JP2017506898A5 - - Google Patents
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- JP2017506898A5 JP2017506898A5 JP2016553505A JP2016553505A JP2017506898A5 JP 2017506898 A5 JP2017506898 A5 JP 2017506898A5 JP 2016553505 A JP2016553505 A JP 2016553505A JP 2016553505 A JP2016553505 A JP 2016553505A JP 2017506898 A5 JP2017506898 A5 JP 2017506898A5
- Authority
- JP
- Japan
- Prior art keywords
- nucleases
- donor sequences
- composition
- target sequence
- item
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201461943865P | 2014-02-24 | 2014-02-24 | |
| US61/943,865 | 2014-02-24 | ||
| PCT/US2015/017302 WO2015127439A1 (en) | 2014-02-24 | 2015-02-24 | Methods and compositions for nuclease-mediated targeted integration |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019165181A Division JP6788082B2 (ja) | 2014-02-24 | 2019-09-11 | ヌクレアーゼ媒介性標的化組み込みのための方法および組成物 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2017506898A JP2017506898A (ja) | 2017-03-16 |
| JP2017506898A5 true JP2017506898A5 (enExample) | 2018-02-08 |
| JP6606088B2 JP6606088B2 (ja) | 2019-11-13 |
Family
ID=53879145
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2016553505A Expired - Fee Related JP6606088B2 (ja) | 2014-02-24 | 2015-02-24 | ヌクレアーゼ媒介性標的化組み込みのための方法および組成物 |
| JP2019165181A Expired - Fee Related JP6788082B2 (ja) | 2014-02-24 | 2019-09-11 | ヌクレアーゼ媒介性標的化組み込みのための方法および組成物 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2019165181A Expired - Fee Related JP6788082B2 (ja) | 2014-02-24 | 2019-09-11 | ヌクレアーゼ媒介性標的化組み込みのための方法および組成物 |
Country Status (6)
| Country | Link |
|---|---|
| US (3) | US10370680B2 (enExample) |
| EP (1) | EP3110454B1 (enExample) |
| JP (2) | JP6606088B2 (enExample) |
| AU (1) | AU2015218576B2 (enExample) |
| CA (1) | CA2939942A1 (enExample) |
| WO (1) | WO2015127439A1 (enExample) |
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| CA2788560A1 (en) * | 2010-02-08 | 2011-08-11 | Sangamo Biosciences, Inc. | Engineered cleavage half-domains |
| CA2788850C (en) | 2010-02-09 | 2019-06-25 | Sangamo Biosciences, Inc. | Targeted genomic modification with partially single-stranded donor molecules |
| US9290748B2 (en) * | 2010-02-26 | 2016-03-22 | Cellectis | Use of endonucleases for inserting transgenes into safe harbor loci |
| KR101880536B1 (ko) | 2010-04-26 | 2018-07-23 | 상가모 테라퓨틱스, 인코포레이티드 | 아연 핑거 뉴클레아제를 사용하는 로사 좌위의 게놈 편집 |
| US9057057B2 (en) * | 2010-07-27 | 2015-06-16 | The Johns Hopkins University | Obligate heterodimer variants of foki cleavage domain |
| JP6018069B2 (ja) | 2010-10-12 | 2016-11-02 | ザ・チルドレンズ・ホスピタル・オブ・フィラデルフィアＴｈｅ Ｃｈｉｌｄｒｅｎ’Ｓ Ｈｏｓｐｉｔａｌ Ｏｆ Ｐｈｉｌａｄｅｌｐｈｉａ | 血友病ｂを治療する方法及び組成物 |
| CA3186126A1 (en) * | 2011-09-21 | 2013-03-28 | Sangamo Biosciences, Inc. | Methods and compositions for regulation of transgene expression |
| JP6188703B2 (ja) | 2011-10-27 | 2017-08-30 | サンガモ セラピューティクス， インコーポレイテッド | Ｈｐｒｔ遺伝子座を修飾するための方法および組成物 |
| WO2013176772A1 (en) * | 2012-05-25 | 2013-11-28 | The Regents Of The University Of California | Methods and compositions for rna-directed target dna modification and for rna-directed modulation of transcription |
| AR091482A1 (es) * | 2012-06-21 | 2015-02-04 | Recombinetics Inc | Celulas modificadas geneticamente y metodos par su obtencion |
| RS60838B1 (sr) | 2012-08-29 | 2020-10-30 | Sangamo Therapeutics Inc | Postupci i kompozicije za tretman genskog stanja |
| US9255250B2 (en) | 2012-12-05 | 2016-02-09 | Sangamo Bioscience, Inc. | Isolated mouse or human cell having an exogenous transgene in an endogenous albumin gene |
| WO2014186585A2 (en) | 2013-05-15 | 2014-11-20 | Sangamo Biosciences, Inc. | Methods and compositions for treatment of a genetic condition |
| CA3194037A1 (en) * | 2013-10-17 | 2015-04-23 | Sangamo Biosciences, Inc. | Delivery methods and compositions for nuclease-mediated genome engineering |
| WO2015057976A1 (en) * | 2013-10-17 | 2015-04-23 | Sangamo Biosciences, Inc. | Delivery methods and compositions for nuclease-mediated genome engineering in hematopoietic stem cells |
| AU2014364051B2 (en) * | 2013-12-09 | 2018-12-20 | Sangamo Therapeutics, Inc. | Methods and compositions for treating hemophilia |
-
2015
- 2015-02-24 WO PCT/US2015/017302 patent/WO2015127439A1/en not_active Ceased
- 2015-02-24 AU AU2015218576A patent/AU2015218576B2/en not_active Ceased
- 2015-02-24 EP EP15752803.5A patent/EP3110454B1/en not_active Not-in-force
- 2015-02-24 US US14/630,128 patent/US10370680B2/en active Active
- 2015-02-24 JP JP2016553505A patent/JP6606088B2/ja not_active Expired - Fee Related
- 2015-02-24 CA CA2939942A patent/CA2939942A1/en active Pending
-
2019
- 2019-08-05 US US16/531,749 patent/US11591622B2/en active Active
- 2019-09-11 JP JP2019165181A patent/JP6788082B2/ja not_active Expired - Fee Related
-
2022
- 2022-12-20 US US18/085,420 patent/US20230203540A1/en not_active Abandoned
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