JP2020033360A5 - - Google Patents

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Publication number
JP2020033360A5
JP2020033360A5 JP2019186952A JP2019186952A JP2020033360A5 JP 2020033360 A5 JP2020033360 A5 JP 2020033360A5 JP 2019186952 A JP2019186952 A JP 2019186952A JP 2019186952 A JP2019186952 A JP 2019186952A JP 2020033360 A5 JP2020033360 A5 JP 2020033360A5
Authority
JP
Japan
Prior art keywords
deoxygalactonojirimycin
salt
gal
therapeutic agent
administered
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2019186952A
Other languages
English (en)
Japanese (ja)
Other versions
JP2020033360A (ja
Filing date
Publication date
Application filed filed Critical
Publication of JP2020033360A publication Critical patent/JP2020033360A/ja
Publication of JP2020033360A5 publication Critical patent/JP2020033360A5/ja
Priority to JP2021018456A priority Critical patent/JP2021098697A/ja
Pending legal-status Critical Current

Links

JP2019186952A 2011-03-11 2019-10-10 ファブリー病の治療用投薬レジメン Pending JP2020033360A (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2021018456A JP2021098697A (ja) 2011-03-11 2021-02-08 ファブリー病の治療用投薬レジメン

Applications Claiming Priority (6)

Application Number Priority Date Filing Date Title
US201161451798P 2011-03-11 2011-03-11
US61/451,798 2011-03-11
US201161578201P 2011-12-20 2011-12-20
US61/578,201 2011-12-20
US201261596165P 2012-02-07 2012-02-07
US61/596,165 2012-02-07

Related Parent Applications (1)

Application Number Title Priority Date Filing Date
JP2017038469A Division JP2017132780A (ja) 2011-03-11 2017-03-01 ファブリー病の治療用投薬レジメン

Related Child Applications (1)

Application Number Title Priority Date Filing Date
JP2021018456A Division JP2021098697A (ja) 2011-03-11 2021-02-08 ファブリー病の治療用投薬レジメン

Publications (2)

Publication Number Publication Date
JP2020033360A JP2020033360A (ja) 2020-03-05
JP2020033360A5 true JP2020033360A5 (enExample) 2020-04-23

Family

ID=46831259

Family Applications (6)

Application Number Title Priority Date Filing Date
JP2013557862A Pending JP2014528901A (ja) 2011-03-11 2012-03-08 ファブリー病の治療用投薬レジメン
JP2017038469A Pending JP2017132780A (ja) 2011-03-11 2017-03-01 ファブリー病の治療用投薬レジメン
JP2019186952A Pending JP2020033360A (ja) 2011-03-11 2019-10-10 ファブリー病の治療用投薬レジメン
JP2021018456A Withdrawn JP2021098697A (ja) 2011-03-11 2021-02-08 ファブリー病の治療用投薬レジメン
JP2023045001A Pending JP2023093448A (ja) 2011-03-11 2023-03-22 ファブリー病の治療用投薬レジメン
JP2025179237A Pending JP2026035578A (ja) 2011-03-11 2025-10-24 ファブリー病の治療用投薬レジメン

Family Applications Before (2)

Application Number Title Priority Date Filing Date
JP2013557862A Pending JP2014528901A (ja) 2011-03-11 2012-03-08 ファブリー病の治療用投薬レジメン
JP2017038469A Pending JP2017132780A (ja) 2011-03-11 2017-03-01 ファブリー病の治療用投薬レジメン

Family Applications After (3)

Application Number Title Priority Date Filing Date
JP2021018456A Withdrawn JP2021098697A (ja) 2011-03-11 2021-02-08 ファブリー病の治療用投薬レジメン
JP2023045001A Pending JP2023093448A (ja) 2011-03-11 2023-03-22 ファブリー病の治療用投薬レジメン
JP2025179237A Pending JP2026035578A (ja) 2011-03-11 2025-10-24 ファブリー病の治療用投薬レジメン

Country Status (16)

Country Link
US (4) US20140219986A1 (enExample)
EP (2) EP2683382B1 (enExample)
JP (6) JP2014528901A (enExample)
KR (1) KR20140011367A (enExample)
CN (2) CN107088225A (enExample)
AU (6) AU2012229330B2 (enExample)
CA (1) CA2829947C (enExample)
CL (1) CL2013002601A1 (enExample)
EA (1) EA031874B1 (enExample)
ES (1) ES2807502T3 (enExample)
HK (1) HK1242998A1 (enExample)
MX (1) MX2013010446A (enExample)
SG (2) SG10201604757RA (enExample)
TW (3) TWI624259B (enExample)
WO (1) WO2012125402A2 (enExample)
ZA (1) ZA201306735B (enExample)

