JP2023536618A5 - - Google Patents
Info
- Publication number
- JP2023536618A5 JP2023536618A5 JP2023507388A JP2023507388A JP2023536618A5 JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5 JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023507388 A JP2023507388 A JP 2023507388A JP 2023536618 A5 JP2023536618 A5 JP 2023536618A5
- Authority
- JP
- Japan
- Prior art keywords
- promoter
- mlp
- polynucleotide
- vector
- identity
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (3)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| US202063061727P | 2020-08-05 | 2020-08-05 | |
| US63/061,727 | 2020-08-05 | ||
| PCT/US2021/044412 WO2022031756A1 (en) | 2020-08-05 | 2021-08-03 | Csrp3 (cysteine and glycine rich protein 3) gene therapy |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023536618A JP2023536618A (ja) | 2023-08-28 |
| JP2023536618A5 true JP2023536618A5 (enExample) | 2024-08-08 |
Family
ID=80118758
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023507388A Pending JP2023536618A (ja) | 2020-08-05 | 2021-08-03 | Ｃｓｒｐ３（システイン及びグリシンリッチタンパク質３）遺伝子治療 |
Country Status (11)
| Country | Link |
|---|---|
| US (1) | US20230257431A1 (enExample) |
| EP (1) | EP4192962A4 (enExample) |
| JP (1) | JP2023536618A (enExample) |
| KR (1) | KR20230042468A (enExample) |
| CN (1) | CN116234916A (enExample) |
| AU (1) | AU2021321410A1 (enExample) |
| BR (1) | BR112023001336A2 (enExample) |
| CA (1) | CA3184983A1 (enExample) |
| IL (1) | IL300187A (enExample) |
| MX (1) | MX2023000994A (enExample) |
| WO (1) | WO2022031756A1 (enExample) |
Families Citing this family (8)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| HUE055862T2 (hu) | 2016-04-20 | 2021-12-28 | Centro De Investig Energeticas | Készítmények és eljárások PKLR fokozott génexpressziójára |
| SG11202002263TA (en) | 2017-10-16 | 2020-04-29 | Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas | Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency |
| WO2019200167A1 (en) | 2018-04-11 | 2019-10-17 | Rocket Pharmaceuticals, Ltd. | Compositions and methods for stem cell transplant |
| MX2020011386A (es) | 2018-04-27 | 2021-01-29 | Spacecraft Seven Llc | Terapia genica para la degeneracion del snc. |
| EP4103214B1 (en) | 2020-02-13 | 2026-04-29 | Tenaya Therapeutics, Inc. | Gene therapy vectors for treating heart disease |
| KR20230043869A (ko) | 2020-08-07 | 2023-03-31 | 스페이스크래프트 세븐, 엘엘씨 | Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법 |
| JP2025508743A (ja) * | 2022-02-18 | 2025-04-10 | ギンコ バイオワークス インコーポレイテッド | 不整脈原性心筋症のための遺伝子治療 |
| US20250205365A1 (en) * | 2022-03-18 | 2025-06-26 | University Of Florida Research Foundation, Incorporated | Methods and compositions for treating rbm20 related cardiomyopathy with a viral vector |
Family Cites Families (11)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| DE10004857A1 (de) * | 2000-02-03 | 2001-08-16 | Schering Ag | MLP-Gen, Nukleinsäuren, Polypeptide und deren Verwendung |
| EP2176283B1 (en) | 2007-07-14 | 2016-11-02 | University of Iowa Research Foundation | Methods and compositions for treating brain diseases |
| EP2792742A1 (en) * | 2013-04-17 | 2014-10-22 | Universitätsklinikum Hamburg-Eppendorf (UKE) | Gene-therapy vectors for treating cardiomyopathy |
| ES2739288T3 (es) | 2013-09-13 | 2020-01-30 | California Inst Of Techn | Recuperación selectiva |
| LT3137497T (lt) | 2014-05-02 | 2021-07-26 | Genzyme Corporation | Aav vektoriai, skirti tinklainės ir cns genų terapijai |
| KR102423442B1 (ko) | 2015-12-11 | 2022-07-20 | 캘리포니아 인스티튜트 오브 테크놀로지 | 아데노-관련 바이러스를 지시하기 위한 타겟팅 펩타이드 |
| JP7676111B2 (ja) * | 2017-03-17 | 2025-05-14 | リサーチ インスティチュート アット ネイションワイド チルドレンズ ホスピタル | 筋ジストロフィーを治療するための筋肉特異的マイクロジストロフィンのアデノ随伴ウイルスベクター送達 |
| RU2770922C2 (ru) * | 2017-09-20 | 2022-04-25 | 4Д Молекьюлар Терапьютикс Инк. | Капсиды вариантов аденоассоциированных вирусов и методы их применения |
| US20210363193A1 (en) * | 2018-04-27 | 2021-11-25 | Universität Heidelberg | Modified aav capsid polypeptides for treatment of muscular diseases |
| CA3100280A1 (en) * | 2018-06-08 | 2019-12-12 | University Of Florida Research Foundation, Incorporated | Aav cardiac gene therapy for cardiomyopathy |
| EP3947700A4 (en) * | 2019-04-01 | 2023-01-04 | Tenaya Therapeutics, Inc. | Adeno-associated virus with engineered capsid |
-
2021
- 2021-08-03 KR KR1020237003436A patent/KR20230042468A/ko active Pending
- 2021-08-03 MX MX2023000994A patent/MX2023000994A/es unknown
- 2021-08-03 CA CA3184983A patent/CA3184983A1/en active Pending
- 2021-08-03 BR BR112023001336A patent/BR112023001336A2/pt unknown
- 2021-08-03 WO PCT/US2021/044412 patent/WO2022031756A1/en not_active Ceased
- 2021-08-03 JP JP2023507388A patent/JP2023536618A/ja active Pending
- 2021-08-03 US US18/019,396 patent/US20230257431A1/en active Pending
- 2021-08-03 IL IL300187A patent/IL300187A/en unknown
- 2021-08-03 AU AU2021321410A patent/AU2021321410A1/en active Pending
- 2021-08-03 EP EP21852527.7A patent/EP4192962A4/en active Pending
- 2021-08-03 CN CN202180057650.8A patent/CN116234916A/zh active Pending
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