PL3448382T3 - Arimoklomol do leczenia zaburzeń powiązanych z glukocerebrozydazą - Google Patents

Arimoklomol do leczenia zaburzeń powiązanych z glukocerebrozydazą

Info

Publication number
PL3448382T3
PL3448382T3 PL17720480.7T PL17720480T PL3448382T3 PL 3448382 T3 PL3448382 T3 PL 3448382T3 PL 17720480 T PL17720480 T PL 17720480T PL 3448382 T3 PL3448382 T3 PL 3448382T3
Authority
PL
Poland
Prior art keywords
arimoclomol
glucocerebrosidase
treatment
related disorders
disorders
Prior art date
Application number
PL17720480.7T
Other languages
English (en)
Inventor
Anders Mørkeberg HINSBY
Thomas Kirkegaard Jensen
Cathrine Kolster Fog-Tønnesen
Nikolaj Havnsøe Torp Petersen
Claus Bornaes
Original Assignee
Zevra Denmark A/S
Priority date (The priority date is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the date listed.)
Filing date
Publication date
Application filed by Zevra Denmark A/S filed Critical Zevra Denmark A/S
Publication of PL3448382T3 publication Critical patent/PL3448382T3/pl

Links

Classifications

    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K31/00—Medicinal preparations containing organic active ingredients
    • A61K31/33—Heterocyclic compounds
    • A61K31/395—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins
    • A61K31/435—Heterocyclic compounds having nitrogen as a ring hetero atom, e.g. guanethidine or rifamycins having six-membered rings with one nitrogen as the only ring hetero atom
    • A61K31/44—Non condensed pyridines; Hydrogenated derivatives thereof
    • A61K31/445—Non condensed piperidines, e.g. piperocaine
    • A61K31/4523—Non condensed piperidines, e.g. piperocaine containing further heterocyclic ring systems
    • A61K31/4545—Non condensed piperidines, e.g. piperocaine containing further heterocyclic ring systems containing a six-membered ring with nitrogen as a ring hetero atom, e.g. pipamperone, anabasine
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K45/00—Medicinal preparations containing active ingredients not provided for in groups A61K31/00 - A61K41/00
    • A61K45/06—Mixtures of active ingredients without chemical characterisation, e.g. antiphlogistics and cardiaca
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00—Drugs for disorders of the nervous system
    • A61P25/14—Drugs for disorders of the nervous system for treating abnormal movements, e.g. chorea, dyskinesia
    • A61P25/16—Anti-Parkinson drugs
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P25/00—Drugs for disorders of the nervous system
    • A61P25/28—Drugs for disorders of the nervous system for treating neurodegenerative disorders of the central nervous system, e.g. nootropic agents, cognition enhancers, drugs for treating Alzheimer's disease or other forms of dementia
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P3/00—Drugs for disorders of the metabolism
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61P—SPECIFIC THERAPEUTIC ACTIVITY OF CHEMICAL COMPOUNDS OR MEDICINAL PREPARATIONS
    • A61P43/00—Drugs for specific purposes, not provided for in groups A61P1/00-A61P41/00
    • A—HUMAN NECESSITIES
    • A61—MEDICAL OR VETERINARY SCIENCE; HYGIENE
    • A61K—PREPARATIONS FOR MEDICAL, DENTAL OR TOILETRY PURPOSES
    • A61K2300/00—Mixtures or combinations of active ingredients, wherein at least one active ingredient is fully defined in groups A61K31/00 - A61K41/00

Landscapes

  • Health & Medical Sciences (AREA)
  • Life Sciences & Earth Sciences (AREA)
  • Animal Behavior & Ethology (AREA)
  • General Health & Medical Sciences (AREA)
  • Public Health (AREA)
  • Veterinary Medicine (AREA)
  • Chemical & Material Sciences (AREA)
  • Medicinal Chemistry (AREA)
  • Pharmacology & Pharmacy (AREA)
  • Bioinformatics & Cheminformatics (AREA)
  • Engineering & Computer Science (AREA)
  • Neurology (AREA)
  • Biomedical Technology (AREA)
  • Neurosurgery (AREA)
  • Chemical Kinetics & Catalysis (AREA)
  • General Chemical & Material Sciences (AREA)
  • Nuclear Medicine, Radiotherapy & Molecular Imaging (AREA)
  • Organic Chemistry (AREA)
  • Epidemiology (AREA)
  • Diabetes (AREA)
  • Hematology (AREA)
  • Obesity (AREA)
  • Hospice & Palliative Care (AREA)
  • Psychiatry (AREA)
  • Psychology (AREA)
  • Pharmaceuticals Containing Other Organic And Inorganic Compounds (AREA)
  • Acyclic And Carbocyclic Compounds In Medicinal Compositions (AREA)
PL17720480.7T 2016-04-29 2017-04-28 Arimoklomol do leczenia zaburzeń powiązanych z glukocerebrozydazą PL3448382T3 (pl)

Applications Claiming Priority (2)

Application Number Priority Date Filing Date Title
DKPA201670281 2016-04-29
PCT/EP2017/060205 WO2017186919A1 (en) 2016-04-29 2017-04-28 Arimoclomol for treating glucocerebrosidase associated disorders

Publications (1)

Publication Number Publication Date
PL3448382T3 true PL3448382T3 (pl) 2021-02-22

Family

ID=58645076

Family Applications (1)

Application Number Title Priority Date Filing Date
PL17720480.7T PL3448382T3 (pl) 2016-04-29 2017-04-28 Arimoklomol do leczenia zaburzeń powiązanych z glukocerebrozydazą

Country Status (22)

Country Link
US (4) US20190111041A1 (pl)
EP (2) EP3782624B1 (pl)
JP (2) JP6818045B2 (pl)
KR (2) KR102254140B1 (pl)
CN (2) CN121221602A (pl)
AU (2) AU2017255959B2 (pl)
BR (1) BR112018070653A2 (pl)
CA (2) CA3287846A1 (pl)
CY (1) CY1123717T1 (pl)
DK (2) DK3782624T3 (pl)
ES (1) ES2831764T3 (pl)
HR (1) HRP20210047T1 (pl)
HU (1) HUE052158T2 (pl)
IL (2) IL262411B (pl)
LT (1) LT3448382T (pl)
PL (1) PL3448382T3 (pl)
PT (2) PT3782624T (pl)
RS (1) RS61291B1 (pl)
RU (2) RU2021117465A (pl)
SI (1) SI3448382T1 (pl)
SM (1) SMT202100022T1 (pl)
WO (1) WO2017186919A1 (pl)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN103338784A (zh) * 2010-11-30 2013-10-02 奥菲泽米有限公司 用于增加Hsp70细胞内活性的方法
US20230226036A1 (en) * 2020-06-24 2023-07-20 Orphazyme A/S Arimoclomol for treating gaucher disease
WO2022106614A1 (en) 2020-11-19 2022-05-27 Orphazyme A/S Processes for preparing arimoclomol citrate and intermediates thereof
CN119487188A (zh) * 2022-04-19 2025-02-18 上海天泽云泰生物医药有限公司 用于治疗神经退行性障碍的重组aav载体

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