JP2024500786A5 - - Google Patents

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Publication number
JP2024500786A5
JP2024500786A5 JP2023537130A JP2023537130A JP2024500786A5 JP 2024500786 A5 JP2024500786 A5 JP 2024500786A5 JP 2023537130 A JP2023537130 A JP 2023537130A JP 2023537130 A JP2023537130 A JP 2023537130A JP 2024500786 A5 JP2024500786 A5 JP 2024500786A5
Authority
JP
Japan
Prior art keywords
aav
sequence
construct
itr
utr
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023537130A
Other languages
English (en)
Japanese (ja)
Other versions
JP2024500786A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/064924 external-priority patent/WO2022146839A1/en
Publication of JP2024500786A publication Critical patent/JP2024500786A/ja
Publication of JP2024500786A5 publication Critical patent/JP2024500786A5/ja
Pending legal-status Critical Current

Links

JP2023537130A 2020-12-29 2021-12-22 Clrn1関連難聴及び/または視力低下を治療するための組成物及び方法 Pending JP2024500786A (ja)

Applications Claiming Priority (3)

Application Number Priority Date Filing Date Title
US202063131413P 2020-12-29 2020-12-29
US63/131,413 2020-12-29
PCT/US2021/064924 WO2022146839A1 (en) 2020-12-29 2021-12-22 Compositions and methods for treating clrn1-associated hearing loss and/or vision loss

Publications (2)

Publication Number Publication Date
JP2024500786A JP2024500786A (ja) 2024-01-10
JP2024500786A5 true JP2024500786A5 (enExample) 2024-12-27

Family

ID=80050943

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023537130A Pending JP2024500786A (ja) 2020-12-29 2021-12-22 Clrn1関連難聴及び/または視力低下を治療するための組成物及び方法

Country Status (16)

Country Link
US (1) US20240139344A1 (enExample)
EP (1) EP4271419A1 (enExample)
JP (1) JP2024500786A (enExample)
KR (1) KR20230127263A (enExample)
CN (1) CN117157108A (enExample)
AU (1) AU2021412962A1 (enExample)
CA (1) CA3203373A1 (enExample)
CL (1) CL2023001896A1 (enExample)
CO (1) CO2023007325A2 (enExample)
DO (2) DOP2023000132A (enExample)
EC (1) ECSP23057004A (enExample)
IL (1) IL304006A (enExample)
JO (1) JOP20230151A1 (enExample)
MX (1) MX2023007800A (enExample)
PE (1) PE20240012A1 (enExample)
WO (1) WO2022146839A1 (enExample)

Families Citing this family (1)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CN120285151B (zh) * 2025-04-14 2026-03-31 山东第一医科大学(山东省医学科学院) HuR及其编码基因在制备治疗老年性耳聋药物中的应用

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WO2019200016A1 (en) * 2018-04-10 2019-10-17 President And Fellows Of Harvard College Aav vectors encoding clarin-1 or gjb2 and uses thereof
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