KR20180041120A - Cprispr/cas9-기반 치료 - Google Patents
Cprispr/cas9-기반 치료 Download PDFInfo
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- KR20180041120A KR20180041120A KR1020187002971A KR20187002971A KR20180041120A KR 20180041120 A KR20180041120 A KR 20180041120A KR 1020187002971 A KR1020187002971 A KR 1020187002971A KR 20187002971 A KR20187002971 A KR 20187002971A KR 20180041120 A KR20180041120 A KR 20180041120A
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- corneal dystrophy
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Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201562188013P | 2015-07-02 | 2015-07-02 | |
| US62/188,013 | 2015-07-02 | ||
| PCT/US2016/040962 WO2017004616A1 (en) | 2015-07-02 | 2016-07-05 | Crispr/cas9-based treatments |
Publications (1)
| Publication Number | Publication Date |
|---|---|
| KR20180041120A true KR20180041120A (ko) | 2018-04-23 |
Family
ID=57609222
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| KR1020187002971A Withdrawn KR20180041120A (ko) | 2015-07-02 | 2016-07-05 | Cprispr/cas9-기반 치료 |
Country Status (13)
| Country | Link |
|---|---|
| US (1) | US20200010854A1 (https=) |
| EP (1) | EP3317409A4 (https=) |
| JP (1) | JP2018520149A (https=) |
| KR (1) | KR20180041120A (https=) |
| CN (1) | CN108350446A (https=) |
| AU (1) | AU2016287836A1 (https=) |
| BR (1) | BR112017028201A2 (https=) |
| CA (1) | CA2989331A1 (https=) |
| CL (1) | CL2017003411A1 (https=) |
| EA (1) | EA201890203A1 (https=) |
| IL (1) | IL256279A (https=) |
| MX (1) | MX2017016921A (https=) |
| WO (1) | WO2017004616A1 (https=) |
Cited By (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20200044235A (ko) | 2018-10-18 | 2020-04-29 | 대한민국(산림청 국립산림과학원장) | CRISPR-Cas9 시스템을 이용한 유색고약버섯의 리그닌 분해효소의 유전자 편집방법 및 이의 용도 |
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| WO2019023680A1 (en) | 2017-07-28 | 2019-01-31 | President And Fellows Of Harvard College | METHODS AND COMPOSITIONS FOR EVOLUTION OF BASIC EDITORS USING PHAGE-ASSISTED CONTINUOUS EVOLUTION (PACE) |
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| WO2019118949A1 (en) | 2017-12-15 | 2019-06-20 | The Broad Institute, Inc. | Systems and methods for predicting repair outcomes in genetic engineering |
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| EP3797160A1 (en) | 2018-05-23 | 2021-03-31 | The Broad Institute Inc. | Base editors and uses thereof |
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| US12435330B2 (en) | 2019-10-10 | 2025-10-07 | The Broad Institute, Inc. | Methods and compositions for prime editing RNA |
| JP2022551970A (ja) * | 2019-10-16 | 2022-12-14 | ブラウン ユニバーシティ | 筋再生および筋成長 |
| DE112021002672T5 (de) | 2020-05-08 | 2023-04-13 | President And Fellows Of Harvard College | Vefahren und zusammensetzungen zum gleichzeitigen editieren beider stränge einer doppelsträngigen nukleotid-zielsequenz |
| CN111849991B (zh) * | 2020-08-05 | 2022-04-08 | 武汉纽福斯生物科技有限公司 | 一种寡核苷酸及其应用 |
| EP4430185A1 (en) * | 2021-11-09 | 2024-09-18 | Prime Medicine, Inc. | Genome editing compositions and methods for treatment of fuchs endothelial corneal dystrophy |
| WO2023092132A1 (en) * | 2021-11-22 | 2023-05-25 | Mammoth Biosciences, Inc. | Effector proteins and uses thereof |
| WO2024097900A1 (en) * | 2022-11-02 | 2024-05-10 | Emendobio Inc. | Compositions and methods for transcription factor 4 (tcf4) repeat expansion excision |
| CN116286823A (zh) * | 2023-04-04 | 2023-06-23 | 尧唐(上海)生物科技有限公司 | 靶向TGFBI基因的sgRNA、载体及其应用 |
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| DK2931898T3 (en) * | 2012-12-12 | 2016-06-20 | Massachusetts Inst Technology | CONSTRUCTION AND OPTIMIZATION OF SYSTEMS, PROCEDURES AND COMPOSITIONS FOR SEQUENCE MANIPULATION WITH FUNCTIONAL DOMAINS |
| WO2015048577A2 (en) * | 2013-09-27 | 2015-04-02 | Editas Medicine, Inc. | Crispr-related methods and compositions |
| AU2014361781B2 (en) * | 2013-12-12 | 2021-04-01 | Massachusetts Institute Of Technology | Delivery, use and therapeutic applications of the CRISPR -Cas systems and compositions for genome editing |
| MX2016007325A (es) * | 2013-12-12 | 2017-07-19 | Broad Inst Inc | Composiciones y metodos de uso de sistemas crispr-cas en desordenes debidos a repeticion de nucleotidos. |
| EP3445375A1 (en) * | 2016-04-22 | 2019-02-27 | Intellia Therapeutics, Inc. | Compositions and methods for treatment of diseases associated with trinucleotide repeats in transcription factor four |
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2016
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- 2016-07-05 BR BR112017028201A patent/BR112017028201A2/pt not_active Application Discontinuation
- 2016-07-05 WO PCT/US2016/040962 patent/WO2017004616A1/en not_active Ceased
- 2016-07-05 MX MX2017016921A patent/MX2017016921A/es unknown
- 2016-07-05 EA EA201890203A patent/EA201890203A1/ru unknown
- 2016-07-05 EP EP16818953.8A patent/EP3317409A4/en not_active Withdrawn
- 2016-07-05 AU AU2016287836A patent/AU2016287836A1/en not_active Abandoned
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Cited By (1)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20200044235A (ko) | 2018-10-18 | 2020-04-29 | 대한민국(산림청 국립산림과학원장) | CRISPR-Cas9 시스템을 이용한 유색고약버섯의 리그닌 분해효소의 유전자 편집방법 및 이의 용도 |
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| EA201890203A1 (ru) | 2018-07-31 |
| MX2017016921A (es) | 2018-04-10 |
| EP3317409A1 (en) | 2018-05-09 |
| CA2989331A1 (en) | 2017-01-05 |
| CN108350446A (zh) | 2018-07-31 |
| AU2016287836A1 (en) | 2018-02-15 |
| CL2017003411A1 (es) | 2018-08-17 |
| BR112017028201A2 (pt) | 2018-08-28 |
| IL256279A (en) | 2018-02-28 |
| US20200010854A1 (en) | 2020-01-09 |
| EP3317409A4 (en) | 2019-02-20 |
| WO2017004616A1 (en) | 2017-01-05 |
| JP2018520149A (ja) | 2018-07-26 |
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