KR102700963B1 - 리소좀 장애를 위한 유전자 요법 - Google Patents

리소좀 장애를 위한 유전자 요법 Download PDF

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KR102700963B1
KR102700963B1 KR1020227002135A KR20227002135A KR102700963B1 KR 102700963 B1 KR102700963 B1 KR 102700963B1 KR 1020227002135 A KR1020227002135 A KR 1020227002135A KR 20227002135 A KR20227002135 A KR 20227002135A KR 102700963 B1 KR102700963 B1 KR 102700963B1
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nucleic acid
raav
sequence
vector
itr
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KR20220015499A (ko
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아사 아벨리오비치
로라 헤크만
허브 린
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프리베일 테라퓨틱스, 인크.
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KR1020227002135A 2017-10-03 2018-10-03 리소좀 장애를 위한 유전자 요법 Active KR102700963B1 (ko)

Applications Claiming Priority (12)

Application Number Priority Date Filing Date Title
US201762567311P 2017-10-03 2017-10-03
US201762567296P 2017-10-03 2017-10-03
US201762567310P 2017-10-03 2017-10-03
US201762567319P 2017-10-03 2017-10-03
US201762567301P 2017-10-03 2017-10-03
US62/567,310 2017-10-03
US62/567,301 2017-10-03
US62/567,319 2017-10-03
US62/567,296 2017-10-03
US62/567,311 2017-10-03
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