JP2022530264A5 - - Google Patents
Info
- Publication number
- JP2022530264A5 JP2022530264A5 JP2021564486A JP2021564486A JP2022530264A5 JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5 JP 2021564486 A JP2021564486 A JP 2021564486A JP 2021564486 A JP2021564486 A JP 2021564486A JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5
- Authority
- JP
- Japan
- Prior art keywords
- virus particle
- polynucleotide
- aav virus
- aav
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962840360P | 2019-04-29 | 2019-04-29 | |
| US62/840,360 | 2019-04-29 | ||
| PCT/US2020/030427 WO2020223322A1 (en) | 2019-04-29 | 2020-04-29 | Intrathecal and intravenous combination gene therapy for the treatment of infantile batten disease |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022530264A JP2022530264A (ja) | 2022-06-28 |
| JP2022530264A5 true JP2022530264A5 (enExample) | 2023-05-12 |
| JP7788594B2 JP7788594B2 (ja) | 2025-12-19 |
Family
ID=73029200
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021564486A Active JP7788594B2 (ja) | 2019-04-29 | 2020-04-29 | 乳児バッテン病の治療のための髄腔内および静脈内組合せ遺伝子療法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220193268A1 (enExample) |
| EP (1) | EP3963081A4 (enExample) |
| JP (1) | JP7788594B2 (enExample) |
| KR (1) | KR20220046513A (enExample) |
| CN (1) | CN114269935A (enExample) |
| AU (1) | AU2020264438A1 (enExample) |
| BR (1) | BR112021021632A8 (enExample) |
| CA (1) | CA3138274A1 (enExample) |
| IL (1) | IL287608A (enExample) |
| MX (1) | MX2021013275A (enExample) |
| SG (1) | SG11202111908XA (enExample) |
| WO (1) | WO2020223322A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2023303015A1 (en) * | 2022-07-06 | 2025-01-23 | Research Institute At Nationwide Children's Hospital | Adeno-associated virus delivery of cln1 polynucleotide |
| WO2024015794A2 (en) * | 2022-07-12 | 2024-01-18 | The Research Institute At Nationwide Children's Hospital | Adeno-associated virus gene therapy products and methods |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| EP2550359B1 (en) * | 2010-03-23 | 2017-08-09 | Intrexon Corporation | Vectors conditionally expressing therapeutic proteins, host cells comprising the vectors, and uses thereof |
| JP6754361B2 (ja) * | 2014-12-16 | 2020-09-09 | ボード オブ リージェンツ オブ ザ ユニバーシティ オブ ネブラスカ | 若年型バッテン病のための遺伝子療法 |
| JP2019517274A (ja) * | 2016-06-13 | 2019-06-24 | ザ ユニバーシティ オブ ノース カロライナ アット チャペル ヒルＴｈｅ Ｕｎｉｖｅｒｓｉｔｙ Ｏｆ Ｎｏｒｔｈ Ｃａｒｏｌｉｎａ Ａｔ Ｃｈａｐｅｌ Ｈｉｌｌ | 最適化されたｃｌｎ１遺伝子および発現カセットおよびそれらの使用 |
| WO2019011817A1 (en) * | 2017-07-08 | 2019-01-17 | Genethon | TREATMENT OF SPINAL AMYOTROPHY |
| US20210115453A1 (en) | 2017-08-31 | 2021-04-22 | Poseida Therapeutics, Inc. | Transposon system and methods of use |
-
2020
- 2020-04-29 CN CN202080047719.4A patent/CN114269935A/zh active Pending
- 2020-04-29 US US17/607,315 patent/US20220193268A1/en not_active Abandoned
- 2020-04-29 JP JP2021564486A patent/JP7788594B2/ja active Active
- 2020-04-29 WO PCT/US2020/030427 patent/WO2020223322A1/en not_active Ceased
- 2020-04-29 BR BR112021021632A patent/BR112021021632A8/pt not_active Application Discontinuation
- 2020-04-29 KR KR1020217038864A patent/KR20220046513A/ko not_active Withdrawn
- 2020-04-29 AU AU2020264438A patent/AU2020264438A1/en active Pending
- 2020-04-29 CA CA3138274A patent/CA3138274A1/en not_active Abandoned
- 2020-04-29 EP EP20798198.6A patent/EP3963081A4/en active Pending
- 2020-04-29 MX MX2021013275A patent/MX2021013275A/es unknown
- 2020-04-29 SG SG11202111908XA patent/SG11202111908XA/en unknown
-
2021
- 2021-10-27 IL IL287608A patent/IL287608A/en unknown
Similar Documents
| Publication | Publication Date | Title |
|---|---|---|
| US20220331409A1 (en) | Factor ix gene therapy | |
| JP2022520232A5 (enExample) | ||
| JP2025179046A5 (enExample) | ||
| J. McCown | Adeno-associated virus (AAV) vectors in the CNS | |
| JP2022516283A5 (enExample) | ||
| US20250305001A1 (en) | Genetic Construct | |
| JP2023514242A5 (enExample) | ||
| JP2021500922A5 (enExample) | ||
| JP2021533805A5 (enExample) | ||
| RU2018145010A (ru) | Оптимизированные гены и экспрессионные кассеты cln1, и их применение | |
| JP2025512574A5 (enExample) | ||
| JP2023503850A5 (enExample) | ||
| JP2022533448A5 (enExample) | ||
| JP2022539156A (ja) | ヒアルロン酸を用いた眼組織へのａａｖ媒介形質導入の増強 | |
| JP2024545507A5 (enExample) | ||
| JP2024546103A5 (enExample) | ||
| EP3773748A1 (en) | Bicistronic aav vectors encoding hexosaminidase alpha and beta-subunits and uses thereof | |
| IL298772A (en) | Coding-optimized nucleic acid encoding the SMN1 protein and its use | |
| EP4509606A1 (en) | Nucleic acid construct for treating hereditary coagulation factor deficiency and use thereof | |
| JP2023526923A5 (enExample) | ||
| CA3178591A1 (en) | Immunosuppressive agents and viral delivery re-dosing methods for gene therapy | |
| JP2022530359A5 (enExample) | ||
| JP2023536067A5 (enExample) | ||
| JP2025504478A5 (enExample) | ||
| JP2025503868A5 (enExample) |