JP2024500786A - Clrn1関連難聴及び/または視力低下を治療するための組成物及び方法 - Google Patents

Clrn1関連難聴及び/または視力低下を治療するための組成物及び方法 Download PDF

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JP2024500786A
JP2024500786A JP2023537130A JP2023537130A JP2024500786A JP 2024500786 A JP2024500786 A JP 2024500786A JP 2023537130 A JP2023537130 A JP 2023537130A JP 2023537130 A JP2023537130 A JP 2023537130A JP 2024500786 A JP2024500786 A JP 2024500786A
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ジョン シモンズ,エマニュエル
ング,ロバート
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アコーオス インコーポレイテッド
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    • C12N2840/00—Vectors comprising a special translation-regulating system
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    • C12N2840/445—Vectors comprising a special translation-regulating system being a specific part of the splice mechanism, e.g. donor, acceptor for trans-splicing, e.g. polypyrimidine tract, branch point splicing

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JP2023537130A 2020-12-29 2021-12-22 Clrn1関連難聴及び/または視力低下を治療するための組成物及び方法 Pending JP2024500786A (ja)

Applications Claiming Priority (3)

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US202063131413P 2020-12-29 2020-12-29
US63/131,413 2020-12-29
PCT/US2021/064924 WO2022146839A1 (en) 2020-12-29 2021-12-22 Compositions and methods for treating clrn1-associated hearing loss and/or vision loss

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JP2024500786A true JP2024500786A (ja) 2024-01-10
JP2024500786A5 JP2024500786A5 (enExample) 2024-12-27

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US (1) US20240139344A1 (enExample)
EP (1) EP4271419A1 (enExample)
JP (1) JP2024500786A (enExample)
KR (1) KR20230127263A (enExample)
CN (1) CN117157108A (enExample)
AU (1) AU2021412962A1 (enExample)
CA (1) CA3203373A1 (enExample)
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MX (1) MX2023007800A (enExample)
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KR20250059407A (ko) * 2022-08-05 2025-05-02 데시벨 테라퓨틱스, 인크. Slc26a4 조절 요소 및 이의 용도
CN120285151B (zh) * 2025-04-14 2026-03-31 山东第一医科大学(山东省医学科学院) HuR及其编码基因在制备治疗老年性耳聋药物中的应用

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ECSP23057004A (es) 2023-08-31
EP4271419A1 (en) 2023-11-08
WO2022146839A1 (en) 2022-07-07
AU2021412962A1 (en) 2023-08-17
DOP2023000132A (es) 2023-07-31
DOP2025000286A (es) 2025-12-30
JOP20230151A1 (ar) 2023-06-25
CN117157108A (zh) 2023-12-01
PE20240012A1 (es) 2024-01-04
CO2023007325A2 (es) 2023-06-20
US20240139344A1 (en) 2024-05-02
CA3203373A1 (en) 2022-07-07
CL2023001896A1 (es) 2023-12-15
KR20230127263A (ko) 2023-08-31
MX2023007800A (es) 2023-07-11
IL304006A (en) 2023-08-01

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