JP2023536618A5 - - Google Patents
Info
- Publication number
- JP2023536618A5 JP2023536618A5 JP2023507388A JP2023507388A JP2023536618A5 JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5 JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- mlp
- polynucleotide
- vector
- identity
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063061727P | 2020-08-05 | 2020-08-05 | |
| US63/061,727 | 2020-08-05 | ||
| PCT/US2021/044412 WO2022031756A1 (en) | 2020-08-05 | 2021-08-03 | Csrp3 (cysteine and glycine rich protein 3) gene therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023536618A JP2023536618A (ja) | 2023-08-28 |
| JP2023536618A5 true JP2023536618A5 (enExample) | 2024-08-08 |
Family
ID=80118758
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507388A Pending JP2023536618A (ja) | 2020-08-05 | 2021-08-03 | Ｃｓｒｐ３（システイン及びグリシンリッチタンパク質３）遺伝子治療 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20230257431A1 (enExample) |
| EP (1) | EP4192962A4 (enExample) |
| JP (1) | JP2023536618A (enExample) |
| KR (1) | KR20230042468A (enExample) |
| CN (1) | CN116234916A (enExample) |
| AU (1) | AU2021321410A1 (enExample) |
| BR (1) | BR112023001336A2 (enExample) |
| CA (1) | CA3184983A1 (enExample) |
| IL (1) | IL300187A (enExample) |
| MX (1) | MX2023000994A (enExample) |
| WO (1) | WO2022031756A1 (enExample) |
Families Citing this family (10)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| KR102673203B1 (ko) | 2016-04-20 | 2024-06-10 | 센트로 데 인베스띠가씨오네스 에너제티까스 메디오암비엔딸레스 와이 테크놀로지까스, 오.에이., 엠.피. | Pklr의 유전자 발현 증강을 위한 조성물 및 방법 |
| AU2018352583B2 (en) | 2017-10-16 | 2025-04-17 | Centro de Investigaciones Energeticas, Medioambientales Y Tecnologicas, O.A., M.P. | Lentiviral vectors for delivery of PKLR to treat Pyruvate Kinase Deficiency |
| US12539316B2 (en) | 2018-04-11 | 2026-02-03 | Spacecraft Seven, Llc | Compositions and methods for stem cell transplant |
| IL278213B2 (en) | 2018-04-27 | 2026-04-01 | Rocket Pharmaceuticals Ltd | A gene therapy vector encoding an e3 ubiquitin protein ligase (park2) and use thereof in treating or inhibiting the onset of parkinson’s disease (pd) |
| IL280465B2 (en) | 2018-07-30 | 2025-03-01 | Centro De Investig Energeticas Medioambientales Y Tecnologicas O A M P | Methods for gene modification of hematopoietic cells |
| FI4103214T3 (fi) | 2020-02-13 | 2026-07-03 | Tenaya Therapeutics Inc | Geeniterapian vektorit sydänsairauden hoitoon |
| WO2022032226A1 (en) | 2020-08-07 | 2022-02-10 | Spacecraft Seven, Llc | Plakophilin-2 (pkp2) gene therapy using aav vector |
| WO2023159190A1 (en) * | 2022-02-18 | 2023-08-24 | Ginkgo Bioworks, Inc. | Gene therapy for arrhythmogenic cardiomyopathy |
| IL315695A (en) * | 2022-03-18 | 2024-11-01 | Univ Florida | Methods and compositions for treating RBM20-associated cardiomyopathy with a viral vector |
| JP2025512574A (ja) * | 2022-04-22 | 2025-04-17 | スペースクラフト セブン リミテッド ライアビリティ カンパニー | ＡＡＶベクターを使用するＢ細胞リンパ腫２関連Ａｎｔｈａｎｏｇｅｎｅ ３ （ＢＡＧ３）遺伝子治療 |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE10004857A1 (de) * | 2000-02-03 | 2001-08-16 | Schering Ag | MLP-Gen, Nukleinsäuren, Polypeptide und deren Verwendung |
| CA2693712C (en) | 2007-07-14 | 2018-05-29 | The University Of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| EP2792742A1 (en) * | 2013-04-17 | 2014-10-22 | Universitätsklinikum Hamburg-Eppendorf (UKE) | Gene-therapy vectors for treating cardiomyopathy |
| EP3564379A1 (en) | 2013-09-13 | 2019-11-06 | California Institute of Technology | Selective recovery |
| LT3137497T (lt) | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| AU2016366549B2 (en) | 2015-12-11 | 2022-11-10 | California Institute Of Technology | Targeting peptides for directing adeno-associated viruses (AAVs) |
| CN110997923B (zh) * | 2017-03-17 | 2024-01-02 | 全国儿童医院研究所 | 腺相关病毒载体递送肌肉特异性微肌营养不良蛋白以治疗肌营养不良症 |
| DK3684423T5 (da) * | 2017-09-20 | 2024-08-26 | 4D Molecular Therapeutics Inc | Adeno-associerede virusvariantcapsider og fremgangsmåder til anvendelse deraf |
| CA3097375A1 (en) * | 2018-04-27 | 2019-10-31 | Universitat Heidelberg | Modified aav capsid polypeptides for treatment of muscular diseases |
| CN112272705A (zh) * | 2018-06-08 | 2021-01-26 | 佛罗里达大学研究基金会有限公司 | 用于心肌病的aav心脏基因治疗 |
| CN114450411A (zh) * | 2019-04-01 | 2022-05-06 | 特纳亚治疗股份有限公司 | 具有工程化衣壳的腺相关病毒 |
-
2021
- 2021-08-03 IL IL300187A patent/IL300187A/en unknown
- 2021-08-03 WO PCT/US2021/044412 patent/WO2022031756A1/en not_active Ceased
- 2021-08-03 EP EP21852527.7A patent/EP4192962A4/en active Pending
- 2021-08-03 MX MX2023000994A patent/MX2023000994A/es unknown
- 2021-08-03 CA CA3184983A patent/CA3184983A1/en active Pending
- 2021-08-03 BR BR112023001336A patent/BR112023001336A2/pt unknown
- 2021-08-03 CN CN202180057650.8A patent/CN116234916A/zh active Pending
- 2021-08-03 AU AU2021321410A patent/AU2021321410A1/en active Pending
- 2021-08-03 KR KR1020237003436A patent/KR20230042468A/ko active Pending
- 2021-08-03 US US18/019,396 patent/US20230257431A1/en active Pending
- 2021-08-03 JP JP2023507388A patent/JP2023536618A/ja active Pending
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