JP2023534647A5 - - Google Patents

Info

Publication number
JP2023534647A5
JP2023534647A5 JP2023501075A JP2023501075A JP2023534647A5 JP 2023534647 A5 JP2023534647 A5 JP 2023534647A5 JP 2023501075 A JP2023501075 A JP 2023501075A JP 2023501075 A JP2023501075 A JP 2023501075A JP 2023534647 A5 JP2023534647 A5 JP 2023534647A5
Authority
JP
Japan
Prior art keywords
seq
pharmaceutical composition
composition according
polypeptide
dworf
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023501075A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023534647A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/040428 external-priority patent/WO2022010834A1/en
Publication of JP2023534647A publication Critical patent/JP2023534647A/ja
Publication of JP2023534647A5 publication Critical patent/JP2023534647A5/ja
Pending legal-status Critical Current

Links

JP2023501075A 2020-07-07 2021-07-06 Dwarfオープンリーディングフレームのためのアデノ随伴ウイルスベクター Pending JP2023534647A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063048743P 2020-07-07 2020-07-07
US63/048,743 2020-07-07
PCT/US2021/040428 WO2022010834A1 (en) 2020-07-07 2021-07-06 Adeno-associated virus vector for dwarf open reading frame

Publications (2)

Publication Number Publication Date
JP2023534647A JP2023534647A (ja) 2023-08-10
JP2023534647A5 true JP2023534647A5 (enExample) 2024-07-10

Family

ID=79552029

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023501075A Pending JP2023534647A (ja) 2020-07-07 2021-07-06 Dwarfオープンリーディングフレームのためのアデノ随伴ウイルスベクター

Country Status (11)

Country Link
US (1) US20230241249A1 (enExample)
EP (1) EP4179083A4 (enExample)
JP (1) JP2023534647A (enExample)
KR (1) KR20230035584A (enExample)
CN (1) CN115885043A (enExample)
AU (1) AU2021306697A1 (enExample)
BR (1) BR112022026997A2 (enExample)
CA (1) CA3183844A1 (enExample)
IL (1) IL299638A (enExample)
MX (1) MX2023000318A (enExample)
WO (1) WO2022010834A1 (enExample)

Families Citing this family (2)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
EP4087489B1 (en) 2020-01-08 2025-05-14 Vitruvia Holdings Inc. Methods and computing system for processing ultrasound image to determine health of subdermal tissue
KR20240032971A (ko) 2021-07-08 2024-03-12 테나야 테라퓨틱스, 인코포레이티드 유전자 요법을 위한 최적화된 발현 카세트

Family Cites Families (10)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20030148968A1 (en) * 1995-02-28 2003-08-07 Hammond H. Kirk Techniques and compositions for treating cardiovascular disease by in vivo gene delivery
EP2345731B1 (en) * 2003-09-30 2015-10-21 The Trustees of the University of Pennsylvania Adeno-associated virus (AAV) clades, sequences, vectors containing same, and uses thereof
US10570183B2 (en) * 2016-04-19 2020-02-25 The Board Of Regents Of The University Of Texas System Use of a small native peptide activator of SERCA pump for treatment of heart failure and other disorders characterized by cytosolic calcium overload
WO2018026766A1 (en) * 2016-08-01 2018-02-08 The Board Of Supervisors Of Louisiana State University And Agricultural And Mechanical College Compositions and methods for treating cardiac injury
JP7332474B2 (ja) * 2017-02-24 2023-08-23 ザ ボード オブ リージェンツ オブ ザ ユニバーシティー オブ テキサス システム ミオミキサーにより促進される筋細胞融合に関連する組成物および方法
US20180326022A1 (en) * 2017-04-21 2018-11-15 The Trustees Of The University Of Pennsylvania Compositions and methods for improving heart function and treating heart failure
ES2976559T3 (es) * 2017-09-20 2024-08-05 Univ California Terapia génica con conexina 43 para restaurar la función eléctrica y cardíaca y la estructura cardíaca, en la miocardiopatía arritmogénica del ventrículo derecho
CA3112883A1 (en) * 2018-10-25 2020-04-30 Baxalta Incorporated Aav triple-plasmid system
EP3947700A4 (en) * 2019-04-01 2023-01-04 Tenaya Therapeutics, Inc. Adeno-associated virus with engineered capsid
US12552838B2 (en) * 2020-04-20 2026-02-17 Tenaya Therapeutics, Inc. Adeno-associated virus with engineered capsid

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