JP2022515140A5 - - Google Patents

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Publication number
JP2022515140A5
JP2022515140A5 JP2021535612A JP2021535612A JP2022515140A5 JP 2022515140 A5 JP2022515140 A5 JP 2022515140A5 JP 2021535612 A JP2021535612 A JP 2021535612A JP 2021535612 A JP2021535612 A JP 2021535612A JP 2022515140 A5 JP2022515140 A5 JP 2022515140A5
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JP
Japan
Prior art keywords
modified
modified oligonucleotide
compound according
nucleosides
nucleic acid
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2021535612A
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English (en)
Japanese (ja)
Other versions
JP7561129B2 (ja
JP2022515140A (ja
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Priority claimed from PCT/US2019/068040 external-priority patent/WO2020132558A1/en
Publication of JP2022515140A publication Critical patent/JP2022515140A/ja
Publication of JP2022515140A5 publication Critical patent/JP2022515140A5/ja
Priority to JP2024163353A priority Critical patent/JP2025000717A/ja
Application granted granted Critical
Publication of JP7561129B2 publication Critical patent/JP7561129B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2021535612A 2018-12-21 2019-12-20 Pmp22の発現を低減するための化合物及び方法 Active JP7561129B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024163353A JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862783997P 2018-12-21 2018-12-21
US62/783,997 2018-12-21
PCT/US2019/068040 WO2020132558A1 (en) 2018-12-21 2019-12-20 Compounds and methods for reducing pmp22 expression

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2024163353A Division JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Publications (3)

Publication Number Publication Date
JP2022515140A JP2022515140A (ja) 2022-02-17
JP2022515140A5 true JP2022515140A5 (https=) 2022-12-14
JP7561129B2 JP7561129B2 (ja) 2024-10-03

Family

ID=71101859

Family Applications (2)

Application Number Title Priority Date Filing Date
JP2021535612A Active JP7561129B2 (ja) 2018-12-21 2019-12-20 Pmp22の発現を低減するための化合物及び方法
JP2024163353A Pending JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Family Applications After (1)

Application Number Title Priority Date Filing Date
JP2024163353A Pending JP2025000717A (ja) 2018-12-21 2024-09-20 Pmp22の発現を低減するための化合物及び方法

Country Status (4)

Country Link
US (1) US20220112503A1 (https=)
EP (1) EP3897837A4 (https=)
JP (2) JP7561129B2 (https=)
WO (1) WO2020132558A1 (https=)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SG11202006528XA (en) 2018-01-12 2020-08-28 Bristol Myers Squibb Co Antisense oligonucleotides targeting alpha-synuclein and uses thereof
CN120310791A (zh) 2018-01-12 2025-07-15 百时美施贵宝公司 靶向α-突触核蛋白的反义寡核苷酸及其用途
EP4168549A4 (en) * 2020-06-19 2024-10-09 Ionis Pharmaceuticals, Inc. COMPOUNDS AND METHODS FOR PMP22 MODULATION
US20240318172A1 (en) * 2020-12-01 2024-09-26 Research Institute At Nationwide Children's Hospital Products and methods for inhibition of expression of peripheral myelin protein-22

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20030198983A1 (en) * 2002-02-01 2003-10-23 Affymetrix, Inc. Methods of genetic analysis of human genes
ATE459886T1 (de) * 2003-07-11 2010-03-15 Robert Zeillinger Verfahren zur vorhersage der metastasefähigkeit von mammakarzinom
WO2012177639A2 (en) * 2011-06-22 2012-12-27 Alnylam Pharmaceuticals, Inc. Bioprocessing and bioproduction using avian cell lines
RS62672B1 (sr) * 2015-04-03 2021-12-31 Univ Massachusetts Oligonukleotidna jedinjenja za tretman preeklampsije i drugih angiogenskih poremećaja
ES2903394T3 (es) * 2015-12-14 2022-04-01 Cold Spring Harbor Laboratory Composiciones para el tratamiento de la retinitis pigmentosa 13
WO2017156242A1 (en) * 2016-03-09 2017-09-14 Ionis Pharmaceuticals, Inc. Methods and compositions for inhibiting pmp22 expression
KR101889072B1 (ko) * 2017-09-15 2018-08-16 한국생명공학연구원 디지털 PCR을 이용한 유전성 강직성 대마비(Hereditary spastic paraplegia, HSP) 관련 유전자 SPG4의 거대결손 검증법

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