CA3073137A1 - Methods and compositions for treating conditions using recombinant self-complementary adeno-associated virus - Google Patents
Methods and compositions for treating conditions using recombinant self-complementary adeno-associated virus Download PDFInfo
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- CA3073137A1 CA3073137A1 CA3073137A CA3073137A CA3073137A1 CA 3073137 A1 CA3073137 A1 CA 3073137A1 CA 3073137 A CA3073137 A CA 3073137A CA 3073137 A CA3073137 A CA 3073137A CA 3073137 A1 CA3073137 A1 CA 3073137A1
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| AU2017371043B2 (en) * | 2016-12-07 | 2022-12-15 | University Of Florida Research Foundation, Incorporated | IL-1Ra cDNAs |
| DK3740222T5 (da) | 2018-01-17 | 2024-08-26 | Meiragtx Uk Ltd | Modificeret RAAV-capsidprotein til genterapi |
| US12370240B2 (en) | 2018-11-28 | 2025-07-29 | Genascence Corporation | Methods and compositions for treating osteoarthritis |
| KR20210126096A (ko) | 2019-02-15 | 2021-10-19 | 상가모 테라퓨틱스, 인코포레이티드 | 재조합 aav를 제조하기 위한 조성물 및 방법 |
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| WO2021138559A1 (en) * | 2019-12-31 | 2021-07-08 | Swanbio Therapeutics Limited | Improved aav-abcd1 constructs and use for treatment or prevention of adrenoleukodystrophy (ald) and/or adrenomyeloneuropathy (amn) |
| WO2025049993A1 (en) | 2023-08-31 | 2025-03-06 | Dyno Therapeutics, Inc. | Capsid polypeptides and methods of use thereof |
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| WO2018035451A1 (en) | 2018-02-22 |
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| AU2017313844A1 (en) | 2019-04-11 |
| KR20190055086A (ko) | 2019-05-22 |
| AU2017313844B2 (en) | 2023-10-12 |
| JP2019524890A (ja) | 2019-09-05 |
| CN109843306A (zh) | 2019-06-04 |
| ES2982489T3 (es) | 2024-10-16 |
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