DK3244931T3 - Fabry's disease gene therapy - Google Patents
Fabry's disease gene therapy Download PDFInfo
- Publication number
- DK3244931T3 DK3244931T3 DK16721916.1T DK16721916T DK3244931T3 DK 3244931 T3 DK3244931 T3 DK 3244931T3 DK 16721916 T DK16721916 T DK 16721916T DK 3244931 T3 DK3244931 T3 DK 3244931T3
- Authority
- DK
- Denmark
- Prior art keywords
- vector
- galactosidase
- nucleic acid
- sequence
- nucleotide sequence
- Prior art date
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- A01K2217/075—Animals genetically altered by homologous recombination inducing loss of function, i.e. knock out
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- C—CHEMISTRY; METALLURGY
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- C12N2750/00011—Details
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- C12Y302/00—Hydrolases acting on glycosyl compounds, i.e. glycosylases (3.2)
- C12Y302/01—Glycosidases, i.e. enzymes hydrolysing O- and S-glycosyl compounds (3.2.1)
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| PCT/GB2016/051328 WO2016181122A1 (en) | 2015-05-11 | 2016-05-10 | Fabry disease gene therapy |
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| US11103596B2 (en) | 2021-08-31 |
| WO2016181122A1 (en) | 2016-11-17 |
| JP6688812B2 (ja) | 2020-04-28 |
| TR201820102T4 (tr) | 2019-01-21 |
| US12370268B2 (en) | 2025-07-29 |
| KR20180012772A (ko) | 2018-02-06 |
| CN107980063B (zh) | 2021-12-10 |
| TW201706412A (zh) | 2017-02-16 |
| AU2016261453C1 (en) | 2019-09-12 |
| US20220016263A1 (en) | 2022-01-20 |
| EP3244931A1 (en) | 2017-11-22 |
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