JP2024546103A5 - - Google Patents
Info
- Publication number
- JP2024546103A5 JP2024546103A5 JP2024534162A JP2024534162A JP2024546103A5 JP 2024546103 A5 JP2024546103 A5 JP 2024546103A5 JP 2024534162 A JP2024534162 A JP 2024534162A JP 2024534162 A JP2024534162 A JP 2024534162A JP 2024546103 A5 JP2024546103 A5 JP 2024546103A5
- Authority
- JP
- Japan
- Prior art keywords
- vector
- approximately
- polynucleotide
- promoter
- jph2
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202163287393P | 2021-12-08 | 2021-12-08 | |
| US63/287,393 | 2021-12-08 | ||
| PCT/US2022/081122 WO2023108029A2 (en) | 2021-12-08 | 2022-12-07 | Junctophilin-2 (jph2) gene therapy using aav vector |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2024546103A JP2024546103A (ja) | 2024-12-17 |
| JP2024546103A5 true JP2024546103A5 (enExample) | 2025-10-29 |
Family
ID=86731395
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2024534162A Pending JP2024546103A (ja) | 2021-12-08 | 2022-12-07 | Ａａｖベクターを用いたジャンクトフィリン－２（ｊｐｈ２）遺伝子治療 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20240335565A1 (enExample) |
| EP (1) | EP4444892A4 (enExample) |
| JP (1) | JP2024546103A (enExample) |
| CN (1) | CN118660969A (enExample) |
| CA (1) | CA3240080A1 (enExample) |
| WO (1) | WO2023108029A2 (enExample) |
Families Citing this family (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102673203B1 (ko) | 2016-04-20 | 2024-06-10 | 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피. | Pklr의 유전자 발현 증강을 위한 조성물 및 방법 |
| AU2018352583B2 (en) | 2017-10-16 | 2025-04-17 | Centro de Investigaciones Energeticas, Medioambientales Y Tecnologicas, O.A., M.P. | Lentiviral vectors for delivery of PKLR to treat Pyruvate Kinase Deficiency |
| US12539316B2 (en) | 2018-04-11 | 2026-02-03 | Spacecraft Seven, Llc | Compositions and methods for stem cell transplant |
| IL280465B2 (en) | 2018-07-30 | 2025-03-01 | Centro De Investig Energeticas Medioambientales Y Tecnologicas O A M P | Methods for gene modification of hematopoietic cells |
| WO2025212838A1 (en) * | 2024-04-03 | 2025-10-09 | Research Institute At Nationwide Children's Hospital | Products and methods for treating diseases or disorders associated with dux4 overexpression |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20040043382A1 (en) * | 2001-03-08 | 2004-03-04 | Muralidhara Padigaru | Novel proteins and nucleic acids encoding same |
| EP2792742A1 (en) * | 2013-04-17 | 2014-10-22 | Universitätsklinikum Hamburg-Eppendorf (UKE) | Gene-therapy vectors for treating cardiomyopathy |
| WO2017214296A1 (en) * | 2016-06-07 | 2017-12-14 | University Of Iowa Research Foundation | Junctophilin-2 fragments and uses therefor |
| IL324506A (en) * | 2018-06-18 | 2026-01-01 | Res Inst Nationwide Childrens Hospital | Adeno-associated virus vector for delivery of muscle-specific microdystrophin for the treatment of muscular dystrophy |
| TW202317768A (zh) * | 2021-07-08 | 2023-05-01 | 美商特納亞治療股份有限公司 | 用於基因療法的優化表現卡匣 |
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2022
- 2022-12-07 CA CA3240080A patent/CA3240080A1/en active Pending
- 2022-12-07 WO PCT/US2022/081122 patent/WO2023108029A2/en not_active Ceased
- 2022-12-07 EP EP22905350.9A patent/EP4444892A4/en active Pending
- 2022-12-07 JP JP2024534162A patent/JP2024546103A/ja active Pending
- 2022-12-07 CN CN202280090617.XA patent/CN118660969A/zh active Pending
- 2022-12-07 US US18/718,021 patent/US20240335565A1/en active Pending