JP2022031772A5 - - Google Patents

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JP2022031772A5
JP2022031772A5 JP2021189823A JP2021189823A JP2022031772A5 JP 2022031772 A5 JP2022031772 A5 JP 2022031772A5 JP 2021189823 A JP2021189823 A JP 2021189823A JP 2021189823 A JP2021189823 A JP 2021189823A JP 2022031772 A5 JP2022031772 A5 JP 2022031772A5
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Japan
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pharmaceutical composition
sense strand
hemophilia
ligand
seq
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JP2021189823A
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Japanese (ja)
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JP7422120B2 (ja
JP2022031772A (ja
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Priority claimed from PCT/US2016/065245 external-priority patent/WO2017100236A1/en
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Priority to JP2024002987A priority Critical patent/JP7820420B2/ja
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JP2021189823A 2015-12-07 2021-11-24 Serpinc1関連障害を処置するための方法および組成物 Active JP7422120B2 (ja)

Priority Applications (1)

Application Number Priority Date Filing Date Title
JP2024002987A JP7820420B2 (ja) 2015-12-07 2024-01-12 Serpinc1関連障害を処置するための方法および組成物

Applications Claiming Priority (10)

Application Number Priority Date Filing Date Title
US201562264013P 2015-12-07 2015-12-07
US62/264,013 2015-12-07
US201662315228P 2016-03-30 2016-03-30
US62/315,228 2016-03-30
US201662366304P 2016-07-25 2016-07-25
US62/366,304 2016-07-25
US201662429241P 2016-12-02 2016-12-02
US62/429,241 2016-12-02
PCT/US2016/065245 WO2017100236A1 (en) 2015-12-07 2016-12-07 Methods and compositions for treating a serpinc1-associated disorder
JP2018549141A JP6985283B2 (ja) 2015-12-07 2016-12-07 Serpinc1関連障害を処置するための方法および組成物

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JP2018549141A Division JP6985283B2 (ja) 2015-12-07 2016-12-07 Serpinc1関連障害を処置するための方法および組成物

Related Child Applications (1)

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JP2024002987A Division JP7820420B2 (ja) 2015-12-07 2024-01-12 Serpinc1関連障害を処置するための方法および組成物

Publications (3)

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JP2022031772A JP2022031772A (ja) 2022-02-22
JP2022031772A5 true JP2022031772A5 (enExample) 2022-08-22
JP7422120B2 JP7422120B2 (ja) 2024-01-25

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ID=58800158

Family Applications (3)

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JP2018549141A Active JP6985283B2 (ja) 2015-12-07 2016-12-07 Serpinc1関連障害を処置するための方法および組成物
JP2021189823A Active JP7422120B2 (ja) 2015-12-07 2021-11-24 Serpinc1関連障害を処置するための方法および組成物
JP2024002987A Active JP7820420B2 (ja) 2015-12-07 2024-01-12 Serpinc1関連障害を処置するための方法および組成物

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JP2018549141A Active JP6985283B2 (ja) 2015-12-07 2016-12-07 Serpinc1関連障害を処置するための方法および組成物

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JP2024002987A Active JP7820420B2 (ja) 2015-12-07 2024-01-12 Serpinc1関連障害を処置するための方法および組成物

Country Status (25)

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US (2) US11091759B2 (enExample)
EP (2) EP3386518B1 (enExample)
JP (3) JP6985283B2 (enExample)
KR (3) KR20210157474A (enExample)
CN (2) CN120284999A (enExample)
AU (3) AU2016368289C1 (enExample)
BR (1) BR112018011450A2 (enExample)
CA (1) CA3007014A1 (enExample)
CO (1) CO2018006590A2 (enExample)
DK (1) DK3386518T3 (enExample)
ES (1) ES3041380T3 (enExample)
FI (1) FI3386518T3 (enExample)
HR (1) HRP20251125T1 (enExample)
HU (1) HUE072861T2 (enExample)
IL (2) IL308717A (enExample)
LT (1) LT3386518T (enExample)
MX (2) MX2018006989A (enExample)
PL (1) PL3386518T3 (enExample)
PT (1) PT3386518T (enExample)
RS (1) RS67250B1 (enExample)
RU (1) RU2754188C2 (enExample)
SG (2) SG10201913085TA (enExample)
SI (1) SI3386518T1 (enExample)
TW (3) TW202423457A (enExample)
WO (1) WO2017100236A1 (enExample)

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WO2024094698A1 (en) 2022-10-31 2024-05-10 Sanofi Front sub-assembly for a drug delivery device
CN120153425A (zh) 2022-11-02 2025-06-13 建新公司 用于对凝血酶-抗凝血酶建模的系统和方法
CN118853663A (zh) * 2023-04-28 2024-10-29 北京福元医药股份有限公司 用于抑制marc1基因表达的双链核糖核酸及其修饰物、缀合物和用途
CN121263219A (zh) 2023-06-05 2026-01-02 赛诺菲 药物递送装置
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WO2024251792A1 (en) 2023-06-05 2024-12-12 Sanofi Drug delivery device
CN121263160A (zh) 2023-06-05 2026-01-02 赛诺菲 刺孔封闭辅助构件、药物递送装置和方法
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WO2024251800A1 (en) 2023-06-05 2024-12-12 Sanofi Drug delivery device
CN121311264A (zh) 2023-06-05 2026-01-09 赛诺菲 药物递送装置和用于将药物施用元件与药物递送装置的至少一部分断开联接的方法
WO2024251793A1 (en) 2023-06-05 2024-12-12 Sanofi Drug delivery device
CN121285405A (zh) 2023-06-05 2026-01-06 赛诺菲 药物递送装置
WO2025059635A1 (en) 2023-09-15 2025-03-20 Genzyme Corporation Treatment of hemophilia a with fitusiran
WO2025162928A1 (en) 2024-01-29 2025-08-07 Sanofi Needle shroud unlock device for a medicament delivery device
WO2025162926A1 (en) 2024-01-29 2025-08-07 Sanofi Needle arrangement, drug delivery device comprising the needle arrangement and method for operating the drug delivery device
WO2025162927A1 (en) 2024-01-29 2025-08-07 Sanofi Purifying device, system and method for purifying a needle for delivering a medicament
WO2025171279A1 (en) 2024-02-09 2025-08-14 Genzyme Corporation Treatment of hemophilia with fitusiran
TW202547528A (zh) 2024-04-01 2025-12-16 美商健臻公司 以非妥西蘭治療因子x缺失
CN118557756B (zh) * 2024-05-24 2025-04-29 华中科技大学同济医学院附属协和医院 一种基于aav的遗传性抗凝血酶缺乏的基因疗法
WO2026012399A1 (zh) * 2024-07-10 2026-01-15 正大天晴药业集团股份有限公司 靶向serpinc1的双链核糖核酸

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