JP2021512072A5 - - Google Patents

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Publication number
JP2021512072A5
JP2021512072A5 JP2020540722A JP2020540722A JP2021512072A5 JP 2021512072 A5 JP2021512072 A5 JP 2021512072A5 JP 2020540722 A JP2020540722 A JP 2020540722A JP 2020540722 A JP2020540722 A JP 2020540722A JP 2021512072 A5 JP2021512072 A5 JP 2021512072A5
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Japan
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muscle
composition
item
aav
sarcoglycan
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JP2020540722A
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English (en)
Japanese (ja)
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JP7361701B2 (ja
JP2021512072A (ja
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Priority claimed from PCT/US2019/015779 external-priority patent/WO2019152474A1/en
Publication of JP2021512072A publication Critical patent/JP2021512072A/ja
Publication of JP2021512072A5 publication Critical patent/JP2021512072A5/ja
Priority to JP2023171950A priority Critical patent/JP7752157B2/ja
Application granted granted Critical
Publication of JP7361701B2 publication Critical patent/JP7361701B2/ja
Priority to JP2025121245A priority patent/JP2025162557A/ja
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Anticipated expiration legal-status Critical

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JP2020540722A 2018-01-31 2019-01-30 肢帯型筋ジストロフィー2c型のための遺伝子治療 Active JP7361701B2 (ja)

Priority Applications (2)

Application Number Priority Date Filing Date Title
JP2023171950A JP7752157B2 (ja) 2018-01-31 2023-10-03 肢帯型筋ジストロフィー2c型のための遺伝子治療
JP2025121245A JP2025162557A (ja) 2018-01-31 2025-07-18 肢帯型筋ジストロフィー2c型のための遺伝子治療

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862624616P 2018-01-31 2018-01-31
US62/624,616 2018-01-31
PCT/US2019/015779 WO2019152474A1 (en) 2018-01-31 2019-01-30 Gene therapy for limb-girdle muscular dystrophy type 2c

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JP2023171950A Division JP7752157B2 (ja) 2018-01-31 2023-10-03 肢帯型筋ジストロフィー2c型のための遺伝子治療

Publications (3)

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JP2021512072A JP2021512072A (ja) 2021-05-13
JP2021512072A5 true JP2021512072A5 (enExample) 2022-02-07
JP7361701B2 JP7361701B2 (ja) 2023-10-16

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JP2020540722A Active JP7361701B2 (ja) 2018-01-31 2019-01-30 肢帯型筋ジストロフィー2c型のための遺伝子治療
JP2023171950A Active JP7752157B2 (ja) 2018-01-31 2023-10-03 肢帯型筋ジストロフィー2c型のための遺伝子治療
JP2025121245A Pending JP2025162557A (ja) 2018-01-31 2025-07-18 肢帯型筋ジストロフィー2c型のための遺伝子治療

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JP2023171950A Active JP7752157B2 (ja) 2018-01-31 2023-10-03 肢帯型筋ジストロフィー2c型のための遺伝子治療
JP2025121245A Pending JP2025162557A (ja) 2018-01-31 2025-07-18 肢帯型筋ジストロフィー2c型のための遺伝子治療

Country Status (19)

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US (2) US12263230B2 (enExample)
EP (1) EP3746100A4 (enExample)
JP (3) JP7361701B2 (enExample)
KR (2) KR20250099758A (enExample)
CN (2) CN119770682A (enExample)
AR (1) AR114350A1 (enExample)
AU (2) AU2019216257B2 (enExample)
BR (1) BR112020015173A2 (enExample)
CA (1) CA3089080A1 (enExample)
CL (2) CL2020001948A1 (enExample)
CO (1) CO2020010270A2 (enExample)
EA (1) EA202091739A1 (enExample)
IL (2) IL320714A (enExample)
MX (1) MX2020007876A (enExample)
MY (1) MY209273A (enExample)
SG (1) SG11202006722RA (enExample)
TW (1) TWI815856B (enExample)
WO (1) WO2019152474A1 (enExample)
ZA (1) ZA202004598B (enExample)

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