ES2786039T3 - Vector génico - Google Patents
Vector génico Download PDFInfo
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- ES2786039T3 ES2786039T3 ES10723305T ES10723305T ES2786039T3 ES 2786039 T3 ES2786039 T3 ES 2786039T3 ES 10723305 T ES10723305 T ES 10723305T ES 10723305 T ES10723305 T ES 10723305T ES 2786039 T3 ES2786039 T3 ES 2786039T3
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| US9987309B2 (en) * | 2010-07-08 | 2018-06-05 | Duke University | Direct reprogramming of cells to cardiac myocyte fate |
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| FI3597749T3 (fi) | 2012-05-25 | 2023-10-09 | Univ California | Menetelmiä ja koostumuksia rna-ohjattua kohde-dna-modifikaatiota varten ja rna-ohjattua transkription modulaatiota varten |
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| PT3363902T (pt) | 2012-12-06 | 2019-12-19 | Sigma Aldrich Co Llc | Modificação e regulação de genoma baseadas em crispr |
| LT2956477T (lt) | 2013-02-15 | 2021-02-10 | Bioverativ Therapeutics Inc. | Optimizuotas faktoriaus viii genas |
| AU2014235794A1 (en) | 2013-03-14 | 2015-10-22 | Caribou Biosciences, Inc. | Compositions and methods of nucleic acid-targeting nucleic acids |
| JP6691048B2 (ja) | 2013-10-24 | 2020-04-28 | オスペダーレ サン ラファエレ エス．アール．エル | 方法 |
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| US10457940B2 (en) | 2016-09-22 | 2019-10-29 | University Of Massachusetts | AAV treatment of Huntington's disease |
| BR112019007982A2 (pt) * | 2016-10-18 | 2019-07-02 | Univ Oregon Health & Science | vetores de citomegalovírus elicitando células t restringidas por moléculas do complexo de histocompatibilidade e principal |
| CN106566838B (zh) * | 2016-11-14 | 2019-11-01 | 上海伯豪生物技术有限公司 | 一种基于CRISPR-Cas9技术的miR-126全长基因敲除试剂盒及其应用 |
| FI3612624T3 (fi) * | 2017-04-21 | 2024-12-04 | Ospedale San Raffaele Srl | Geeniterapia |
| IT201700086403A1 (it) * | 2017-07-27 | 2019-01-27 | Univ Del Piemonte Orientale | Endothelial-specific promoter sequences and uses thereof |
| JP7374883B2 (ja) | 2017-08-09 | 2023-11-07 | バイオベラティブ セラピューティクス インコーポレイテッド | 核酸分子およびその使用 |
| WO2019152692A1 (en) | 2018-02-01 | 2019-08-08 | Bioverativ Therapeutics, Inc. | Use of lentiviral vectors expressing factor viii |
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