JP2022515140A5 - - Google Patents

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Publication number
JP2022515140A5
JP2022515140A5 JP2021535612A JP2021535612A JP2022515140A5 JP 2022515140 A5 JP2022515140 A5 JP 2022515140A5 JP 2021535612 A JP2021535612 A JP 2021535612A JP 2021535612 A JP2021535612 A JP 2021535612A JP 2022515140 A5 JP2022515140 A5 JP 2022515140A5
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JP
Japan
Application number
JP2021535612A
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Japanese (ja)
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JP7561129B2 (ja
JP2022515140A (ja
JPWO2020132558A5 (https=
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Priority claimed from PCT/US2019/068040 external-priority patent/WO2020132558A1/en
Publication of JP2022515140A publication Critical patent/JP2022515140A/ja
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Publication of JPWO2020132558A5 publication Critical patent/JPWO2020132558A5/ja
Priority to JP2024163353A priority Critical patent/JP2025000717A/ja
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JP2021535612A 2018-12-21 2019-12-20 Pmp22の発現を低減するための化合物及び方法 Active JP7561129B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024163353A JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862783997P 2018-12-21 2018-12-21
US62/783,997 2018-12-21
PCT/US2019/068040 WO2020132558A1 (en) 2018-12-21 2019-12-20 Compounds and methods for reducing pmp22 expression

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024163353A Division JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Publications (4)

Publication Number Publication Date
JP2022515140A JP2022515140A (ja) 2022-02-17
JP2022515140A5 true JP2022515140A5 (https=) 2022-12-14
JPWO2020132558A5 JPWO2020132558A5 (https=) 2022-12-14
JP7561129B2 JP7561129B2 (ja) 2024-10-03

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ID=71101859

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021535612A Active JP7561129B2 (ja) 2018-12-21 2019-12-20 Pmp22の発現を低減するための化合物及び方法
JP2024163353A Pending JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

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JP2024163353A Pending JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Country Status (4)

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US (1) US20220112503A1 (https=)
EP (1) EP3897837A4 (https=)
JP (2) JP7561129B2 (https=)
WO (1) WO2020132558A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EA202091693A1 (ru) 2018-01-12 2021-04-14 Бристол-Маерс Сквибб Компани Антисмысловые олигонуклеотиды, целенаправленно воздействующие на альфа-синуклеин, и их применения
BR112020013994A2 (pt) 2018-01-12 2020-12-08 Bristol-Myers Squibb Company Oligonucleotídeos antissenso que direcionam alfa-sinucleína e seus usos
EP4168549A4 (en) * 2020-06-19 2024-10-09 Ionis Pharmaceuticals, Inc. COMPOUNDS AND METHODS FOR PMP22 MODULATION
AU2021390471A1 (en) * 2020-12-01 2023-06-29 Research Institute At Nationwide Children's Hospital Products and methods for inhibition of expression of peripheral myelin protein-22

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20030198983A1 (en) * 2002-02-01 2003-10-23 Affymetrix, Inc. Methods of genetic analysis of human genes
EP1646874B1 (en) * 2003-07-11 2010-03-03 ZEILLINGER, Robert A method for predicting the metastatic potential of breast cancer
WO2012177639A2 (en) * 2011-06-22 2012-12-27 Alnylam Pharmaceuticals, Inc. Bioprocessing and bioproduction using avian cell lines
PT3277815T (pt) * 2015-04-03 2021-11-11 Beth Israel Deaconess Medical Ct Inc Compostos de oligonucleótidos para o tratamento de pré-eclâmpsia e outros distúrbios angiogénicos
JP7054675B2 (ja) * 2015-12-14 2022-04-14 コールド スプリング ハーバー ラボラトリー 網膜色素変性症18と網膜色素変性症13の処置のための組成物と方法
AU2017229778A1 (en) * 2016-03-09 2018-08-16 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting PMP22 expression
KR101889072B1 (ko) * 2017-09-15 2018-08-16 한국생명공학연구원 디지털 PCR을 이용한 유전성 강직성 대마비(Hereditary spastic paraplegia, HSP) 관련 유전자 SPG4의 거대결손 검증법

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