP2024522147A5 - - Google Patents

Info

Publication number
JP2024522147A5
JP2024522147A5 JP2023574553A JP2023574553A JP2024522147A5 JP 2024522147 A5 JP2024522147 A5 JP 2024522147A5 JP 2023574553 A JP2023574553 A JP 2023574553A JP 2023574553 A JP2023574553 A JP 2023574553A JP 2024522147 A5 JP2024522147 A5 JP 2024522147A5
Authority
JP
Japan
Prior art keywords
oligonucleotide
pharmaceutically acceptable
composition according
place
spinocerebellar ataxia
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023574553A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024522147A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/032128 external-priority patent/WO2022256631A2/en
Publication of JP2024522147A publication Critical patent/JP2024522147A/ja
Publication of JP2024522147A5 publication Critical patent/JP2024522147A5/ja
Pending legal-status Critical Current

Links

JP2023574553A 2021-06-04 2022-06-03 Ｍｓｈ３活性と関連するヌクレオチドリピート伸長障害の治療方法 Pending JP2024522147A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163196896P 2021-06-04 2021-06-04
US63/196,896 2021-06-04
PCT/US2022/032128 WO2022256631A2 (en) 2021-06-04 2022-06-03 Methods for the treatment of nucleotide repeat expansion disorders associated with msh3 activity

Publications (2)

Publication Number Publication Date
JP2024522147A JP2024522147A (ja) 2024-06-11
JP2024522147A5 true JP2024522147A5 (https=) 2025-06-11

Family

ID=84323606

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023574553A Pending JP2024522147A (ja) 2021-06-04 2022-06-03 Ｍｓｈ３活性と関連するヌクレオチドリピート伸長障害の治療方法

Country Status (4)

Country Link
US (1) US20240263179A1 (https=)
EP (1) EP4347837A4 (https=)
JP (1) JP2024522147A (https=)
WO (1) WO2022256631A2 (https=)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP7714162B6 (ja) * 2018-12-03 2025-09-08 タケダ ファーマシューティカルズ ユーエスエー インコーポレイテッド Ｍｓｈ３活性に関連するトリヌクレオチドリピート伸長障害の処置のための方法
AR122534A1 (es) 2020-06-03 2022-09-21 Triplet Therapeutics Inc Métodos para el tratamiento de los trastornos de expansión por repetición de nucleótidos asociados con la actividad de msh3

Family Cites Families (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EA201492116A1 (ru) * 2012-05-16 2015-05-29 Рана Терапьютикс, Инк. Композиции и способы для модулирования экспрессии mecp2
WO2016172795A1 (en) * 2015-04-27 2016-11-03 Adaerata Limited Partnership Modulating uracil-dna glycosylase and uses thereof
JOP20190197A1 (ar) * 2017-02-24 2019-08-22 Bayer Pharma AG مثبط كيناز ايه تي آر للاستخدام في طريقة لعلاج مرض فرط التكاثر
JP7714162B6 (ja) * 2018-12-03 2025-09-08 タケダ ファーマシューティカルズ ユーエスエー インコーポレイテッド Ｍｓｈ３活性に関連するトリヌクレオチドリピート伸長障害の処置のための方法

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