Families Citing this family (30)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP2009537149A (ja) 2006-05-16 2009-10-29 アミークス セラピューティックス インコーポレイテッド ファブリー病に対する治療の選択を診断し、評価するためのアッセイ
WO2009102895A2 (en) 2008-02-12 2009-08-20 Amicus Therapeutics, Inc. Method to predict response to pharmacological chaperone treatment of diseases
UY34317A (es) 2011-09-12 2013-02-28 Genzyme Corp Anticuerpo antireceptor de célula T (alfa)/ß
US9790268B2 (en) 2012-09-12 2017-10-17 Genzyme Corporation Fc containing polypeptides with altered glycosylation and reduced effector function
RU2711935C2 (ru) 2013-03-11 2020-01-23 Джензим Корпорейшн Сайт-специфическая конъюгация антитело-лекарственное средство посредством гликоинженерии
EP3108002A1 (en) * 2014-02-17 2016-12-28 GlaxoSmithKline Intellectual Property Development Limited Microbiological process
PL3129067T3 (pl) 2014-03-19 2023-05-08 Genzyme Corporation Specyficzne dla miejsca glikomodyfikowanie ugrupowań celujących
US9675627B2 (en) * 2014-04-14 2017-06-13 Amicus Therapeutics, Inc. Dosing regimens for treating and/or preventing cerebral amyloidoses
GB201508025D0 (en) * 2015-05-11 2015-06-24 Ucl Business Plc Fabry disease gene therapy
CN108351862B (zh) 2015-08-11 2023-08-22 科格诺亚公司 利用人工智能和用户输入来确定发育进展的方法和装置
US11972336B2 (en) 2015-12-18 2024-04-30 Cognoa, Inc. Machine learning platform and system for data analysis
KR20190087673A (ko) * 2016-03-22 2019-07-24 아미쿠스 세라퓨틱스, 인코포레이티드 Gla 유전자에 g9331a 돌연변이를 갖는 환자에서 파브리 질병의 치료 방법
AU2017298376A1 (en) * 2016-07-19 2019-03-07 Amicus Therapeutics, Inc. Treatment of Fabry disease in ERT-naive and ERT-experienced patients
WO2018090009A1 (en) 2016-11-14 2018-05-17 Cognoa, Inc. Methods and apparatus for evaluating developmental conditions and providing control over coverage and reliability
WO2018148365A1 (en) * 2017-02-09 2018-08-16 Cognoa, Inc. Platform and system for digital personalized medicine
PT4324522T (pt) * 2017-05-30 2026-03-13 Amicus Therapeutics Inc Métodos de tratamento de pacientes com fabry tendo insuficiência renal
KR20220116305A (ko) 2017-05-30 2022-08-22 아미쿠스 세라퓨틱스, 인코포레이티드 신장 손상을 갖는 파브리 환자를 치료하는 방법
JP7066157B2 (ja) 2017-06-14 2022-05-13 学校法人 明治薬科大学 ファブリー病治療用医薬の組合せ物及びその利用
EP3749307B1 (en) 2018-02-06 2025-12-10 Amicus Therapeutics, Inc. Use of migalastat for treating fabry disease in pregnant patients
EP4289476A3 (en) * 2018-08-20 2024-02-21 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
AU2020248351B2 (en) 2019-03-22 2025-09-25 Cognoa, Inc. Personalized digital therapy methods and devices
MA55529A (fr) 2019-04-03 2022-02-09 Genzyme Corp Polypeptides de liaison anti-alpha bêta tcr à fragmentation réduite
BR112021024886A2 (pt) * 2019-06-11 2022-01-25 Amicus Therapeutics Inc Métodos de tratar a doença de fabry em pacientes com insuficiência renal
WO2021026447A1 (en) 2019-08-07 2021-02-11 Amicus Therapeutics, Inc. Methods of treating fabry disease in patients having a mutation in the gla gene
CA3153086A1 (en) 2019-09-06 2021-03-11 Cognoa, Inc. Methods, systems, and devices for the diagnosis of behavioral disorders, developmental delays, and neurologic impairments
US11623916B2 (en) 2020-12-16 2023-04-11 Amicus Therapeutics, Inc. Highly purified batches of pharmaceutical grade migalastat and methods of producing the same
US20240120050A1 (en) * 2022-10-07 2024-04-11 Insight Direct Usa, Inc. Machine learning method for predicting a health outcome of a patient using video and audio analytics
US20240197706A1 (en) * 2022-12-13 2024-06-20 Amicus Therapeutics, Inc. Methods of improving the pharmacokinetics of migalastat
TR2024011149A1 (tr) * 2024-08-23 2026-03-23 Sanovel İlaç Sanayi̇ Ve Ti̇caret Anoni̇m Şi̇rketi̇ Mi̇galastat i̇çeren kapsül formülasyonlari
TR2024011147A1 (tr) 2024-08-23 2026-03-23 Sanovel İlaç Sanayi̇ Ve Ti̇caret Anoni̇m Şi̇rketi̇ Mi̇galastat i̇çeren kapsül formülasyonu

Family Cites Families (9)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US4551177A (en) * 1984-04-23 1985-11-05 National Starch And Chemical Corporation Compressible starches as binders for tablets or capsules
US6274597B1 (en) * 1998-06-01 2001-08-14 Mount Sinai School Of Medicine Of New York University Method of enhancing lysosomal α-Galactosidase A
PT2857036T (pt) * 2003-01-31 2017-03-13 Mount Sinai School Of Medicine Of N Y Univ Terapia combinada para o tratamento de distúrbios de deficiência proteica
US7879354B2 (en) * 2004-01-13 2011-02-01 Mcneil-Ppc, Inc. Rapidly disintegrating gelatinous coated tablets
CN100457106C (zh) * 2005-06-15 2009-02-04 同济大学 1-脱氧野尻霉素在制备治疗糖尿病肾病药物中的应用
JP2009537149A (ja) * 2006-05-16 2009-10-29 アミークス セラピューティックス インコーポレイテッド ファブリー病に対する治療の選択を診断し、評価するためのアッセイ
MX2009010557A (es) * 2007-03-30 2009-11-19 Amicus Therapeutics Inc Metodo para el tratamiento de la enfermedad de fabry que utiliza chaperonas farmacologicas.
WO2008134628A2 (en) * 2007-04-26 2008-11-06 Amicus Therapeutics, Inc. Dosing regimens for the treatment of lysosomal storage diseases using pharmacological chaperones
US20100291060A1 (en) * 2007-08-29 2010-11-18 Shire Human Genetic Therapies, Inc Subcutaneous administration of alpha-galactosidase a

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