JP2019524890A5 - - Google Patents

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JP2019524890A5
JP2019524890A5 JP2019530369A JP2019530369A JP2019524890A5 JP 2019524890 A5 JP2019524890 A5 JP 2019524890A5 JP 2019530369 A JP2019530369 A JP 2019530369A JP 2019530369 A JP2019530369 A JP 2019530369A JP 2019524890 A5 JP2019524890 A5 JP 2019524890A5
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nucleic acid
raav
promoter
item
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JP2019530369A
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JP2019524890A (ja
JP7165410B2 (ja
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Priority claimed from PCT/US2017/047589 external-priority patent/WO2018035451A1/en
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JP2019530369A 2016-08-19 2017-08-18 組換え自己相補的アデノ随伴ウイルスを使用して疾患を治療するための方法及び組成物 Active JP7165410B2 (ja)

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JP2022111264A JP7653150B2 (ja) 2016-08-19 2022-07-11 組換え自己相補的アデノ随伴ウイルスを使用して疾患を治療するための方法及び組成物

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US201662377297P 2016-08-19 2016-08-19
US62/377,297 2016-08-19
PCT/US2017/047589 WO2018035451A1 (en) 2016-08-19 2017-08-18 Methods and compositions for treating conditions using recombinant self-complementary adeno-associated virus

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JP2022111264A Division JP7653150B2 (ja) 2016-08-19 2022-07-11 組換え自己相補的アデノ随伴ウイルスを使用して疾患を治療するための方法及び組成物

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JP2019524890A JP2019524890A (ja) 2019-09-05
JP2019524890A5 true JP2019524890A5 (enExample) 2020-12-24
JP7165410B2 JP7165410B2 (ja) 2022-11-04

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JP2019530369A Active JP7165410B2 (ja) 2016-08-19 2017-08-18 組換え自己相補的アデノ随伴ウイルスを使用して疾患を治療するための方法及び組成物
JP2022111264A Active JP7653150B2 (ja) 2016-08-19 2022-07-11 組換え自己相補的アデノ随伴ウイルスを使用して疾患を治療するための方法及び組成物

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US (2) US11207382B2 (enExample)
EP (1) EP3500278B1 (enExample)
JP (2) JP7165410B2 (enExample)
KR (2) KR20230130155A (enExample)
CN (1) CN109843306A (enExample)
AU (1) AU2017313844B2 (enExample)
CA (1) CA3073137A1 (enExample)
ES (1) ES2982489T3 (enExample)
WO (1) WO2018035451A1 (enExample)

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