JP2018526994A5 - - Google Patents

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Publication number
JP2018526994A5
JP2018526994A5 JP2018510981A JP2018510981A JP2018526994A5 JP 2018526994 A5 JP2018526994 A5 JP 2018526994A5 JP 2018510981 A JP2018510981 A JP 2018510981A JP 2018510981 A JP2018510981 A JP 2018510981A JP 2018526994 A5 JP2018526994 A5 JP 2018526994A5
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JP
Japan
Prior art keywords
raav
epo
sequence
promoter
seq
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Granted
Application number
JP2018510981A
Other languages
English (en)
Japanese (ja)
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JP2018526994A (ja
JP6877408B2 (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2016/049487 external-priority patent/WO2017040524A1/en
Publication of JP2018526994A publication Critical patent/JP2018526994A/ja
Publication of JP2018526994A5 publication Critical patent/JP2018526994A5/ja
Application granted granted Critical
Publication of JP6877408B2 publication Critical patent/JP6877408B2/ja
Active legal-status Critical Current
Anticipated expiration legal-status Critical

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JP2018510981A 2015-08-31 2016-08-30 ペット治療用aav−epo Active JP6877408B2 (ja)

Applications Claiming Priority (5)

Application Number Priority Date Filing Date Title
US201562212144P 2015-08-31 2015-08-31
US62/212,144 2015-08-31
US201662336211P 2016-05-13 2016-05-13
US62/336,211 2016-05-13
PCT/US2016/049487 WO2017040524A1 (en) 2015-08-31 2016-08-30 Aav-epo for treating companion animals

Publications (3)

Publication Number Publication Date
JP2018526994A JP2018526994A (ja) 2018-09-20
JP2018526994A5 true JP2018526994A5 (enExample) 2019-09-26
JP6877408B2 JP6877408B2 (ja) 2021-05-26

Family

ID=58188403

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2018510981A Active JP6877408B2 (ja) 2015-08-31 2016-08-30 ペット治療用aav−epo

Country Status (10)

Country Link
US (2) US11117942B2 (enExample)
EP (1) EP3344650B1 (enExample)
JP (1) JP6877408B2 (enExample)
KR (1) KR20180057636A (enExample)
CN (1) CN108137664B (enExample)
AU (1) AU2016315699B2 (enExample)
CA (1) CA2995733A1 (enExample)
ES (1) ES3069921T3 (enExample)
HK (1) HK1257024A1 (enExample)
WO (1) WO2017040524A1 (enExample)

Families Citing this family (6)

* Cited by examiner, † Cited by third party
Publication number Priority date Publication date Assignee Title
CA3068328A1 (en) * 2017-07-06 2019-01-10 The Trustees Of The University Of Pennsylvania Aav9-mediated gene therapy for treating mucopolysaccharidosis type i
BR112021001498A2 (pt) * 2018-07-27 2021-04-27 Regenxbio Inc. vírus adeno-associado recombinante (raav), composição farmacêutica, polinucleotídeo, plasmídeo de raav, célula ex vivo, método de produção de um raav e métodos para tratar um sujeito humano diagnosticado com mucopolissacaridose tipo iva (mps iva)
JP2022511882A (ja) * 2018-12-12 2022-02-01 キンドレッド バイオサイエンシズ インコーポレイテッド 獣医学的使用のためのエリスロポエチンアナログ
CA3200863A1 (en) * 2020-09-28 2022-03-31 Scout Bio, Inc. Composition and uses thereof
MX2023008826A (es) 2021-02-01 2023-09-15 Regenxbio Inc Terapia génica para lipofuscinosis neuronal ceroidea.
KR20240107201A (ko) 2021-08-31 2024-07-08 스카우트 바이오, 인코포레이티드 항원-결합 분자 및 이의 용도

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US5741683A (en) 1995-06-07 1998-04-21 The Research Foundation Of State University Of New York In vitro packaging of adeno-associated virus DNA
US5846528A (en) * 1996-01-18 1998-12-08 Avigen, Inc. Treating anemia using recombinant adeno-associated virus virions comprising an EPO DNA sequence
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DK2359869T3 (en) 2001-12-17 2019-04-15 Univ Pennsylvania Sequences of adeno-associated virus (AAV) serotype 8, vectors containing these, and uses thereof
AU2003274397A1 (en) 2002-06-05 2003-12-22 University Of Florida Production of pseudotyped recombinant aav virions
EP1668143B1 (en) 2003-09-30 2013-03-20 The Trustees of The University of Pennsylvania Adeno-associated virus (aav) clades, sequences, vectors containing same, and uses therefor
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US9988427B2 (en) * 2005-05-13 2018-06-05 Charite Universitaetsmedizen-Berlin Erythropoietin variants
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