JP2022530264A5 - - Google Patents
Info
- Publication number
- JP2022530264A5 JP2022530264A5 JP2021564486A JP2021564486A JP2022530264A5 JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5 JP 2021564486 A JP2021564486 A JP 2021564486A JP 2021564486 A JP2021564486 A JP 2021564486A JP 2022530264 A5 JP2022530264 A5 JP 2022530264A5
- Authority
- JP
- Japan
- Prior art keywords
- virus particle
- polynucleotide
- aav virus
- aav
- sequence
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Granted
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US201962840360P | 2019-04-29 | 2019-04-29 | |
| US62/840,360 | 2019-04-29 | ||
| PCT/US2020/030427 WO2020223322A1 (en) | 2019-04-29 | 2020-04-29 | Intrathecal and intravenous combination gene therapy for the treatment of infantile batten disease |
Publications (3)
| Publication Number | Publication Date |
|---|---|
| JP2022530264A JP2022530264A (ja) | 2022-06-28 |
| JP2022530264A5 true JP2022530264A5 (enExample) | 2023-05-12 |
| JP7788594B2 JP7788594B2 (ja) | 2025-12-19 |
Family
ID=73029200
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2021564486A Active JP7788594B2 (ja) | 2019-04-29 | 2020-04-29 | 乳児バッテン病の治療のための髄腔内および静脈内組合せ遺伝子療法 |
Country Status (12)
| Country | Link |
|---|---|
| US (1) | US20220193268A1 (enExample) |
| EP (1) | EP3963081A4 (enExample) |
| JP (1) | JP7788594B2 (enExample) |
| KR (1) | KR20220046513A (enExample) |
| CN (1) | CN114269935A (enExample) |
| AU (1) | AU2020264438A1 (enExample) |
| BR (1) | BR112021021632A8 (enExample) |
| CA (1) | CA3138274A1 (enExample) |
| IL (1) | IL287608A (enExample) |
| MX (1) | MX2021013275A (enExample) |
| SG (1) | SG11202111908XA (enExample) |
| WO (1) | WO2020223322A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| JP2025524569A (ja) * | 2022-07-06 | 2025-07-30 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | Ｃｌｎ１ポリヌクレオチドのアデノ随伴ウイルス送達 |
| JP2025524636A (ja) * | 2022-07-12 | 2025-07-30 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | アデノ随伴ウイルス遺伝子療法産物及び方法 |
Family Cites Families (5)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR20130010121A (ko) * | 2010-03-23 | 2013-01-25 | 인트렉손 코포레이션 | 치료적 단백질을 조건부로 발현하는 벡터，상기 벡터를 포함하는 숙주 세포 및 이의 용도 |
| WO2016100575A1 (en) * | 2014-12-16 | 2016-06-23 | Board Of Regents Of The University Of Nebraska | Gene therapy for juvenile batten disease |
| CN109415730A (zh) * | 2016-06-13 | 2019-03-01 | 北卡罗来纳大学教堂山分校 | 优化的cln1基因和表达盒以及它们的应用 |
| WO2019011817A1 (en) * | 2017-07-08 | 2019-01-17 | Genethon | TREATMENT OF SPINAL AMYOTROPHY |
| WO2019046815A1 (en) * | 2017-08-31 | 2019-03-07 | Poseida Therapeutics, Inc. | TRANSPOSON SYSTEM AND METHODS OF USE |
-
2020
- 2020-04-29 MX MX2021013275A patent/MX2021013275A/es unknown
- 2020-04-29 SG SG11202111908XA patent/SG11202111908XA/en unknown
- 2020-04-29 JP JP2021564486A patent/JP7788594B2/ja active Active
- 2020-04-29 BR BR112021021632A patent/BR112021021632A8/pt not_active Application Discontinuation
- 2020-04-29 EP EP20798198.6A patent/EP3963081A4/en active Pending
- 2020-04-29 CA CA3138274A patent/CA3138274A1/en not_active Abandoned
- 2020-04-29 AU AU2020264438A patent/AU2020264438A1/en active Pending
- 2020-04-29 WO PCT/US2020/030427 patent/WO2020223322A1/en not_active Ceased
- 2020-04-29 US US17/607,315 patent/US20220193268A1/en active Pending
- 2020-04-29 CN CN202080047719.4A patent/CN114269935A/zh active Pending
- 2020-04-29 KR KR1020217038864A patent/KR20220046513A/ko not_active Withdrawn
-
2021
- 2021-10-27 IL IL287608A patent/IL287608A/en unknown