JP2024545183A5 - - Google Patents

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Publication number
JP2024545183A5
JP2024545183A5 JP2024534647A JP2024534647A JP2024545183A5 JP 2024545183 A5 JP2024545183 A5 JP 2024545183A5 JP 2024534647 A JP2024534647 A JP 2024534647A JP 2024534647 A JP2024534647 A JP 2024534647A JP 2024545183 A5 JP2024545183 A5 JP 2024545183A5
Authority
JP
Japan
Prior art keywords
sequence
nucleic acid
raav
particles
expression construct
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2024534647A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024545183A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2022/081323 external-priority patent/WO2023108159A1/en
Publication of JP2024545183A publication Critical patent/JP2024545183A/ja
Publication of JP2024545183A5 publication Critical patent/JP2024545183A5/ja
Pending legal-status Critical Current

Links

JP2024534647A 2021-12-10 2022-12-09 ウイルスベクターによりbag-3関連心筋症を処置するための方法および組成物 Pending JP2024545183A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202163288520P 2021-12-10 2021-12-10
US63/288,520 2021-12-10
PCT/US2022/081323 WO2023108159A1 (en) 2021-12-10 2022-12-09 Methods and compositions for treating bag-3 related cardiomyopathy with a viral vector

Publications (2)

Publication Number Publication Date
JP2024545183A JP2024545183A (ja) 2024-12-05
JP2024545183A5 true JP2024545183A5 (enExample) 2025-12-17

Family

ID=86731334

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2024534647A Pending JP2024545183A (ja) 2021-12-10 2022-12-09 ウイルスベクターによりbag-3関連心筋症を処置するための方法および組成物

Country Status (8)

Country Link
US (1) US20250041453A1 (enExample)
EP (1) EP4444364A4 (enExample)
JP (1) JP2024545183A (enExample)
KR (1) KR20240118855A (enExample)
AU (1) AU2022407655A1 (enExample)
CA (1) CA3242351A1 (enExample)
IL (1) IL313427A (enExample)
WO (1) WO2023108159A1 (enExample)

Families Citing this family (4)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
US20250195694A1 (en) * 2022-03-18 2025-06-19 University Of Florida Research Foundation, Incorporated Methods and compositions for treating tnnt2 related cardiomyopathy with a viral vector
KR20250169529A (ko) * 2023-02-13 2025-12-03 아스트라제네카 아일랜드 리미티드 유전자 요법을 위한 Bcl2-관련 아타노진 3(BAG3)을 인코딩하는 핵산
WO2024215655A1 (en) * 2023-04-10 2024-10-17 Tenaya Therapeutics, Inc. Cardioprotective bag3 therapies
AU2024265705A1 (en) * 2023-05-02 2025-11-20 Research Institute At Nationwide Children's Hospital Gene therapy for treatment of protein misfolding diseases

Family Cites Families (7)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
WO2015117010A2 (en) * 2014-01-31 2015-08-06 Temple University Of The Commonwealth System Of Higher Education Bag3 as a target for therapy of heart failure
WO2015153889A2 (en) * 2014-04-02 2015-10-08 University Of Florida Research Foundation, Incorporated Materials and methods for the treatment of latent viral infection
WO2017191274A2 (en) * 2016-05-04 2017-11-09 Curevac Ag Rna encoding a therapeutic protein
US20190328836A1 (en) * 2017-01-09 2019-10-31 Duke University Methods for treating ischemic injury
CN113015742A (zh) * 2018-06-08 2021-06-22 联邦高等教育系统天普大学 优化bag3基因治疗
KR20210112339A (ko) * 2019-01-04 2021-09-14 울트라제닉스 파마수티컬 인코포레이티드 윌슨병을 치료하기 위한 유전자 요법 구축물
WO2021154923A2 (en) * 2020-01-29 2021-08-05 Voyager Therapeutics, Inc. Methods and systems for producing aav particles

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