JP2023524065A5 - - Google Patents

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Publication number
JP2023524065A5
JP2023524065A5 JP2022566328A JP2022566328A JP2023524065A5 JP 2023524065 A5 JP2023524065 A5 JP 2023524065A5 JP 2022566328 A JP2022566328 A JP 2022566328A JP 2022566328 A JP2022566328 A JP 2022566328A JP 2023524065 A5 JP2023524065 A5 JP 2023524065A5
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pharmaceutical composition
group
modified oligonucleotides
tds
ceo
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JP2022566328A
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JP2023524065A (ja
JP7738573B2 (ja
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Priority claimed from PCT/US2021/030203 external-priority patent/WO2021222768A2/en
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Priority to JP2025145172A priority Critical patent/JP2026012176A/ja
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JP2022566328A 2020-05-01 2021-04-30 Atxn1を調節するための化合物及び方法 Active JP7738573B2 (ja)

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JP2025145172A JP2026012176A (ja) 2020-05-01 2025-09-02 Atxn1を調節するための化合物及び方法

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US202063019089P 2020-05-01 2020-05-01
US63/019,089 2020-05-01
PCT/US2021/030203 WO2021222768A2 (en) 2020-05-01 2021-04-30 Compounds and methods for modulating atxn1

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JP2023524065A JP2023524065A (ja) 2023-06-08
JP2023524065A5 true JP2023524065A5 (enExample) 2024-05-13
JP7738573B2 JP7738573B2 (ja) 2025-09-12

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JP2025145172A Pending JP2026012176A (ja) 2020-05-01 2025-09-02 Atxn1を調節するための化合物及び方法

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US (3) US11542504B2 (enExample)
EP (1) EP4143321A4 (enExample)
JP (2) JP7738573B2 (enExample)
KR (1) KR20230005933A (enExample)
CN (1) CN116096380B (enExample)
AU (1) AU2021264010A1 (enExample)
BR (1) BR112022021333A2 (enExample)
CA (1) CA3181546A1 (enExample)
IL (1) IL297435A (enExample)
MX (1) MX2022013707A (enExample)
TW (1) TWI901676B (enExample)
WO (1) WO2021222768A2 (enExample)

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* Cited by examiner, † Cited by third party
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TWI901676B (zh) 2020-05-01 2025-10-21 美商Ionis製藥公司 調節atxn1之化合物及方法
CN119410579B (zh) * 2024-12-02 2026-03-17 中国医学科学院输血研究所 一种培养nk细胞的方法及应用

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