JP2022520232A5 - - Google Patents
Info
- Publication number
- JP2022520232A5 JP2022520232A5 JP2021546891A JP2021546891A JP2022520232A5 JP 2022520232 A5 JP2022520232 A5 JP 2022520232A5 JP 2021546891 A JP2021546891 A JP 2021546891A JP 2021546891 A JP2021546891 A JP 2021546891A JP 2022520232 A5 JP2022520232 A5 JP 2022520232A5
- Authority
- JP
- Japan
- Prior art keywords
- gene therapy
- therapy vector
- raav gene
- raav
- administration
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025007633A JP2025063228A (ja) | 2019-02-12 | 2025-01-20 | ダノン病の治療のための遺伝子療法ベクター |
Applications Claiming Priority (5)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962804521P | 2019-02-12 | 2019-02-12 | |
| US62/804,521 | 2019-02-12 | ||
| US201962934928P | 2019-11-13 | 2019-11-13 | |
| US62/934,928 | 2019-11-13 | ||
| PCT/US2020/017987 WO2020167996A1 (en) | 2019-02-12 | 2020-02-12 | Gene therapy vectors for treatment of danon disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025007633A Division JP2025063228A (ja) | 2019-02-12 | 2025-01-20 | ダノン病の治療のための遺伝子療法ベクター |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022520232A JP2022520232A (ja) | 2022-03-29 |
| JP2022520232A5 true JP2022520232A5 (enExample) | 2023-02-21 |
Family
ID=72043957
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021546891A Pending JP2022520232A (ja) | 2019-02-12 | 2020-02-12 | ダノン病の治療のための遺伝子療法ベクター |
| JP2025007633A Pending JP2025063228A (ja) | 2019-02-12 | 2025-01-20 | ダノン病の治療のための遺伝子療法ベクター |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025007633A Pending JP2025063228A (ja) | 2019-02-12 | 2025-01-20 | ダノン病の治療のための遺伝子療法ベクター |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220143215A1 (enExample) |
| EP (1) | EP3924371A4 (enExample) |
| JP (2) | JP2022520232A (enExample) |
| KR (1) | KR20210125999A (enExample) |
| CN (2) | CN120324641A (enExample) |
| AU (3) | AU2020221842A1 (enExample) |
| BR (1) | BR112021015751A2 (enExample) |
| CA (1) | CA3128514A1 (enExample) |
| IL (1) | IL285238A (enExample) |
| MX (1) | MX2021009696A (enExample) |
| SG (1) | SG11202107744SA (enExample) |
| WO (1) | WO2020167996A1 (enExample) |
Families Citing this family (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
| KR102918544B1 (ko) * | 2018-07-12 | 2026-01-27 | 로켓 파마슈티컬스, 리미티드 | 다논병을 치료하기 위한 유전자 요법 벡터 |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| CN116887868A (zh) * | 2020-12-07 | 2023-10-13 | 太空飞船七有限责任公司 | 达农病的治疗 |
| CN114874990A (zh) * | 2021-02-05 | 2022-08-09 | 中国科学院苏州纳米技术与纳米仿生研究所 | 一种功能化外泌体及其制备方法和应用 |
| US12609410B2 (en) | 2021-09-23 | 2026-04-21 | Lg Energy Solution, Ltd. | High heat-resistant connector, and battery module, battery pack, and vehicle including the same |
| CN114457112A (zh) * | 2022-02-07 | 2022-05-10 | 苏州市立医院 | 一种特异性神经靶向mr分子探针及其制备方法和应用 |
| CN115975051B (zh) * | 2022-11-17 | 2025-09-12 | 东南大学 | 靶向外泌体及制备方法、应用、药物和药物递送系统 |
Family Cites Families (9)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2002350039A1 (en) * | 2001-10-29 | 2003-05-12 | Renovis, Inc. | Method for isolating cell-type specific mrnas |
| US9217155B2 (en) * | 2008-05-28 | 2015-12-22 | University Of Massachusetts | Isolation of novel AAV'S and uses thereof |
| US9434928B2 (en) * | 2011-11-23 | 2016-09-06 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| MX367100B (es) * | 2012-02-17 | 2019-08-05 | The Children´S Hospital Of Philadelphia | Composiciones del vector aav y metodos para su transferencia genetica a celulas, organos y tejidos. |
| PT3405215T (pt) * | 2016-01-19 | 2022-09-20 | Univ California | Métodos para o tratamento da doença de danon e outros transtornos da autofagia |
| CA3011939A1 (en) * | 2016-02-02 | 2017-08-10 | University Of Massachusetts | Method to enhance the efficiency of systemic aav gene delivery to the central nervous system |
| WO2019028273A1 (en) * | 2017-08-02 | 2019-02-07 | Dna2.0, Inc. Dba Atum | DNA VECTORS AND ELEMENTS FOR SUSTAINED GENE EXPRESSION IN EUKARYOTIC CELLS |
| KR102918544B1 (ko) * | 2018-07-12 | 2026-01-27 | 로켓 파마슈티컬스, 리미티드 | 다논병을 치료하기 위한 유전자 요법 벡터 |
| EP3833745A1 (en) * | 2018-08-10 | 2021-06-16 | REGENXBIO Inc. | Scalable method for recombinant aav production |
-
2020
- 2020-02-12 BR BR112021015751A patent/BR112021015751A2/pt unknown
- 2020-02-12 US US17/430,107 patent/US20220143215A1/en active Pending
- 2020-02-12 CN CN202510460177.8A patent/CN120324641A/zh active Pending
- 2020-02-12 WO PCT/US2020/017987 patent/WO2020167996A1/en not_active Ceased
- 2020-02-12 EP EP20754942.9A patent/EP3924371A4/en active Pending
- 2020-02-12 KR KR1020217022811A patent/KR20210125999A/ko active Pending
- 2020-02-12 JP JP2021546891A patent/JP2022520232A/ja active Pending
- 2020-02-12 SG SG11202107744SA patent/SG11202107744SA/en unknown
- 2020-02-12 AU AU2020221842A patent/AU2020221842A1/en not_active Abandoned
- 2020-02-12 CA CA3128514A patent/CA3128514A1/en active Pending
- 2020-02-12 MX MX2021009696A patent/MX2021009696A/es unknown
- 2020-02-12 CN CN202080011825.7A patent/CN113508130A/zh active Pending
-
2021
- 2021-07-29 IL IL285238A patent/IL285238A/en unknown
-
2023
- 2023-03-01 AU AU2023201237A patent/AU2023201237B2/en active Active
-
2025
- 2025-01-20 JP JP2025007633A patent/JP2025063228A/ja active Pending
- 2025-07-09 AU AU2025205318A patent/AU2025205318A1/en active Pending
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