KR102655989B1 - 인간 디스트로핀 pre-mRNA의 엑손 51에 결합하는 안티센스 올리고뉴클레오티드 - Google Patents

인간 디스트로핀 pre-mRNA의 엑손 51에 결합하는 안티센스 올리고뉴클레오티드 Download PDF

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KR102655989B1
KR102655989B1 KR1020207005073A KR20207005073A KR102655989B1 KR 102655989 B1 KR102655989 B1 KR 102655989B1 KR 1020207005073 A KR1020207005073 A KR 1020207005073A KR 20207005073 A KR20207005073 A KR 20207005073A KR 102655989 B1 KR102655989 B1 KR 102655989B1
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antisense oligonucleotide
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artificial sequence
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morpholino antisense
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토시후미 요코타
유스케 에치고야
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더 거버너스 오브 더 유니버시티 오브 알버타
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    • C12N2320/33—Alteration of splicing

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KR1020207005073A 2017-07-21 2018-07-20 인간 디스트로핀 pre-mRNA의 엑손 51에 결합하는 안티센스 올리고뉴클레오티드 Active KR102655989B1 (ko)

Priority Applications (1)

Application Number Priority Date Filing Date Title
KR1020247011120A KR20240049639A (ko) 2017-07-21 2018-07-20 인간 디스트로핀 전-ｍＲＮＡ의 엑손 51에 결합하는 안티센스 올리고뉴클레오타이드

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
GB1711809.2 2017-07-21
GBGB1711809.2A GB201711809D0 (en) 2017-07-21 2017-07-21 Antisense oligonucleotide
PCT/CA2018/050881 WO2019014772A1 (en) 2017-07-21 2018-07-20 ANTISENSE OLIGONUCLEOTIDES THAT BIND EXON 51 OF HUMAN DYSTROPHIN PRE-MRNA

Related Child Applications (1)

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KR1020247011120A Division KR20240049639A (ko) 2017-07-21 2018-07-20 인간 디스트로핀 전-ｍＲＮＡ의 엑손 51에 결합하는 안티센스 올리고뉴클레오타이드

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KR20200041326A KR20200041326A (ko) 2020-04-21
KR102655989B1 true KR102655989B1 (ko) 2024-04-08

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KR1020207005073A Active KR102655989B1 (ko) 2017-07-21 2018-07-20 인간 디스트로핀 pre-mRNA의 엑손 51에 결합하는 안티센스 올리고뉴클레오티드
KR1020247011120A Pending KR20240049639A (ko) 2017-07-21 2018-07-20 인간 디스트로핀 전-ｍＲＮＡ의 엑손 51에 결합하는 안티센스 올리고뉴클레오타이드

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US (3) US11142767B2 (https=)
EP (1) EP3655535A4 (https=)
JP (3) JP7365336B2 (https=)
KR (2) KR102655989B1 (https=)
CN (2) CN117701566A (https=)
CA (1) CA3105864A1 (https=)
GB (1) GB201711809D0 (https=)
WO (1) WO2019014772A1 (https=)

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MX2019008199A (es) 2017-01-06 2019-11-25 Avidity Biosciences Llc Composiciones de acido nucleico polipeptido y metodos de induccion de la omision de exon.
GB201711809D0 (en) * 2017-07-21 2017-09-06 Governors Of The Univ Of Alberta Antisense oligonucleotide
WO2019241385A2 (en) * 2018-06-13 2019-12-19 Sarepta Therapeutics, Inc. Exon skipping oligomers for muscular dystropy
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US11168141B2 (en) 2018-08-02 2021-11-09 Dyne Therapeutics, Inc. Muscle targeting complexes and uses thereof for treating dystrophinopathies
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