JP2022527105A5 - - Google Patents

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JP2022527105A5
JP2022527105A5 JP2021557917A JP2021557917A JP2022527105A5 JP 2022527105 A5 JP2022527105 A5 JP 2022527105A5 JP 2021557917 A JP2021557917 A JP 2021557917A JP 2021557917 A JP2021557917 A JP 2021557917A JP 2022527105 A5 JP2022527105 A5 JP 2022527105A5
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US201962826521P 2019-03-29 2019-03-29
US62/826,521 2019-03-29
US201962877765P 2019-07-23 2019-07-23
US62/877,765 2019-07-23
PCT/US2020/025110 WO2020205463A1 (en) 2019-03-29 2020-03-27 Compounds and methods for modulating ube3a-ats

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JP2022527105A JP2022527105A (ja) 2022-05-30
JP2022527105A5 true JP2022527105A5 (https=) 2023-04-04
JPWO2020205463A5 JPWO2020205463A5 (https=) 2023-04-04
JP7550165B2 JP7550165B2 (ja) 2024-09-12

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CA (1) CA3135180A1 (https=)
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CO (1) CO2021012796A2 (https=)
CR (1) CR20210538A (https=)
DK (1) DK3947684T3 (https=)
ES (1) ES3025960T3 (https=)
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HR (1) HRP20250596T1 (https=)
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PE (1) PE20220284A1 (https=)
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ES2809199T3 (es) 2012-06-25 2021-03-03 Ionis Pharmaceuticals Inc Modulación de la expresión de UBE3A-ATS
HUE067905T2 (hu) 2015-11-12 2024-11-28 Hoffmann La Roche Oligonukleotidok paternális UBE3A expresszió indukálására
FI3947684T3 (fi) 2019-03-29 2025-05-27 Ionis Pharmaceuticals Inc Yhdisteitä ja menetelmiä ube3a-ats:n moduloimiseksi
CA3211396A1 (en) * 2021-02-17 2022-08-25 Q-State Biosciences, Inc. Ube3a antisense therapeutics
KR20250068540A (ko) * 2023-11-08 2025-05-16 한국과학기술원 Ube3a를 표적으로 하여 발현증강을 유도하는 안티센스 올리고뉴클레오티드 및 이의 용도
WO2025101991A1 (en) * 2023-11-09 2025-05-15 Ionis Pharmaceuticals, Inc. Methods for modulating ube3a-ats
US20250353873A1 (en) * 2024-05-17 2025-11-20 Ionis Pharmaceuticals, Inc. Compounds and methods for modulating apoe expression

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