AU2019310459A1 - Systems and methods for producing gene therapy formulations - Google Patents
Systems and methods for producing gene therapy formulations Download PDFInfo
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- AU2019310459A1 AU2019310459A1 AU2019310459A AU2019310459A AU2019310459A1 AU 2019310459 A1 AU2019310459 A1 AU 2019310459A1 AU 2019310459 A AU2019310459 A AU 2019310459A AU 2019310459 A AU2019310459 A AU 2019310459A AU 2019310459 A1 AU2019310459 A1 AU 2019310459A1
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- A61P25/00—Drugs for disorders of the nervous system
- A61P25/14—Drugs for disorders of the nervous system for treating abnormal movements, e.g. chorea, dyskinesia
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
- C12N—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA
- C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
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- C12N15/79—Vectors or expression systems specially adapted for eukaryotic hosts
- C12N15/85—Vectors or expression systems specially adapted for eukaryotic hosts for animal cells
- C12N15/86—Viral vectors
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- C12N2310/14—Type of nucleic acid interfering nucleic acids [NA]
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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- C12N2750/00—MICROORGANISMS OR ENZYMES; COMPOSITIONS THEREOF; PROPAGATING, PRESERVING, OR MAINTAINING MICROORGANISMS; MUTATION OR GENETIC ENGINEERING; CULTURE MEDIA ssDNA viruses
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- C12N2750/14143—Use of virus, viral particle or viral elements as a vector viral genome or elements thereof as genetic vector
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| US201862702687P | 2018-07-24 | 2018-07-24 | |
| US62/702,679 | 2018-07-24 | ||
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| US201862725432P | 2018-08-31 | 2018-08-31 | |
| US62/725,432 | 2018-08-31 | ||
| US201862741508P | 2018-10-04 | 2018-10-04 | |
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| US201962794199P | 2019-01-18 | 2019-01-18 | |
| US201962794212P | 2019-01-18 | 2019-01-18 | |
| US201962794213P | 2019-01-18 | 2019-01-18 | |
| US62/794,212 | 2019-01-18 | ||
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| US62/794,199 | 2019-01-18 | ||
| US201962826363P | 2019-03-29 | 2019-03-29 | |
| US62/826,363 | 2019-03-29 | ||
| US201962839880P | 2019-04-29 | 2019-04-29 | |
| US62/839,880 | 2019-04-29 | ||
| PCT/US2019/043196 WO2020023612A1 (en) | 2018-07-24 | 2019-07-24 | Systems and methods for producing gene therapy formulations |
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