JP2023536994A5 - - Google Patents

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JP2023536994A5
JP2023536994A5 JP2023507945A JP2023507945A JP2023536994A5 JP 2023536994 A5 JP2023536994 A5 JP 2023536994A5 JP 2023507945 A JP2023507945 A JP 2023507945A JP 2023507945 A JP2023507945 A JP 2023507945A JP 2023536994 A5 JP2023536994 A5 JP 2023536994A5
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JP2023507945A 2020-08-07 2021-08-06 Ｓｃｎ２ａを調節する化合物および方法 Active JP7834712B2 (ja)

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US202063063120P 2020-08-07 2020-08-07
US63/063,120 2020-08-07
PCT/US2021/044887 WO2022032060A2 (en) 2020-08-07 2021-08-06 Compounds and methods for modulating scn2a

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JPWO2022032060A5 JPWO2022032060A5 (https=) 2024-08-15
JP2023536994A5 true JP2023536994A5 (https=) 2024-08-15
JP7834712B2 JP7834712B2 (ja) 2026-03-24

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US (3) US20240026353A1 (https=)
EP (1) EP4192476A4 (https=)
JP (1) JP7834712B2 (https=)
KR (1) KR20230048052A (https=)
CN (1) CN116322707B (https=)
AU (1) AU2021320384A1 (https=)
BR (1) BR112023002034A2 (https=)
CA (1) CA3186935A1 (https=)
CL (2) CL2023000393A1 (https=)
CO (1) CO2023002128A2 (https=)
EC (1) ECSP23008455A (https=)
IL (1) IL300258A (https=)
MX (1) MX2023001486A (https=)
PE (1) PE20231567A1 (https=)
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Publication number Priority date Publication date Assignee Title
IL300258A (en) 2020-08-07 2023-03-01 Ionis Pharmaceuticals Inc Compounds and methods for modulating SCN2A
US20240002852A1 (en) * 2020-10-01 2024-01-04 Ionis Pharmaceuticals, Inc. Compounds for modulating chmp7
CA3219942A1 (en) * 2021-05-10 2022-11-17 Q-State Biosciences, Inc. Compositions targeting sodium channel 1.6
AU2023244348A1 (en) * 2022-03-28 2024-10-10 Praxis Precision Medicines, Inc. Methods of using oligomeric compounds to treat scn2a-related disorders
AU2023348346A1 (en) * 2022-09-30 2025-03-27 Contera Pharma A/S Antisense oligonucleotides for the treatment of canavan disease
WO2025059511A1 (en) * 2023-09-15 2025-03-20 Praxis Precision Medicines, Inc. Elsunersen / prax-222 for use in the treatment of scn2a-related disorders

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