JP2024545507A5 - - Google Patents

Info

Publication number
JP2024545507A5
JP2024545507A5 JP2024534532A JP2024534532A JP2024545507A5 JP 2024545507 A5 JP2024545507 A5 JP 2024545507A5 JP 2024534532 A JP2024534532 A JP 2024534532A JP 2024534532 A JP2024534532 A JP 2024534532A JP 2024545507 A5 JP2024545507 A5 JP 2024545507A5
Authority
JP
Japan
Prior art keywords
approximately
vector
tnnc1
polynucleotide
promoter
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024534532A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024545507A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081282 external-priority patent/WO2023108129A1/en
Publication of JP2024545507A publication Critical patent/JP2024545507A/ja
Publication of JP2024545507A5 publication Critical patent/JP2024545507A5/ja
Pending legal-status Critical Current

Links

JP2024534532A 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療 Pending JP2024545507A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163288255P 2021-12-10 2021-12-10
US63/288,255 2021-12-10
PCT/US2022/081282 WO2023108129A1 (en) 2021-12-10 2022-12-09 Troponin c (tnnc1) gene therapy using aav vector

Publications (2)

Publication Number Publication Date
JP2024545507A JP2024545507A (ja) 2024-12-09
JP2024545507A5 true JP2024545507A5 (enExample) 2025-10-29

Family

ID=86731323

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024534532A Pending JP2024545507A (ja) 2021-12-10 2022-12-09 Aavベクターを用いたトロポニンc(tnnc1)遺伝子治療

Country Status (6)

Country Link
US (1) US20240335566A1 (enExample)
EP (1) EP4444893A4 (enExample)
JP (1) JP2024545507A (enExample)
CN (1) CN118613591A (enExample)
CA (1) CA3240616A1 (enExample)
WO (1) WO2023108129A1 (enExample)

Families Citing this family (3)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
HUE055862T2 (hu) 2016-04-20 2021-12-28 Centro De Investig Energeticas Készítmények és eljárások PKLR fokozott génexpressziójára
SG11202002263TA (en) 2017-10-16 2020-04-29 Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency
WO2019200167A1 (en) 2018-04-11 2019-10-17 Rocket Pharmaceuticals, Ltd. Compositions and methods for stem cell transplant

Family Cites Families (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
JP5553547B2 (ja) * 2009-07-14 2014-07-16 俊一 梶岡 トロポニン含有医薬組成物
EP2714709B1 (en) * 2011-05-26 2018-04-18 University of Washington Compositions for use in cell and gene based methods to improve cardiac function
EP2792742A1 (en) * 2013-04-17 2014-10-22 Universitätsklinikum Hamburg-Eppendorf (UKE) Gene-therapy vectors for treating cardiomyopathy
WO2018178067A1 (en) * 2017-03-27 2018-10-04 Vrije Universiteit Brussel Diaphragm-specific nucleic acid regulatory elements and methods and use thereof
EP3947700A4 (en) * 2019-04-01 2023-01-04 Tenaya Therapeutics, Inc. Adeno-associated virus with engineered capsid
AR126660A1 (es) * 2021-07-28 2023-11-01 Univ Brussel Vrije Mejorando la eficacia de la terapia génica dirigida a músculos

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