JP2024534157A5 - - Google Patents

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Publication number
JP2024534157A5
JP2024534157A5 JP2024513011A JP2024513011A JP2024534157A5 JP 2024534157 A5 JP2024534157 A5 JP 2024534157A5 JP 2024513011 A JP2024513011 A JP 2024513011A JP 2024513011 A JP2024513011 A JP 2024513011A JP 2024534157 A5 JP2024534157 A5 JP 2024534157A5
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JP
Japan
Application number
JP2024513011A
Other languages
Japanese (ja)
Other versions
JPWO2023028575A5 (https=
JP2024534157A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/075493 external-priority patent/WO2023028575A2/en
Publication of JP2024534157A publication Critical patent/JP2024534157A/ja
Publication of JPWO2023028575A5 publication Critical patent/JPWO2023028575A5/ja
Publication of JP2024534157A5 publication Critical patent/JP2024534157A5/ja
Pending legal-status Critical Current

Links

JP2024513011A 2021-08-27 2022-08-26 Scn1a発現を調節するための化合物及び方法 Pending JP2024534157A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163237898P 2021-08-27 2021-08-27
US63/237,898 2021-08-27
PCT/US2022/075493 WO2023028575A2 (en) 2021-08-27 2022-08-26 Compounds and methods for modulating scn1a expression

Publications (3)

Publication Number Publication Date
JP2024534157A JP2024534157A (ja) 2024-09-18
JPWO2023028575A5 JPWO2023028575A5 (https=) 2025-09-02
JP2024534157A5 true JP2024534157A5 (https=) 2025-09-02

Family

ID=85322277

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024513011A Pending JP2024534157A (ja) 2021-08-27 2022-08-26 Scn1a発現を調節するための化合物及び方法

Country Status (10)

Country Link
US (1) US20240360449A1 (https=)
EP (1) EP4392562A4 (https=)
JP (1) JP2024534157A (https=)
KR (1) KR20240049349A (https=)
CN (1) CN118451183A (https=)
AU (1) AU2022334739A1 (https=)
CA (1) CA3230299A1 (https=)
IL (1) IL310811A (https=)
MX (1) MX2024002553A (https=)
WO (1) WO2023028575A2 (https=)

Families Citing this family (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
KR20210134003A (ko) 2019-02-27 2021-11-08 스톡 테라퓨틱스, 인크. 병태 및 질환의 치료를 위한 안티센스 올리고머
BR112022022889A2 (pt) 2020-05-11 2023-04-04 Stoke Therapeutics Inc Oligômeros antissentido de opa1 para tratamento de condições e doenças
CN116334086A (zh) * 2023-03-29 2023-06-27 广州医科大学附属第二医院 一种用于修复或抑制SCN1A基因异常剪接的U1-snRNA及其用途
WO2025024568A1 (en) * 2023-07-24 2025-01-30 Stoke Therapeutics, Inc. Methods for treating conditions and diseases
WO2026052819A1 (en) * 2024-09-06 2026-03-12 Ospedale San Raffaele S.R.L. Gene therapy

Family Cites Families (5)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
SG11202001590RA (en) * 2017-08-25 2020-03-30 Stoke Therapeutics Inc Antisense oligomers for treatment of conditions and diseases
US20220372489A1 (en) * 2019-06-21 2022-11-24 Quralis Corporation Ppm1a inhibitors and methods of using same
EP4013767A4 (en) * 2019-08-15 2023-10-25 Ionis Pharmaceuticals, Inc. Linkage modified oligomeric compounds and uses thereof
BR112022010882A2 (pt) * 2019-12-06 2022-10-04 Stoke Therapeutics Inc Oligômeros antissenso para tratamento de condições e doenças
WO2021174036A1 (en) * 2020-02-28 2021-09-02 Ionis Pharmaceuticals, Inc. Compounds and methods for modulating scn1a expression

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