JP2022530359A5 - - Google Patents
Info
- Publication number
- JP2022530359A5 JP2022530359A5 JP2021561810A JP2021561810A JP2022530359A5 JP 2022530359 A5 JP2022530359 A5 JP 2022530359A5 JP 2021561810 A JP2021561810 A JP 2021561810A JP 2021561810 A JP2021561810 A JP 2021561810A JP 2022530359 A5 JP2022530359 A5 JP 2022530359A5
- Authority
- JP
- Japan
- Prior art keywords
- aav
- seq
- polypeptide
- cln6
- item
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Ceased
Links
Priority Applications (1)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| JP2025156997A JP2025181954A (ja) | 2019-04-15 | 2025-09-22 | バッテン病の視覚効果を治療または予防するための遺伝子療法 |
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962834340P | 2019-04-15 | 2019-04-15 | |
| US62/834,340 | 2019-04-15 | ||
| PCT/US2020/028366 WO2020214737A1 (en) | 2019-04-15 | 2020-04-15 | Gene therapy for treating or preventing visual effects in batten disease |
Related Child Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025156997A Division JP2025181954A (ja) | 2019-04-15 | 2025-09-22 | バッテン病の視覚効果を治療または予防するための遺伝子療法 |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2022530359A JP2022530359A (ja) | 2022-06-29 |
| JP2022530359A5 true JP2022530359A5 (enExample) | 2023-04-25 |
Family
ID=70739153
Family Applications (2)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021561810A Ceased JP2022530359A (ja) | 2019-04-15 | 2020-04-15 | バッテン病の視覚効果を治療または予防するための遺伝子療法 |
| JP2025156997A Pending JP2025181954A (ja) | 2019-04-15 | 2025-09-22 | バッテン病の視覚効果を治療または予防するための遺伝子療法 |
Family Applications After (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2025156997A Pending JP2025181954A (ja) | 2019-04-15 | 2025-09-22 | バッテン病の視覚効果を治療または予防するための遺伝子療法 |
Country Status (6)
| Country | Link |
|---|---|
| US (1) | US20220193259A1 (enExample) |
| EP (1) | EP3955969A1 (enExample) |
| JP (2) | JP2022530359A (enExample) |
| AU (1) | AU2020257208A1 (enExample) |
| CA (1) | CA3137080A1 (enExample) |
| WO (1) | WO2020214737A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| CN119213133B (zh) * | 2022-05-16 | 2026-01-06 | 上海天泽云泰生物医药有限公司 | 用于治疗i型戊二酸尿症的重组aav载体 |
| CN120842306B (zh) * | 2025-07-17 | 2026-01-06 | 渤海大学 | 一种仿刺参精抗氧化肽及其制备方法和应用 |
Family Cites Families (26)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US5173414A (en) | 1990-10-30 | 1992-12-22 | Applied Immune Sciences, Inc. | Production of recombinant adeno-associated virus vectors |
| EP0733103B1 (en) | 1993-11-09 | 2004-03-03 | Targeted Genetics Corporation | Generation of high titers of recombinant aav vectors |
| DE69433922T2 (de) | 1993-11-09 | 2005-07-28 | Medical College Of Ohio, Toledo | Stabile zellinie, die in der lage ist, das replikationsgen des adenoassoziertenvirus zu exprimieren |
| US5658785A (en) | 1994-06-06 | 1997-08-19 | Children's Hospital, Inc. | Adeno-associated virus materials and methods |
| US5856152A (en) | 1994-10-28 | 1999-01-05 | The Trustees Of The University Of Pennsylvania | Hybrid adenovirus-AAV vector and methods of use therefor |
| WO1996017947A1 (en) | 1994-12-06 | 1996-06-13 | Targeted Genetics Corporation | Packaging cell lines for generation of high titers of recombinant aav vectors |
