JP2023144087A5 - - Google Patents

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Publication number
JP2023144087A5
JP2023144087A5 JP2023133147A JP2023133147A JP2023144087A5 JP 2023144087 A5 JP2023144087 A5 JP 2023144087A5 JP 2023133147 A JP2023133147 A JP 2023133147A JP 2023133147 A JP2023133147 A JP 2023133147A JP 2023144087 A5 JP2023144087 A5 JP 2023144087A5
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JP
Japan
Prior art keywords
composition
medicament
raav
human subject
glut1
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Pending
Application number
JP2023133147A
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English (en)
Japanese (ja)
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JP2023144087A (ja
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Priority claimed from JP2017548205A external-priority patent/JP2018509164A/ja
Application filed filed Critical
Publication of JP2023144087A publication Critical patent/JP2023144087A/ja
Publication of JP2023144087A5 publication Critical patent/JP2023144087A5/ja
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JP2023133147A 2015-03-10 2023-08-17 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法 Pending JP2023144087A (ja)

Applications Claiming Priority (4)

Application Number Priority Date Filing Date Title
US201562130899P 2015-03-10 2015-03-10
US62/130,899 2015-03-10
JP2017548205A JP2018509164A (ja) 2015-03-10 2016-03-10 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法
JP2021032174A JP2021097689A (ja) 2015-03-10 2021-03-01 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法

Related Parent Applications (1)

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JP2021032174A Division JP2021097689A (ja) 2015-03-10 2021-03-01 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法

Publications (2)

Publication Number Publication Date
JP2023144087A JP2023144087A (ja) 2023-10-06
JP2023144087A5 true JP2023144087A5 (https=) 2024-04-08

Family

ID=56879055

Family Applications (3)

Application Number Title Priority Date Filing Date
JP2017548205A Pending JP2018509164A (ja) 2015-03-10 2016-03-10 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法
JP2021032174A Pending JP2021097689A (ja) 2015-03-10 2021-03-01 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法
JP2023133147A Pending JP2023144087A (ja) 2015-03-10 2023-08-17 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法

Family Applications Before (2)

Application Number Title Priority Date Filing Date
JP2017548205A Pending JP2018509164A (ja) 2015-03-10 2016-03-10 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法
JP2021032174A Pending JP2021097689A (ja) 2015-03-10 2021-03-01 組換えGlut1アデノ随伴ウイルスベクターコンストラクトおよびGlut1発現を回復させる方法

Country Status (18)

Country Link
US (2) US20180042991A1 (https=)
EP (1) EP3268024B1 (https=)
JP (3) JP2018509164A (https=)
KR (2) KR20240119152A (https=)
CN (1) CN107635575A (https=)
AU (1) AU2016229000B2 (https=)
CL (1) CL2017002282A1 (https=)
CO (1) CO2017010149A2 (https=)
DK (1) DK3268024T3 (https=)
EA (1) EA036051B1 (https=)
ES (1) ES2836258T3 (https=)
HU (1) HUE052577T2 (https=)
IL (2) IL282053B2 (https=)
MX (2) MX2017011615A (https=)
PT (1) PT3268024T (https=)
SG (1) SG11201707116QA (https=)
UA (1) UA128249C2 (https=)
WO (1) WO2016145217A1 (https=)

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RU2716991C2 (ru) 2014-11-05 2020-03-17 Вояджер Терапьютикс, Инк. Полинуклеотиды aadc для лечения болезни паркинсона
JP6996728B2 (ja) * 2016-01-07 2022-01-17 学校法人自治医科大学 グルコーストランスポーター1発現用アデノ随伴ウイルスベクター
HUE055862T2 (hu) 2016-04-20 2021-12-28 Centro De Investig Energeticas Készítmények és eljárások PKLR fokozott génexpressziójára
JOP20190200A1 (ar) 2017-02-28 2019-08-27 Univ Pennsylvania تركيبات نافعة في معالجة ضمور العضل النخاعي
JOP20190269A1 (ar) 2017-06-15 2019-11-20 Voyager Therapeutics Inc بولي نوكليوتيدات aadc لعلاج مرض باركنسون
AU2018338728B2 (en) * 2017-09-29 2025-01-02 Centre National De La Recherche Scientifique (Cnrs) Rescue of central and peripheral neurological phenotype of Friedreich's Ataxia by intravenous delivery
US12441998B2 (en) 2017-10-12 2025-10-14 The Trustees Of Columbia University In The City Of New York SLC2A1 lncRNA as a biologic and related treatments and methods
SG11202002263TA (en) 2017-10-16 2020-04-29 Centro De Investigaciones Energeticas Medioambientales Y Tecnologicas Lentiviral vectors for delivery of pklr to treat pyruvate kinase deficiency
WO2019200167A1 (en) 2018-04-11 2019-10-17 Rocket Pharmaceuticals, Ltd. Compositions and methods for stem cell transplant
MX2020011386A (es) 2018-04-27 2021-01-29 Spacecraft Seven Llc Terapia genica para la degeneracion del snc.
AU2019265663B2 (en) * 2018-05-08 2024-06-13 Rutgers, The State University Of New Jersey AAV-compatible laminin-linker polymerization proteins
KR20210019996A (ko) 2018-05-15 2021-02-23 보이저 테라퓨틱스, 인크. 파킨슨병의 치료를 위한 조성물 및 방법
EP3856762A1 (en) 2018-09-28 2021-08-04 Voyager Therapeutics, Inc. Frataxin expression constructs having engineered promoters and methods of use thereof
US11162102B2 (en) 2019-05-13 2021-11-02 Dna Twopointo Inc. Modifications of mammalian cells using artificial micro-RNA to alter their properties and the compositions of their products
AU2020346062A1 (en) * 2019-09-13 2022-03-24 Rutgers, The State University Of New Jersey AAV-compatible laminin-linker polymerization proteins
US20230302104A1 (en) * 2020-05-01 2023-09-28 Atlas Biotechnology S.A. Treatment and/or prevention of a disease or a syndrome related to a virus infection
CA3185234A1 (en) * 2020-07-09 2022-01-13 Dorota Danuta KLYSZ Immune cells with increased glycolytic flux
CN116113700A (zh) * 2020-08-05 2023-05-12 太空飞船七有限责任公司 用于glut1表达的腺相关病毒载体及其用途
KR20230043869A (ko) 2020-08-07 2023-03-31 스페이스크래프트 세븐, 엘엘씨 Aav 벡터를 사용한 플라코필린-2(pkp2) 유전자 요법
WO2022051627A2 (en) * 2020-09-04 2022-03-10 Dna Twopointo Inc. Modifications of mammalian cells using artificial micro-rna to alter their properties and the compositions of their products
IL314602A (en) * 2022-02-08 2024-09-01 Spacecraft Seven Llc Adeno-associated viral vector for GLUT1 expression and uses thereof

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