JP2018520149A5 - - Google Patents

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Publication number
JP2018520149A5
JP2018520149A5 JP2017567629A JP2017567629A JP2018520149A5 JP 2018520149 A5 JP2018520149 A5 JP 2018520149A5 JP 2017567629 A JP2017567629 A JP 2017567629A JP 2017567629 A JP2017567629 A JP 2017567629A JP 2018520149 A5 JP2018520149 A5 JP 2018520149A5
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JP
Japan
Prior art keywords
combination
composition
corneal dystrophy
nuclease
dystrophy
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2017567629A
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English (en)
Japanese (ja)
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JP2018520149A (ja
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Publication date
Application filed filed Critical
Priority claimed from PCT/US2016/040962 external-priority patent/WO2017004616A1/en
Publication of JP2018520149A publication Critical patent/JP2018520149A/ja
Publication of JP2018520149A5 publication Critical patent/JP2018520149A5/ja
Pending legal-status Critical Current

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JP2017567629A 2015-07-02 2016-07-05 Ｃｒｉｓｐｒ／ｃａｓ９をベースとした治療 Pending JP2018520149A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201562188013P 2015-07-02 2015-07-02
US62/188,013 2015-07-02
PCT/US2016/040962 WO2017004616A1 (en) 2015-07-02 2016-07-05 Crispr/cas9-based treatments

Publications (2)

Publication Number Publication Date
JP2018520149A JP2018520149A (ja) 2018-07-26
JP2018520149A5 true JP2018520149A5 (https=) 2019-08-15

Family

ID=57609222

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2017567629A Pending JP2018520149A (ja) 2015-07-02 2016-07-05 Ｃｒｉｓｐｒ／ｃａｓ９をベースとした治療

Country Status (13)

Country Link
US (1) US20200010854A1 (https=)
EP (1) EP3317409A4 (https=)
JP (1) JP2018520149A (https=)
KR (1) KR20180041120A (https=)
CN (1) CN108350446A (https=)
AU (1) AU2016287836A1 (https=)
BR (1) BR112017028201A2 (https=)
CA (1) CA2989331A1 (https=)
CL (1) CL2017003411A1 (https=)
EA (1) EA201890203A1 (https=)
IL (1) IL256279A (https=)
MX (1) MX2017016921A (https=)
WO (1) WO2017004616A1 (https=)

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WO2018165541A1 (en) 2017-03-10 2018-09-13 The Board Of Regents Of The University Of Texas System Treatment of fuchs' endothelial corneal dystrophy
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WO2018225807A1 (ja) * 2017-06-07 2018-12-13 国立大学法人東京大学 顆粒状角膜変性症に対する遺伝子治療薬
CN111801345A (zh) 2017-07-28 2020-10-20 哈佛大学的校长及成员们 使用噬菌体辅助连续进化(pace)的进化碱基编辑器的方法和组合物
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KR20180134412A (ko) * 2016-04-22 2018-12-18 인텔리아 테라퓨틱스, 인크. 전사 인자 4에서 트라이뉴클레오타이드 반복부와 연관된 질환의 치료를 위한 조성물 및 방법

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