JP2022514271A5 - - Google Patents

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Publication number
JP2022514271A5
JP2022514271A5 JP2021534702A JP2021534702A JP2022514271A5 JP 2022514271 A5 JP2022514271 A5 JP 2022514271A5 JP 2021534702 A JP2021534702 A JP 2021534702A JP 2021534702 A JP2021534702 A JP 2021534702A JP 2022514271 A5 JP2022514271 A5 JP 2022514271A5
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JP
Japan
Prior art keywords
sequence
raav
nucleic acid
composition according
acid molecule
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JP2021534702A
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English (en)
Japanese (ja)
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JP2022514271A (ja
JP7486274B2 (ja
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Priority claimed from PCT/US2019/067247 external-priority patent/WO2020132115A1/en
Publication of JP2022514271A publication Critical patent/JP2022514271A/ja
Publication of JP2022514271A5 publication Critical patent/JP2022514271A5/ja
Application granted granted Critical
Publication of JP7486274B2 publication Critical patent/JP7486274B2/ja
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JP2021534702A 2018-12-18 2019-12-18 糖原病を処置するための方法および組成物 Active JP7486274B2 (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US201862781380P 2018-12-18 2018-12-18
US62/781,380 2018-12-18
PCT/US2019/067247 WO2020132115A1 (en) 2018-12-18 2019-12-18 Methods and compositions for treating glycogen storage diseases

Publications (3)

Publication Number Publication Date
JP2022514271A JP2022514271A (ja) 2022-02-10
JP2022514271A5 true JP2022514271A5 (enExample) 2022-05-20
JP7486274B2 JP7486274B2 (ja) 2024-05-17

Family

ID=69400618

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2021534702A Active JP7486274B2 (ja) 2018-12-18 2019-12-18 糖原病を処置するための方法および組成物

Country Status (15)

Country Link
US (1) US12692512B2 (enExample)
EP (1) EP3898981B1 (enExample)
JP (1) JP7486274B2 (enExample)
KR (1) KR102965926B1 (enExample)
CN (1) CN113454226B (enExample)
AU (1) AU2019405758B2 (enExample)
BR (1) BR112021012104A2 (enExample)
CA (1) CA3123841A1 (enExample)
DK (1) DK3898981T5 (enExample)
ES (1) ES2969222T3 (enExample)
IL (1) IL283956A (enExample)
MX (1) MX2021007379A (enExample)
PL (1) PL3898981T3 (enExample)
PT (1) PT3898981T (enExample)
WO (1) WO2020132115A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2023069891A1 (en) * 2021-10-19 2023-04-27 University Of Connecticut Compositions and methods for the treatment of glycogen storage disorders

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