JP7576754B2 - 幹細胞移植のための組成物および方法 - Google Patents

幹細胞移植のための組成物および方法 Download PDF

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JP7576754B2
JP7576754B2 JP2020555511A JP2020555511A JP7576754B2 JP 7576754 B2 JP7576754 B2 JP 7576754B2 JP 2020555511 A JP2020555511 A JP 2020555511A JP 2020555511 A JP2020555511 A JP 2020555511A JP 7576754 B2 JP7576754 B2 JP 7576754B2
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cells
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JP2021521180A (ja
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ブライアン ビアード
ナバーロ フリアン セビラ
ゴーラヴ シャー
キンナリー パテル
ラジ プラバカール
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スペースクラフト セブン リミテッド ライアビリティ カンパニー
フンダシオン パラ ラ インベスティガシオン バイオメディカ デル オスピタル インファンティル ウニベルシタリオ ニーニョ ヘスス
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    • A61K35/28—Bone marrow; Haematopoietic stem cells; Mesenchymal stem cells of any origin, e.g. adipose-derived stem cells
    • A—HUMAN NECESSITIES
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    • C12N15/00—Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor
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    • C12N5/00—Undifferentiated human, animal or plant cells, e.g. cell lines; Tissues; Cultivation or maintenance thereof; Culture media therefor
    • C12N5/06—Animal cells or tissues; Human cells or tissues
    • C12N5/0602—Vertebrate cells
    • C12N5/0634—Cells from the blood or the immune system
    • C12N5/0647—Haematopoietic stem cells; Uncommitted or multipotent progenitors
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    • C12—BIOCHEMISTRY; BEER; SPIRITS; WINE; VINEGAR; MICROBIOLOGY; ENZYMOLOGY; MUTATION OR GENETIC ENGINEERING
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    • C12N2310/00—Structure or type of the nucleic acid
    • C12N2310/10—Type of nucleic acid
    • C12N2310/20—Type of nucleic acid involving clustered regularly interspaced short palindromic repeats [CRISPR]
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    • C12N2800/00—Nucleic acids vectors
    • C12N2800/10—Plasmid DNA
    • C12N2800/106—Plasmid DNA for vertebrates
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    • C12N2800/00—Nucleic acids vectors
    • C12N2800/80—Vectors containing sites for inducing double-stranded breaks, e.g. meganuclease restriction sites

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  • Medicines Containing Material From Animals Or Micro-Organisms (AREA)
  • Medicines That Contain Protein Lipid Enzymes And Other Medicines (AREA)
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US201862656292P 2018-04-11 2018-04-11
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US (1) US12539316B2 (https=)
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KR (1) KR20210003738A (https=)
CN (1) CN112153973A (https=)
AU (2) AU2019252662A1 (https=)
BR (1) BR112020020841A2 (https=)
CA (1) CA3093708A1 (https=)
IL (2) IL307996A (https=)
MX (1) MX2020010718A (https=)
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EP3773636A1 (en) 2021-02-17
BR112020020841A2 (pt) 2021-01-19
KR20210003738A (ko) 2021-01-12
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SG11202008400SA (en) 2020-09-29
AU2026200325A1 (en) 2026-04-09
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