JP2021529513A5 - - Google Patents

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Publication number
JP2021529513A5
JP2021529513A5 JP2020570046A JP2020570046A JP2021529513A5 JP 2021529513 A5 JP2021529513 A5 JP 2021529513A5 JP 2020570046 A JP2020570046 A JP 2020570046A JP 2020570046 A JP2020570046 A JP 2020570046A JP 2021529513 A5 JP2021529513 A5 JP 2021529513A5
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Japan
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sequence
vector genome
nucleotide sequence
seq
nucleotide
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JP2020570046A
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Japanese (ja)
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JP7565218B2 (ja
JP2021529513A (ja
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Priority claimed from PCT/US2019/040230 external-priority patent/WO2020010042A1/en
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JP2020570046A 2018-07-02 2019-07-02 筋萎縮性側索硬化症および脊髄に関連する障害の治療 Active JP7565218B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862693040P 2018-07-02 2018-07-02
US62/693,040 2018-07-02
US201862746104P 2018-10-16 2018-10-16
US62/746,104 2018-10-16
PCT/US2019/040230 WO2020010042A1 (en) 2018-07-02 2019-07-02 Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord

Publications (3)

Publication Number Publication Date
JP2021529513A JP2021529513A (ja) 2021-11-04
JP2021529513A5 true JP2021529513A5 (enExample) 2022-07-11
JP7565218B2 JP7565218B2 (ja) 2024-10-10

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JP2020570046A Active JP7565218B2 (ja) 2018-07-02 2019-07-02 筋萎縮性側索硬化症および脊髄に関連する障害の治療

Country Status (7)

Country Link
US (1) US20210254103A1 (enExample)
EP (1) EP3818161A1 (enExample)
JP (1) JP7565218B2 (enExample)
CN (1) CN112567035A (enExample)
AU (1) AU2019299861A1 (enExample)
CA (1) CA3103963A1 (enExample)
WO (1) WO2020010042A1 (enExample)

Families Citing this family (10)

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KR20240056729A (ko) 2016-05-18 2024-04-30 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
JP2020518258A (ja) 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドVoyager Therapeutics,Inc. 筋萎縮性側索硬化症(als)治療組成物および方法
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
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