JP2023545731A5 - - Google Patents

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Publication number
JP2023545731A5
JP2023545731A5 JP2023521337A JP2023521337A JP2023545731A5 JP 2023545731 A5 JP2023545731 A5 JP 2023545731A5 JP 2023521337 A JP2023521337 A JP 2023521337A JP 2023521337 A JP2023521337 A JP 2023521337A JP 2023545731 A5 JP2023545731 A5 JP 2023545731A5
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JP
Japan
Prior art keywords
nucleic acid
sequence
subject
seq
aav vector
Prior art date
Legal status (The legal status is an assumption and is not a legal conclusion. Google has not performed a legal analysis and makes no representation as to the accuracy of the status listed.)
Pending
Application number
JP2023521337A
Other languages
English (en)
Japanese (ja)
Other versions
JP2023545731A (ja
Filing date
Publication date
Application filed filed Critical
Priority claimed from PCT/US2021/053768 external-priority patent/WO2022076556A2/en
Publication of JP2023545731A publication Critical patent/JP2023545731A/ja
Publication of JP2023545731A5 publication Critical patent/JP2023545731A5/ja
Pending legal-status Critical Current

Links

JP2023521337A 2020-10-07 2021-10-06 肢帯型2i(lgmd2i)を含むジストログリカノパチー障害を処置するためのフクチン関連タンパク質(fkrp)の治療的アデノ随伴ウイルス送達 Pending JP2023545731A (ja)

Applications Claiming Priority (7)

Application Number Priority Date Filing Date Title
US202063088757P 2020-10-07 2020-10-07
US63/088,757 2020-10-07
US202163214123P 2021-06-23 2021-06-23
US63/214,123 2021-06-23
US202163229726P 2021-08-05 2021-08-05
US63/229,726 2021-08-05
PCT/US2021/053768 WO2022076556A2 (en) 2020-10-07 2021-10-06 Therapeutic adeno-associated virus delivery of fukutin related protein (fkrp) for treating dystroglycanopathy disorders including limb girdle 2i (lgmd2i)

Publications (2)

Publication Number Publication Date
JP2023545731A JP2023545731A (ja) 2023-10-31
JP2023545731A5 true JP2023545731A5 (https=) 2024-10-15

Family

ID=81127135

Family Applications (1)

Application Number Title Priority Date Filing Date
JP2023521337A Pending JP2023545731A (ja) 2020-10-07 2021-10-06 肢帯型2i(lgmd2i)を含むジストログリカノパチー障害を処置するためのフクチン関連タンパク質(fkrp)の治療的アデノ随伴ウイルス送達

Country Status (7)

Country Link
US (1) US20230374542A1 (https=)
EP (1) EP4225382A4 (https=)
JP (1) JP2023545731A (https=)
AU (1) AU2021358957A1 (https=)
CA (1) CA3195177A1 (https=)
IL (1) IL301955A (https=)
WO (1) WO2022076556A2 (https=)

Families Citing this family (4)

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IL322735A (en) * 2023-02-13 2025-10-01 Astrazeneca Ireland Ltd Nucleic acids encoding BCL2-associated athenogen 3 (BAG3) for gene therapy

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