JP2007534637A5 - - Google Patents

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Publication number
JP2007534637A5
JP2007534637A5 JP2006539994A JP2006539994A JP2007534637A5 JP 2007534637 A5 JP2007534637 A5 JP 2007534637A5 JP 2006539994 A JP2006539994 A JP 2006539994A JP 2006539994 A JP2006539994 A JP 2006539994A JP 2007534637 A5 JP2007534637 A5 JP 2007534637A5
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JP
Japan
Prior art keywords
group
substituted
groups
chain alkyl
alkyl
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2006539994A
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English (en)
Japanese (ja)
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JP5184783B2 (ja
JP2007534637A (ja
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Application filed filed Critical
Priority claimed from PCT/US2004/038313 external-priority patent/WO2005049614A2/en
Publication of JP2007534637A publication Critical patent/JP2007534637A/ja
Publication of JP2007534637A5 publication Critical patent/JP2007534637A5/ja
Application granted granted Critical
Publication of JP5184783B2 publication Critical patent/JP5184783B2/ja
Anticipated expiration legal-status Critical
Expired - Lifetime legal-status Critical Current

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JP2006539994A 2003-11-17 2004-11-17 テトラヒドロビオプテリン、及びテトラヒドロビオプテリン類似体の製造方法 Expired - Lifetime JP5184783B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US52036803P 2003-11-17 2003-11-17
US52036703P 2003-11-17 2003-11-17
US60/520,367 2003-11-17
US60/520,368 2003-11-17
PCT/US2004/038313 WO2005049614A2 (en) 2003-11-17 2004-11-17 Processes for preparing tetrahydrobiopterin, and analogs of tetrahydrobiopterin

Publications (3)

Publication Number Publication Date
JP2007534637A JP2007534637A (ja) 2007-11-29
JP2007534637A5 true JP2007534637A5 (https=) 2008-01-17
JP5184783B2 JP5184783B2 (ja) 2013-04-17

Family

ID=34623128

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2006539994A Expired - Lifetime JP5184783B2 (ja) 2003-11-17 2004-11-17 テトラヒドロビオプテリン、及びテトラヒドロビオプテリン類似体の製造方法

Country Status (6)

Country Link
US (1) US7732599B2 (https=)
EP (1) EP1776364A2 (https=)
JP (1) JP5184783B2 (https=)
AU (1) AU2004290692A1 (https=)
CA (1) CA2545484A1 (https=)
WO (1) WO2005049614A2 (https=)

Families Citing this family (20)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
PL1708690T3 (pl) 2003-11-17 2017-01-31 Biomarin Pharmaceutical Inc. Leczenie fenyloketonurii za pomocą BH4
KR20070084270A (ko) 2004-11-17 2007-08-24 바이오마린 파머수티컬 인크. 안정한 정제 제형물
CA2675134A1 (en) * 2007-01-12 2008-07-24 Biomarin Pharmaceutical Inc. Pterin analogs
LT2545939T (lt) 2007-04-11 2021-03-10 Biomarin Pharmaceutical Inc. Tetrahidrobiopterinas, skirtas gydyti ligas, susijusias supadidėjusiu fenilalanino kiekiu
RU2470642C2 (ru) * 2008-01-03 2012-12-27 Байомарин Фармасьютикл Инк. Аналоги птерина для лечения состояния, чувствительного к вн4
BRPI0907247A2 (pt) 2008-01-07 2015-07-14 Biomarin Pharm Inc Métodos para preparar biopterina e para preparar tetraidrobiopterina
US9216178B2 (en) 2011-11-02 2015-12-22 Biomarin Pharmaceutical Inc. Dry blend formulation of tetrahydrobiopterin
CN102633799B (zh) * 2012-04-10 2014-06-25 凯莱英医药集团(天津)股份有限公司 一种从消旋体中间体拆分路线合成二盐酸沙丙蝶呤的方法
CN104736539B (zh) 2012-05-07 2017-09-01 白鸟制药株式会社 墨蝶呤和四氢乳酰蝶呤的制造法
WO2016189542A1 (en) 2015-05-28 2016-12-01 Natco Pharma Ltd Novel process for the preparation of sapropterin dihydrochloride and its key intermediate, l-biopterin
IL305149A (en) 2016-07-26 2023-10-01 Biomarin Pharm Inc Novel adeno-associated virus capsid proteins
MA46973A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Polymorphes de sépiaptérine et leurs sels
MA46972A (fr) 2016-11-29 2019-10-09 Censa Pharmaceuticals Inc Forme polymorphe de sépiaptérine
JP7811085B2 (ja) 2017-09-01 2026-02-04 ピーティーシー セラピューティクス エムピー,インコーポレイテッド セピアプテリンを含む医薬組成物及びその使用
TW202016314A (zh) 2018-05-09 2020-05-01 美商拜奧馬林製藥公司 治療苯丙酮尿症之方法
TW202005978A (zh) 2018-05-14 2020-02-01 美商拜奧馬林製藥公司 新穎肝靶向腺相關病毒載體
FI3801536T3 (fi) 2018-05-30 2024-08-29 Ptc Therapeutics Mp Inc Sepiapteriinin antaminen ilman ruokaa käytettäväksi menetelmässä sepiapteriinin plasma-altistuksen lisäämiseksi
EP3801534B1 (en) 2018-05-30 2026-02-18 PTC Therapeutics MP, Inc. Treatment of phenylketonuria with sepiapterin
TW202144575A (zh) 2020-04-03 2021-12-01 美商拜奧馬林製藥公司 使用aav及治療調配物之苯酮尿症治療
GB202307239D0 (en) 2023-05-15 2023-06-28 Evox Therapeutics Ltd Gene therapies for Phenylketonuria

Family Cites Families (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JPS617287A (ja) 1984-06-21 1986-01-13 Kanegafuchi Chem Ind Co Ltd 5‐デオキシ‐l‐アラビノースの製造法
JP2575781B2 (ja) * 1988-02-29 1997-01-29 日清製粉株式会社 2,3−ジアシルオキシ−4−ヒドロキシ−トペンタナールおよびその製造方法

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