| FR2737730B1 (fr) | 1995-08-10 | 1997-09-05 | Pasteur Merieux Serums Vacc | Procede de purification de virus par chromatographie |
| JPH11511326A (ja) | 1995-08-30 | 1999-10-05 | ジエンザイム コーポレイション | アデノウィルスおよびａａｖの精製 |
| JPH11514853A (ja) | 1995-09-08 | 1999-12-21 | ジエンザイム コーポレイション | 遺伝子治療のための改良されたａａｖベクター |
| US5910434A (en) | 1995-12-15 | 1999-06-08 | Systemix, Inc. | Method for obtaining retroviral packaging cell lines producing high transducing efficiency retroviral supernatant |
| EP1696036B1 (en) | 1996-09-06 | 2010-04-21 | The Trustees of The University of Pennsylvania | Use of recombinant adeno-associated virus in the manufacture of a medicament for gene therapy via muscle cells |
| US6566118B1 (en) | 1997-09-05 | 2003-05-20 | Targeted Genetics Corporation | Methods for generating high titer helper-free preparations of released recombinant AAV vectors |
| CA2995542A1 (en) | 1997-09-05 | 1999-03-11 | Genzyme Corporation | Methods for generating high titer helper-free preparations of recombinant aav vectors |
| US6258595B1 (en) | 1999-03-18 | 2001-07-10 | The Trustees Of The University Of Pennsylvania | Compositions and methods for helper-free production of recombinant adeno-associated viruses |
| JP2004514407A (ja) | 2000-04-28 | 2004-05-20 | ザ・トラステイーズ・オブ・ザ・ユニバーシテイ・オブ・ペンシルベニア | 異種キャプシド中にシュードタイピングされたａａｖ５キャプシドおよびａａｖ５ベクターを含む組換えａａｖベクター |
| US9441244B2 (en) | 2003-06-30 | 2016-09-13 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| US9233131B2 (en) | 2003-06-30 | 2016-01-12 | The Regents Of The University Of California | Mutant adeno-associated virus virions and methods of use thereof |
| US9434928B2 (en) | 2011-11-23 | 2016-09-06 | Nationwide Children's Hospital, Inc. | Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides |
| DE102012007232B4 (de) | 2012-04-07 | 2014-03-13 | Susanne Weller | Verfahren zur Herstellung von rotierenden elektrischen Maschinen |
| WO2014006078A1 (en) * | 2012-07-04 | 2014-01-09 | Philip Morris Products S.A. | Combustible heat source with improved binding agent |
| CA2880653C (en) * | 2012-08-01 | 2022-05-17 | Nationwide Children's Hospital | Intrathecal delivery of recombinant adeno-associated virus 9 |
| JP2015092462A (ja) | 2013-09-30 | 2015-05-14 | Tdk株式会社 | 正極及びそれを用いたリチウムイオン二次電池 |
| WO2015141521A1 (ja) | 2014-03-21 | 2015-09-24 | 株式会社日立国際電気 | 基板処理装置、半導体装置の製造方法及び記録媒体 |
| JP6197169B2 (ja) | 2014-09-29 | 2017-09-20 | 東芝メモリ株式会社 | 半導体装置の製造方法 |
| WO2017191274A2 (en) * | 2016-05-04 | 2017-11-09 | Curevac Ag | Rna encoding a therapeutic protein |
| AU2020218501B2 (en) * | 2019-02-04 | 2026-01-29 | Research Institute At Nationwide Children's Hospital | Adeno-associated virus delivery of CLN6 polynucleotide |
-
2020
- 2020-04-15 US US17/604,188 patent/US20220193259A1/en not_active Abandoned
- 2020-04-15 EP EP20726260.1A patent/EP3955969A1/en active Pending
- 2020-04-15 JP JP2021561810A patent/JP2022530359A/ja not_active Ceased
- 2020-04-15 CA CA3137080A patent/CA3137080A1/en active Pending
- 2020-04-15 WO PCT/US2020/028366 patent/WO2020214737A1/en not_active Ceased
- 2020-04-15 AU AU2020257208A patent/AU2020257208A1/en active Pending
-
2025
- 2025-09-22 JP JP2025156997A patent/JP2025181954A/ja active Pending
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