CN112567035A - 肌萎缩侧索硬化症及脊髓相关病症的治疗 - Google Patents

肌萎缩侧索硬化症及脊髓相关病症的治疗 Download PDF

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CN112567035A
CN112567035A CN201980052747.2A CN201980052747A CN112567035A CN 112567035 A CN112567035 A CN 112567035A CN 201980052747 A CN201980052747 A CN 201980052747A CN 112567035 A CN112567035 A CN 112567035A
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aav
vhu
sequence
clv
nucleotides
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D·W-Y·沙
陈庆敏
J·卡罗尔索珀
H·帕泽克
侯金兆
S·M·赫尔施
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Voyager Therapeutics Inc
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CN201980052747.2A 2018-07-02 2019-07-02 肌萎缩侧索硬化症及脊髓相关病症的治疗 Pending CN112567035A (zh)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201862693040P 2018-07-02 2018-07-02
US62/693,040 2018-07-02
US201862746104P 2018-10-16 2018-10-16
US62/746,104 2018-10-16
PCT/US2019/040230 WO2020010042A1 (en) 2018-07-02 2019-07-02 Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord

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CN112567035A true CN112567035A (zh) 2021-03-26

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US (1) US20210254103A1 (enExample)
EP (1) EP3818161A1 (enExample)
JP (1) JP7565218B2 (enExample)
CN (1) CN112567035A (enExample)
AU (1) AU2019299861A1 (enExample)
CA (1) CA3103963A1 (enExample)
WO (1) WO2020010042A1 (enExample)

Cited By (1)

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WO2025045130A1 (zh) * 2023-08-29 2025-03-06 石药集团中奇制药技术（石家庄）有限公司 一种抑制sod1基因表达的dsrna分子及其应用

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WO2016077687A1 (en) 2014-11-14 2016-05-19 Voyager Therapeutics, Inc. Compositions and methods of treating amyotrophic lateral sclerosis (als)
KR20230145206A (ko) 2014-11-14 2023-10-17 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
KR20240056729A (ko) 2016-05-18 2024-04-30 보이저 테라퓨틱스, 인크. 조절성 폴리뉴클레오티드
JP2020518258A (ja) 2017-05-05 2020-06-25 ボイジャー セラピューティクス インコーポレイテッドＶｏｙａｇｅｒ Ｔｈｅｒａｐｅｕｔｉｃｓ，Ｉｎｃ． 筋萎縮性側索硬化症（ａｌｓ）治療組成物および方法
TW202413649A (zh) 2017-10-16 2024-04-01 美商航海家醫療公司 肌萎縮性脊髓側索硬化症(als)之治療
EP3697908A1 (en) 2017-10-16 2020-08-26 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis (als)
US20220168450A1 (en) * 2019-04-29 2022-06-02 Voyager Therapeutics, Inc. Treatment of amyotrophic lateral sclerosis and disorders associated with the spinal cord
EP4291654A2 (en) 2021-02-12 2023-12-20 Alnylam Pharmaceuticals, Inc. Superoxide dismutase 1 (sod1) irna compositions and methods of use thereof for treating or preventing superoxide dismutase 1- (sod1-) associated neurodegenerative diseases
WO2024226761A2 (en) 2023-04-26 2024-10-31 Voyager Therapeutics, Inc. Compositions and methods for treating amyotrophic lateral sclerosis

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