JP2020500162A5 - - Google Patents

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JP2020500162A5
JP2020500162A5 JP2019520884A JP2019520884A JP2020500162A5 JP 2020500162 A5 JP2020500162 A5 JP 2020500162A5 JP 2019520884 A JP2019520884 A JP 2019520884A JP 2019520884 A JP2019520884 A JP 2019520884A JP 2020500162 A5 JP2020500162 A5 JP 2020500162A5
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cell
transgene
gal
protein
composition
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JP7042263B2 (ja
JP2020500162A (ja
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JP2019520884A 2016-10-20 2017-10-19 ファブリー病の治療のための方法および組成物 Active JP7042263B2 (ja)

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JP2022039062A JP7418485B2 (ja) 2016-10-20 2022-03-14 ファブリー病の治療のための方法および組成物

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US201662410543P 2016-10-20 2016-10-20
US62/410,543 2016-10-20
US201762444093P 2017-01-09 2017-01-09
US62/444,093 2017-01-09
US201762458324P 2017-02-13 2017-02-13
US62/458,324 2017-02-13
US201762502058P 2017-05-05 2017-05-05
US62/502,058 2017-05-05
US201762516373P 2017-06-07 2017-06-07
US62/516,373 2017-06-07
US201762552792P 2017-08-31 2017-08-31
US62/552,792 2017-08-31
PCT/US2017/057328 WO2018075736A1 (en) 2016-10-20 2017-10-19 Methods and compositions for the treatment of fabry disease

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JP2020500162A5 true JP2020500162A5 (enExample) 2020-10-08
JP7042263B2 JP7042263B2 (ja) 2022-03-25

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US (2) US11219695B2 (enExample)
EP (2) EP3528852B1 (enExample)
JP (2) JP7042263B2 (enExample)
KR (1) KR102712926B1 (enExample)
CN (1) CN110022904B (enExample)
AU (1) AU2017345430B2 (enExample)
BR (1) BR112019007210A2 (enExample)
CA (1) CA3039673A1 (enExample)
ES (1) ES3047063T3 (enExample)
IL (1) IL266047B2 (enExample)
MX (1) MX2019004487A (enExample)
WO (1) WO2018075736A1 (enExample)

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EA202190999A1 (ru) 2018-10-10 2021-10-15 Амикус Терапьютикс, Инк. Композиции на основе полипептидов, стабилизированных с помощью дисульфидной связи, и способы применения
BR112021012249A2 (pt) * 2019-01-04 2021-09-08 Sangamo Therapeutics, Inc. Métodos e composições para o tratamento da doença de fabry

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