JP2023542279A5 - - Google Patents
Info
- Publication number
- JP2023542279A5 JP2023542279A5 JP2023512665A JP2023512665A JP2023542279A5 JP 2023542279 A5 JP2023542279 A5 JP 2023542279A5 JP 2023512665 A JP2023512665 A JP 2023512665A JP 2023512665 A JP2023512665 A JP 2023512665A JP 2023542279 A5 JP2023542279 A5 JP 2023542279A5
- Authority
- JP
- Japan
- Prior art keywords
- sequence
- promoter
- composition according
- seq
- polynucleotide
- Prior art date
- Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
- Pending
Links
Applications Claiming Priority (2)
| Application Number | Priority Date | Filing Date | Title |
|---|---|---|---|
| CN202010705069.XA CN113952472A (zh) | 2020-07-21 | 2020-07-21 | 用于治疗眼部疾病的组合物和方法 |
| PCT/IB2021/000509 WO2022018518A1 (en) | 2020-07-21 | 2021-07-20 | Compositions and methods for the treatment of eye diseases |
Publications (2)
| Publication Number | Publication Date |
|---|---|
| JP2023542279A JP2023542279A (ja) | 2023-10-06 |
| JP2023542279A5 true JP2023542279A5 (enExample) | 2024-07-26 |
Family
ID=79459955
Family Applications (1)
| Application Number | Title | Priority Date | Filing Date |
|---|---|---|---|
| JP2023512665A Pending JP2023542279A (ja) | 2020-07-21 | 2021-07-20 | 眼疾患の処置のための組成物および方法 |
Country Status (7)
| Country | Link |
|---|---|
| US (1) | US20230321281A1 (enExample) |
| EP (1) | EP4185319A4 (enExample) |
| JP (1) | JP2023542279A (enExample) |
| CN (2) | CN113952472A (enExample) |
| AU (1) | AU2021312379A1 (enExample) |
| CA (1) | CA3186826A1 (enExample) |
| WO (1) | WO2022018518A1 (enExample) |
Families Citing this family (2)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| US20230340042A1 (en) * | 2020-09-02 | 2023-10-26 | 4D Molecular Therapeutics Inc. | Codon optimized rpgrorf15 genes and uses thereof |
| WO2026032020A1 (zh) * | 2024-08-06 | 2026-02-12 | 北京中因科技有限公司 | Aav介导的rpgr x连锁视网膜变性的基因编辑治疗方法 |
Family Cites Families (14)
| Publication number | Priority date | Publication date | Assignee | Title |
|---|---|---|---|---|
| AU2003297607A1 (en) * | 2002-12-02 | 2004-06-23 | Genvec, Inc | Materials and methods for treating ocular-related disorders |
| EP2872183B1 (en) * | 2012-07-11 | 2018-09-26 | The Trustees Of The University Of Pennsylvania | Aav-mediated gene therapy for rpgr x-linked retinal degeneration |
| JP5971661B2 (ja) * | 2012-09-19 | 2016-08-17 | 国立大学法人 東京大学 | 神経活動依存的プロモータ活性を有するｄｎａ、及びこれを含むベクター |
| EP3030665B9 (en) * | 2013-08-05 | 2023-10-04 | Academisch Ziekenhuis Leiden H.O.D.N. Leids Universitair Medisch Centrum | Recombinant aav-crumbs homologue composition and methods for treating lca-8 and progressive rp |
| RU2723101C2 (ru) * | 2013-12-06 | 2020-06-08 | Инсерм (Инститьют Насьонал Де Ла Санте Ет Де Ла Решерш Медикаль) | Вектор, способ лечения хороидермии, способ селективной экспрессии полинуклеотида |
| US9534225B2 (en) * | 2014-04-15 | 2017-01-03 | Applied Genetic Technologies Corporation | Codon optimized nucleic acid encoding a retinitis pigmentosa gtpase regulator (RPGR) |
| EP3137497B2 (en) * | 2014-05-02 | 2025-03-05 | Genzyme Corporation | Aav vectors for retinal and cns gene therapy |
| US20160346359A1 (en) * | 2015-05-01 | 2016-12-01 | Spark Therapeutics, Inc. | Adeno-associated Virus-Mediated CRISPR-Cas9 Treatment of Ocular Disease |
| GB201516066D0 (en) * | 2015-09-10 | 2015-10-28 | Young & Co Llp D | Treatment of retinitis pigmentosa |
| EP4700118A3 (en) * | 2016-07-29 | 2026-04-22 | The Regents of the University of California | Adeno-associated virus virions with varint capsid and methods of use thereof |
| EP3645052A4 (en) * | 2017-06-30 | 2021-07-28 | Regents of the University of California | ADENO-ASSOCIATED VIRUS VIRIONS WITH ASSOCIATED CAPSIDE VARIANTS AND METHODS OF USE |
| AR114350A1 (es) * | 2018-01-31 | 2020-08-26 | Res Institute At Nationwide ChildrenS Hospital | Terapia genética para la distrofia muscular de cinturas del tipo 2c |
| JP2022501376A (ja) * | 2018-09-21 | 2022-01-06 | ナイトスター リミテッド | 網膜色素変性症を処置するための組成物及び方法 |
| EP4087617A4 (en) * | 2020-01-10 | 2024-05-01 | Solid Biosciences Inc. | VIRAL VECTOR FOR COMBINATION THERAPY |
-
2020
- 2020-07-21 CN CN202010705069.XA patent/CN113952472A/zh active Pending
-
2021
- 2021-07-20 WO PCT/IB2021/000509 patent/WO2022018518A1/en not_active Ceased
- 2021-07-20 CA CA3186826A patent/CA3186826A1/en active Pending
- 2021-07-20 CN CN202180064480.6A patent/CN116615552A/zh active Pending
- 2021-07-20 EP EP21845856.0A patent/EP4185319A4/en active Pending
- 2021-07-20 JP JP2023512665A patent/JP2023542279A/ja active Pending
- 2021-07-20 AU AU2021312379A patent/AU2021312379A1/en not_active Abandoned
-
2023
- 2023-01-20 US US18/157,589 patent/US20230321281A1/en active Pending
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