JP2023536902A5 - - Google Patents
Info
- Publication number
- JP2023536902A5 JP2023536902A5 JP2023507555A JP2023507555A JP2023536902A5 JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5 JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023507555 A JP2023507555 A JP 2023507555A JP 2023536902 A5 JP2023536902 A5 JP 2023536902A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- vector
- expression cassette
- pharmaceutical composition
- identity
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2026068303A JP2026123072A (ja) | 2020-08-05 | 2026-04-17 | Ｇｌｕｔ１発現のためのアデノ随伴ウイルスベクターおよびその使用 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063061726P | 2020-08-05 | 2020-08-05 | |
| US63/061,726 | 2020-08-05 | ||
| PCT/US2021/044416 WO2022031760A1 (en) | 2020-08-05 | 2021-08-03 | Adeno-associated viral vector for glut1 expression and uses thereof |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2026068303A Division JP2026123072A (ja) | 2020-08-05 | 2026-04-17 | Ｇｌｕｔ１発現のためのアデノ随伴ウイルスベクターおよびその使用 |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2023536902A JP2023536902A (ja) | 2023-08-30 |
| JP2023536902A5 true JP2023536902A5 (enExample) | 2024-08-13 |
| JP7853952B2 JP7853952B2 (ja) | 2026-04-30 |
Family
ID=80118621
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507555A Active JP7853952B2 (ja) | 2020-08-05 | 2021-08-03 | Ｇｌｕｔ１発現のためのアデノ随伴ウイルスベクターおよびその使用 |
| JP2026068303A Pending JP2026123072A (ja) | 2020-08-05 | 2026-04-17 | Ｇｌｕｔ１発現のためのアデノ随伴ウイルスベクターおよびその使用 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2026068303A Pending JP2026123072A (ja) | 2020-08-05 | 2026-04-17 | Ｇｌｕｔ１発現のためのアデノ随伴ウイルスベクターおよびその使用 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20230272422A1 (enExample) |
| EP (1) | EP4192960A4 (enExample) |
| JP (2) | JP7853952B2 (enExample) |
| KR (1) | KR20230043123A (enExample) |
| CN (1) | CN116113700A (enExample) |
| AU (1) | AU2021321412A1 (enExample) |
| BR (1) | BR112023001418A2 (enExample) |
| CA (1) | CA3184233A1 (enExample) |
| IL (1) | IL300185A (enExample) |
| MX (1) | MX2023001419A (enExample) |
| WO (1) | WO2022031760A1 (enExample) |
Families Citing this family (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102673203B1 (ko) | 2016-04-20 | 2024-06-10 | 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피. | Pklr의 유전자 발현 증강을 위한 조성물 및 방법 |
| AU2018352583B2 (en) | 2017-10-16 | 2025-04-17 | Centro de Investigaciones Energeticas, Medioambientales Y Tecnologicas, O.A., M.P. | Lentiviral vectors for delivery of PKLR to treat Pyruvate Kinase Deficiency |
| US12539316B2 (en) | 2018-04-11 | 2026-02-03 | Spacecraft Seven, Llc | Compositions and methods for stem cell transplant |
| IL278213B2 (en) | 2018-04-27 | 2026-04-01 | Rocket Pharmaceuticals Ltd | A gene therapy vector encoding an e3 ubiquitin protein ligase (park2) and use thereof in treating or inhibiting the onset of parkinson’s disease (pd) |
| IL280465B2 (en) | 2018-07-30 | 2025-03-01 | Centro De Investig Energeticas Medioambientales Y Tecnologicas O A M P | Methods for gene modification of hematopoietic cells |
| WO2022032226A1 (en) | 2020-08-07 | 2022-02-10 | Spacecraft Seven, Llc | Plakophilin-2 (pkp2) gene therapy using aav vector |
| CN114457045B (zh) * | 2022-02-25 | 2023-07-14 | 中国人民解放军军事科学院军事医学研究院 | 抑制Slc2a1的RNAi腺相关病毒及其制备和应用 |
| CN121219415A (zh) * | 2023-10-19 | 2025-12-26 | 北京脑科学与类脑研究所 | 一种脑血管内皮细胞嵌合型启动子和重组表达载体及应用 |
| WO2025137149A1 (en) * | 2023-12-19 | 2025-06-26 | The Trustees Of Columbia University In The City Of New York | Compositions and methods for therapeutic vectors targeting brain microvasculature |
Family Cites Families (12)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2004514407A (ja) | 2000-04-28 | 2004-05-20 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 異種キャプシド中にシュードタイピングされたａａｖ５キャプシドおよびａａｖ５ベクターを含む組換えａａｖベクター |
| US8071740B2 (en) * | 2000-11-17 | 2011-12-06 | Vascular Biogenics Ltd. | Promoters exhibiting endothelial cell specificity and methods of using same for regulation of angiogenesis |
| CN103589692B (zh) | 2001-11-13 | 2018-07-24 | 宾夕法尼亚大学托管会 | 检测和/或鉴定腺伴随病毒(aav)序列以及分离所鉴定的新型序列的方法 |
| US20070161031A1 (en) * | 2005-12-16 | 2007-07-12 | The Board Of Trustees Of The Leland Stanford Junior University | Functional arrays for high throughput characterization of gene expression regulatory elements |
| CA2693712C (en) | 2007-07-14 | 2018-05-29 | The University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| US9434928B2 (en) | 2011-11-23 | 2016-09-06 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| EP3564379A1 (en) | 2013-09-13 | 2019-11-06 | California Institute of Technology | Selective recovery |
| LT3137497T (lt) | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| MX2017011615A (es) * | 2015-03-10 | 2018-04-11 | Univ Columbia | Construcciones de vectores virales adeno-asociados de glut1 recombinantes y métodos relacionados para restablecer la expresión de glut1. |
| AU2016366549B2 (en) | 2015-12-11 | 2022-11-10 | California Institute Of Technology | Targeting peptides for directing adeno-associated viruses (AAVs) |
| AU2016378480A1 (en) * | 2015-12-22 | 2018-07-12 | Vrije Universiteit Brussel | Endothelium-specific nucleic acid regulatory elements and methods and use thereof |
| JP6996728B2 (ja) * | 2016-01-07 | 2022-01-17 | 学校法人自治医科大学 | グルコーストランスポーター１発現用アデノ随伴ウイルスベクター |
-
2021
- 2021-08-03 AU AU2021321412A patent/AU2021321412A1/en active Pending
- 2021-08-03 CN CN202180057450.2A patent/CN116113700A/zh active Pending
- 2021-08-03 JP JP2023507555A patent/JP7853952B2/ja active Active
- 2021-08-03 US US18/019,393 patent/US20230272422A1/en active Pending
- 2021-08-03 IL IL300185A patent/IL300185A/en unknown
- 2021-08-03 KR KR1020237003435A patent/KR20230043123A/ko active Pending
- 2021-08-03 WO PCT/US2021/044416 patent/WO2022031760A1/en not_active Ceased
- 2021-08-03 CA CA3184233A patent/CA3184233A1/en active Pending
- 2021-08-03 MX MX2023001419A patent/MX2023001419A/es unknown
- 2021-08-03 BR BR112023001418A patent/BR112023001418A2/pt unknown
- 2021-08-03 EP EP21854255.3A patent/EP4192960A4/en active Pending
-
2026
- 2026-04-17 JP JP2026068303A patent/JP2026123072A/ja active Pending
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