CN104487579B - 使用aav衣壳变异体的高度有效的基因转移的组合物和方法 - Google Patents

使用aav衣壳变异体的高度有效的基因转移的组合物和方法 Download PDF

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CN104487579B
CN104487579B CN201380020980.5A CN201380020980A CN104487579B CN 104487579 B CN104487579 B CN 104487579B CN 201380020980 A CN201380020980 A CN 201380020980A CN 104487579 B CN104487579 B CN 104487579B
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aav
nucleic acid
vector
acid sequence
heterologous nucleic
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CN104487579A (zh
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穆斯塔法·N·雅思斯格鲁
费德里科·麦格兹
泽维尔·安谷拉
凯瑟琳·A·海
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Childrens Hospital of Philadelphia CHOP
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CN201380020980.5A 2012-04-18 2013-04-18 使用aav衣壳变异体的高度有效的基因转移的组合物和方法 Active CN104487579B (zh)

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US201261635273P 2012-04-18 2012-04-18
US61/635,273 2012-04-18
US201361794995P 2013-03-15 2013-03-15
US61/794,995 2013-03-15
PCT/US2013/037170 WO2013158879A1 (en) 2012-04-18 2013-04-18 Composition and methods for highly efficient gene transfer using aav capsid variants

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