JP2024523707A5 - - Google Patents

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Publication number
JP2024523707A5
JP2024523707A5 JP2024500231A JP2024500231A JP2024523707A5 JP 2024523707 A5 JP2024523707 A5 JP 2024523707A5 JP 2024500231 A JP2024500231 A JP 2024500231A JP 2024500231 A JP2024500231 A JP 2024500231A JP 2024523707 A5 JP2024523707 A5 JP 2024523707A5
Authority
JP
Japan
Prior art keywords
expression cassette
seq
sequence
item
polynucleotide sequence
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024500231A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024523707A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/073574 external-priority patent/WO2023283649A1/en
Publication of JP2024523707A publication Critical patent/JP2024523707A/ja
Publication of JP2024523707A5 publication Critical patent/JP2024523707A5/ja
Pending legal-status Critical Current

Links

JP2024500231A 2021-07-08 2022-07-08 遺伝子治療のための最適化された発現カセット Pending JP2024523707A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163219651P 2021-07-08 2021-07-08
US63/219,651 2021-07-08
PCT/US2022/073574 WO2023283649A1 (en) 2021-07-08 2022-07-08 Optimized expression cassettes for gene therapy

Publications (2)

Publication Number Publication Date
JP2024523707A JP2024523707A (ja) 2024-06-28
JP2024523707A5 true JP2024523707A5 (enExample) 2025-07-16

Family

ID=83270905

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024500231A Pending JP2024523707A (ja) 2021-07-08 2022-07-08 遺伝子治療のための最適化された発現カセット

Country Status (12)

Country Link
US (2) US12151001B2 (enExample)
EP (1) EP4367251A1 (enExample)
JP (1) JP2024523707A (enExample)
KR (1) KR20240032971A (enExample)
AR (1) AR126407A1 (enExample)
AU (1) AU2022307365A1 (enExample)
CA (1) CA3224488A1 (enExample)
CO (1) CO2024001148A2 (enExample)
IL (1) IL309742A (enExample)
MX (1) MX2024000175A (enExample)
TW (1) TW202317768A (enExample)
WO (1) WO2023283649A1 (enExample)

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MX2024000175A (es) 2021-07-08 2024-03-05 Tenaya Therapeutics Inc Casetes de expresión optimizada para genoterapia.
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JP2026507523A (ja) * 2023-02-13 2026-03-04 アストラゼネカ アイルランド リミテッド 遺伝子療法のためのbcl2関連アタノゲン3(bag3)をコードする核酸
WO2024215653A1 (en) 2023-04-10 2024-10-17 Tenaya Therapeutics, Inc. Guide rnas, vectors, and virions for targeting mutations in the pln gene
WO2024215655A1 (en) 2023-04-10 2024-10-17 Tenaya Therapeutics, Inc. Cardioprotective bag3 therapies
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WO2025162449A1 (en) * 2024-01-30 2025-08-07 Inspirar Limited Compositions and methods for the treatment of heart disease
WO2025171086A1 (en) * 2024-02-07 2025-08-14 Asimov Inc. Promoters and uses thereof

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